Precise therapeutic gene correction by a simple nuclease-induced double-stranded break von Iyer, Sukanya, Suresh, Sneha, Guo, Dongsheng, Daman, Katelyn, Chen, Jennifer C. J., Liu, Pengpeng, Zieger, Marina, Luk, Kevin, Roscoe, Benjamin P., Mueller, Christian, King, Oliver D., Emerson, Charles P., Wolfe, Scot A.

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Phosphoinositide 3-Kinase and Akt Are Essential for Sonic Hedgehog Signaling von Riobó, Natalia A., Lu, Ke, Ai, Xingbin, Haines, Gwendolyn M., Emerson, Charles P.

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Morpholino-mediated Knockdown of DUX4 Toward Facioscapulohumeral Muscular Dystrophy Therapeutics von Chen, Jennifer CJ, King, Oliver D, Zhang, Yuanfan, Clayton, Nicholas P, Spencer, Carrie, Wentworth, Bruce M, Emerson, Charles P, Wagner, Kathryn R

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SMCHD1 activates the expression of genes required for the expansion of human myoblasts von Wong, Matthew Man-Kin, Hachmer, Sarah, Gardner, Ed, Runfola, Valeria, Arezza, Eric, Megeney, Lynn A, Emerson, Charles P, Gabellini, Davide, Dilworth, F Jeffrey

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SULF1 and SULF2 regulate heparan sulfate-mediated GDNF signaling for esophageal innervation von Ai, Xingbin, Kitazawa, Toshio, Do, Anh-Tri, Kusche-Gullberg, Marion, Labosky, Patricia A, Emerson, Jr, Charles P

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p38 MAPKs - roles in skeletal muscle physiology, disease mechanisms, and as potential therapeutic targets von Brennan, Christopher M, Emerson, Jr, Charles P, Owens, Jane, Christoforou, Nicolas

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Telomere position effect regulates DUX4 in human facioscapulohumeral muscular dystrophy von Stadler, Guido, Rahimov, Fedik, King, Oliver D, Chen, Jennifer C J, Robin, Jerome D, Wagner, Kathryn R, Shay, Jerry W, Emerson, Charles P, Wright, Woodring E

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Flavones provide resistance to DUX4-induced toxicity via an mTor-independent mechanism von Cohen, Justin, Huang, Shushu, Koczwara, Katherine E., Woods, Kristen T., Ho, Vincent, Woodman, Keryn G., Arbiser, Jack L., Daman, Katelyn, Lek, Monkol, Emerson, Charles P., DeSimone, Alec M.

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Increasing intracellular dNTP levels improves prime editing efficiency von Liu, Pengpeng, Ponnienselvan, Karthikeyan, Nyalile, Thomas, Oikemus, Sarah, Joynt, Anya T, Iyer, Sukanya, Kelly, Karen, Guo, Dongsheng, Kyawe, Pyae P, Vanderleeden, Emma, Redick, Sambra D, Huang, Lei, Chen, Zexiang, Lee, Jeong Min, Schiffer, Celia A, Harlan, David M, Wang, Jennifer P, Emerson, Jr, Charles P, Lawson, Nathan D, Watts, Jonathan K, Sontheimer, Erik J, Luban, Jeremy, Wolfe, Scot A

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Impaired mitochondrial oxidative metabolism in skeletal progenitor cells leads to musculoskeletal disintegration von Lin, Chujiao, Yang, Qiyuan, Guo, Dongsheng, Xie, Jun, Yang, Yeon-Suk, Chaugule, Sachin, DeSouza, Ngoc, Oh, Won-Taek, Li, Rui, Chen, Zhihao, John, Aijaz A., Qiu, Qiang, Zhu, Lihua Julie, Greenblatt, Matthew B., Ghosh, Sankar, Li, Shaoguang, Gao, Guangping, Haynes, Cole, Emerson, Charles P., Shim, Jae-Hyuck

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QSulf1 Remodels the 6-O Sulfation States of Cell Surface Heparan Sulfate Proteoglycans to Promote Wnt Signaling von Ai, Xingbin, Do, Anh-Tri, Lozynska, Olga, Kusche-Gullberg, Marion, Lindahl, Ulf, Emerson, Charles P.

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Transcriptional profiling in facioscapulohumeral muscular dystrophy to identify candidate biomarkers von Rahimov, Fedik, King, Oliver D, Leung, Doris G, Bibat, Genila M, Emerson, Charles P, Kunkel, Louis M, Wagner, Kathryn R

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Outcome Measures in Facioscapulohumeral Muscular Dystrophy Clinical Trials von Ghasemi, Mehdi, Emerson, Jr, Charles P, Hayward, Lawrence J

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Pax3 synergizes with Gli2 and Zic1 in transactivating the Myf5 epaxial somite enhancer von Himeda, Charis L., Barro, Marietta V., Emerson, Charles P.

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MYOGENIC REGULATORY FACTORS AND THE SPECIFICATION OF MUSCLE PROGENITORS IN VERTEBRATE EMBRYOS von Pownall, Mary Elizabeth, Gustafsson, Marcus K, Emerson, Charles P

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DUX4 expression activates JNK and p38 MAP kinases in myoblasts von Brennan, Christopher M., Hill, Abby S., St. Andre, Michael, Li, Xianfeng, Madeti, Vijaya, Breitkopf, Susanne, Garren, Seth, Xue, Liang, Gilbert, Tamara, Hadjipanayis, Angela, Monetti, Mara, Emerson, Charles P., Moccia, Robert, Owens, Jane, Christoforou, Nicolas

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Substrate Specificity and Domain Functions of Extracellular Heparan Sulfate 6-O-Endosulfatases, QSulf1 and QSulf2 von Ai, Xingbin, Do, Anh-Tri, Kusche-Gullberg, Marion, Lindahl, Ulf, Lu, Ke, Emerson, Charles P.

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Facioscapulohumeral muscular dystrophy family studies of DUX4 expression: evidence for disease modifiers and a quantitative model of pathogenesis von Jones, Takako Iida, Chen, Jennifer C J, Rahimov, Fedik, Homma, Sachiko, Arashiro, Patricia, Beermann, Mary Lou, King, Oliver D, Miller, Jeffrey B, Kunkel, Louis M, Emerson, Jr, Charles P, Wagner, Kathryn R, Jones, Peter L

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Regulation of Wnt Signaling and Embryo Patterning by an Extracellular Sulfatase von Dhoot, Gurtej K., Gustafsson, Marcus K., Ai, Xingbin, Sun, Weitao, Standiford, David M., Emerson, Charles P.

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iMyoblasts for ex vivo and in vivo investigations of human myogenesis and disease modeling von Guo, Dongsheng, Daman, Katelyn, Chen, Jennifer Jc, Shi, Meng-Jiao, Yan, Jing, Matijasevic, Zdenka, Rickard, Amanda M, Bennett, Monica H, Kiselyov, Alex, Zhou, Haowen, Bang, Anne G, Wagner, Kathryn R, Maehr, René, King, Oliver D, Hayward, Lawrence J, Emerson, Jr, Charles P

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