A conditional knockout mouse model reveals endothelial cells as the principal and possibly exclusive source of plasma factor VIII von Fahs, Scot A., Hille, Matthew T., Shi, Qizhen, Weiler, Hartmut, Montgomery, Robert R.

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Correction of Murine Bernard–Soulier Syndrome by Lentivirus-mediated Gene Therapy von Kanaji, Sachiko, Kuether, Erin L, Fahs, Scot A, Schroeder, Jocelyn A, Ware, Jerry, Montgomery, Robert R, Shi, Qizhen

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The severe spontaneous bleeding phenotype in a novel hemophilia A rat model is rescued by platelet FVIII expression von Shi, Qizhen, Mattson, Jeremy G., Fahs, Scot A., Geurts, Aron M., Weiler, Hartmut, Montgomery, Robert R.

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A rat model of severe VWD by elimination of the VWF gene using CRISPR/Cas9 von Garcia, Jessica, Flood, Veronica H., Haberichter, Sandra L., Fahs, Scot A., Mattson, Jeremy G., Geurts, Aron M., Zogg, Mark, Weiler, Hartmut, Shi, Qizhen, Montgomery, Robert R.

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Platelet gene therapy corrects the hemophilic phenotype in immunocompromised hemophilia A mice transplanted with genetically manipulated human cord blood stem cells von Shi, Qizhen, Kuether, Erin L., Chen, Yingyu, Schroeder, Jocelyn A., Fahs, Scot A., Montgomery, Robert R.

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Re-establishment of VWF-dependent Weibel-Palade bodies in VWD endothelial cells von Haberichter, Sandra L., Merricks, Elizabeth P., Fahs, Scot A., Christopherson, Pamela A., Nichols, Timothy C., Montgomery, Robert R.

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Targeting FVIII expression to endothelial cells regenerates a releasable pool of FVIII and restores hemostasis in a mouse model of hemophilia A von Shi, Qizhen, Fahs, Scot A., Kuether, Erin L., Cooley, Brian C., Weiler, Hartmut, Montgomery, Robert R.

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Syngeneic transplantation of hematopoietic stem cells that are genetically modified to express factor VIII in platelets restores hemostasis to hemophilia A mice with preexisting FV... von Shi, Qizhen, Fahs, Scot A., Wilcox, David A., Kuether, Erin L., Morateck, Patricia A., Mareno, Nicole, Weiler, Hartmut, Montgomery, Robert R.

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Factor VIII ectopically targeted to platelets is therapeutic in hemophilia A with high-titer inhibitory antibodies von Shi, Qizhen, Wilcox, David A, Fahs, Scot A, Weiler, Hartmut, Wells, Clive W, Cooley, Brian C, Desai, Drashti, Morateck, Patricia A, Gorski, Jack, Montgomery, Robert R

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The role of the D1 domain of the von Willebrand factor propeptide in multimerization of VWF von Rosenberg, Jonathan B., Haberichter, Sandra L., Jozwiak, Mary A., Vokac, Elizabeth A., Kroner, Philip A., Fahs, Scot A., Kawai, Yohko, Montgomery, Robert R.

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Factor IX ectopically expressed in platelets can be stored in α-granules and corrects the phenotype of hemophilia B mice von Zhang, Guowei, Shi, Qizhen, Fahs, Scot A., Kuether, Erin L., Walsh, Christopher E., Montgomery, Robert R.

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A novel mouse model of type 2N VWD was developed by CRISPR/Cas9 gene editing and recapitulates human type 2N VWD von Shi, Qizhen, Fahs, Scot A., Mattson, Jeremy G., Yu, Hongyin, Perry, Crystal L., Morateck, Patricia A., Schroeder, Jocelyn A., Rapten, Jessica, Weiler, Hartmut, Montgomery, Robert R.

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Humanized GPIbα–von Willebrand factor interaction in the mouse von Kanaji, Sachiko, Orje, Jennifer N., Kanaji, Taisuke, Kamikubo, Yuichi, Morodomi, Yosuke, Chen, Yunfeng, Zarpellon, Alessandro, Eberhardt, Jerome, Forli, Stefano, Fahs, Scot A., Sood, Rashmi, Haberichter, Sandra L., Montgomery, Robert R., Ruggeri, Zaverio M.

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The Severe Spontaneous Bleeding Phenotype in a Novel Hemophilia a Rat Model with an Inversion Mutation Is Rescued By Platelet-Targeted FVIII Expression von Shi, Qizhen, Mattson, Jeremy G, Fahs, Scot A, Montgomery, Robert R

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A Murine Model of Type 2N VWD Was Developed By CRISPR/Cas9 Gene Editing and Recapitulates Human Type 2N VWD von Montgomery, Robert R, Fahs, Scot A, Mattson, Jeremy G, Weiler, Hartmut, Shi, Qizhen

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Comparative response of plasma VWF in dogs to up-regulation of VWF mRNA by interleukin-11 versus Weibel-Palade body release by desmopressin (DDAVP) von Olsen, EvaH.N., McCain, Arlene S., Merricks, Elizabeth P., Fischer, Thomas H., Dillon, Ivy M., Raymer, Robin A., Bellinger, Dwight A., Fahs, Scot A., Montgomery, Robert R., Keith, James C., Schaub, Robert G., Nichols, Timothy C.

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Von Willebrand Factor Binding to Myosin Assists in Coagulation von Flood, Veronica H, Slobodianuk, Tricia L, Keesler, Daniel A, Lohmeier, Hannah, Fahs, Scot A, Montgomery, Robert R

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Transcriptional Analysis Of a Tissue-Specific Factor VIII Knockout Model Demonstrates The Importance Of Endothelial Factor VIII Synthesis von Fahs, Scot A., Hille, Matthew T., Montgomery, Robert R.

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Non‐myeloablative conditioning with busulfan before hematopoietic stem cell transplantation leads to phenotypic correction of murine Bernard‐Soulier syndrome von Kanaji, S., Fahs, S. A., Ware, J., Montgomery, R. R., Shi, Q.

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Humanized Von Willebrand Factor-Glycoprotein Ibα Interaction in Mouse Models of Hemostasis and Thrombosis von Kanaji, Sachiko, Orje, Jennifer N, Kamikubo, Yuichi, Kanaji, Taisuke, Mattson, Jeremy, Zarpellon, Alessandro, Fahs, Scot A., Sood, Rashmi, Haberichter, Sandra L, Ruggeri, Zaverio M., Montgomery, Robert R

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