O42: Development of an anti-sense oligonucleotide therapeutic targeting RhoBTB2-related epileptic encephalopathy von Wheeler, Matthew, Bonner, Devon, Alvarez, Raquel, Emami, Sara, Coca, Richard, Willis, Brandon, Mendez, Hector, Patel, Ruchi, Duong, Kate, Arthur, Jennifer, Karakikes, Ioannis, Bernstein, Jonathan, Porter, Brenda, Knowles, Juliet, Lloyd, Kent, LaRocca, Thomas

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Tuning Piezo ion channels to detect molecular-scale movements relevant for fine touch von Poole, Kate, Herget, Regina, Lapatsina, Liudmila, Ngo, Ha-Duong, Lewin, Gary R.

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A culture-independent nucleic acid diagnostics method for use in the detection and quantification of Burkholderia cepacia complex contamination in aqueous finished pharmaceutical p... von Duong, Huong, Minogue, Elizabeth, Fullbrook, Shannon, Barry, Thomas, Reddington, Kate

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The cooperative international neuromuscular research group Duchenne natural history study: Glucocorticoid treatment preserves clinically meaningful functional milestones and reduce... von Henricson, Erik K., Abresch, R. Ted, Cnaan, Avital, Hu, Fengming, Duong, Tina, Arrieta, Adrienne, Han, Jay, Escolar, Diana M., Florence, Julaine M., Clemens, Paula R., Hoffman, Eric P., McDonald, Craig M.

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Scary Barbie: An Extremely Energetic, Long-duration Tidal Disruption Event Candidate without a Detected Host Galaxy at z = 0.995 von Subrayan, Bhagya M., Milisavljevic, Dan, Chornock, Ryan, Margutti, Raffaella, Alexander, Kate D., Ramakrishnan, Vandana, Duffell, Paul C., Dickinson, Danielle A., Lee, Kyoung-Soo, Giannios, Dimitrios, Lentner, Geoffery, Linvill, Mark, Garretson, Braden, Graham, Matthew J., Stern, Daniel, Brethauer, Daniel, Duong, Tien, Jacobson-Galán, Wynn, LeBaron, Natalie, Matthews, David, Sears, Huei, Venkatraman, Padma

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APOE Christchurch enhances a disease-associated microglial response to plaque but suppresses response to tau pathology von Tran, Kristine M, Kwang, Nellie E, Butler, Claire A, Gomez-Arboledas, Angela, Kawauchi, Shimako, Mar, Cassandra, Chao, Donna, Barahona, Rocio A, Da Cunha, Celia, Tsourmas, Kate I, Shi, Zechuan, Wang, Shuling, Collins, Sherilyn, Walker, Amber, Shi, Kai-Xuan, Alcantara, Joshua A, Neumann, Jonathan, Duong, Duc M, Seyfried, Nicholas T, Tenner, Andrea J, LaFerla, Frank M, Hohsfield, Lindsay A, Swarup, Vivek, MacGregor, Grant R, Green, Kim N

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Attitudes towards COVID‐19 vaccination in patients with inflammatory bowel disease von Duong, Tuan A., Bryant, Robert V., Andrews, Jane M., Lynch, Kate D.

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Revised Hammersmith Scale for spinal muscular atrophy: A SMA specific clinical outcome assessment tool von Ramsey, Danielle, Scoto, Mariacristina, Mayhew, Anna, Main, Marion, Mazzone, Elena S, Montes, Jacqueline, de Sanctis, Roberto, Dunaway Young, Sally, Salazar, Rachel, Glanzman, Allan M, Pasternak, Amy, Quigley, Janet, Mirek, Elizabeth, Duong, Tina, Gee, Richard, Civitello, Matthew, Tennekoon, Gihan, Pane, Marika, Pera, Maria Carmela, Bushby, Kate, Day, John, Darras, Basil T, De Vivo, Darryl, Finkel, Richard, Mercuri, Eugenio, Muntoni, Francesco

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Improvement of Precision in Recombinant Adeno-Associated Virus Infectious Titer Assay with Droplet Digital PCR as an Endpoint Measurement von Duong, Tam, McAllister, James, Eldahan, Khalid, Wang, Jennifer, Onishi, Eric, Shen, Kate, Schrock, Robert, Gu, Bingnan, Wang, Peng

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The cooperative international neuromuscular research group duchenne natural history study-a longitudinal investigation in the era of glucocorticoid therapy: Design of protocol and... von McDonald, Craig M., Henricson, Erik K., Abresch, R. Ted, Han, Jay J., Escolar, Diana M., Florence, Julaine M., Duong, Tina, Arrieta, Adrienne, Clemens, Paula R., Hoffman, Eric P., Cnaan, Avital

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Pretreatment Transcriptional Profiling for Predicting Response to Neoadjuvant Chemoradiotherapy in Rectal Adenocarcinoma von BRETTINGHAM-MOORE, Kate H, DUONG, Cuong P, BUI, Andrew, DARYL LIM JOON, THOMAS, Robert J. S, PHILLIPS, Wayne A, GREENAWALT, Danielle M, HERIOT, Alexander G, ELLUL, Jason, DOW, Christopher A, MURRAY, William K, HICKS, Rodney J, TJANDRA, Joe, CHAO, Michael

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Delphi Consensus Panel on Assessing Clinically Meaningful Treatment Outcomes in Adults Living with Spinal Muscular Atrophy (SMA) (P2-11.007) von Sully, Kate, Chiriboga, Claudia, Duong, Tina, Erbas, Yasemin, Glascock, Jacqueline, Gusset, Nicole, Muni-Lofra, Robert, O’Connell, Colleen, Vázquez-Costa, Juan F., Walter, Maggie C., Guittari, Carol Jean, Cochrane, James, Townson, Louisa D., Kufakwaro, Jason, Marciniak, Anne, Riley, Danielle, Nam, Julian

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Analysis of Plasmodium falciparum diversity in natural infections by deep sequencing von Manske, Magnus, Miotto, Olivo, Campino, Susana, Auburn, Sarah, Almagro-Garcia, Jacob, Maslen, Gareth, O’Brien, Jack, Djimde, Abdoulaye, Doumbo, Ogobara, Zongo, Issaka, Ouedraogo, Jean-Bosco, Michon, Pascal, Mueller, Ivo, Siba, Peter, Nzila, Alexis, Borrmann, Steffen, Kiara, Steven M., Marsh, Kevin, Jiang, Hongying, Su, Xin-Zhuan, Amaratunga, Chanaki, Fairhurst, Rick, Socheat, Duong, Nosten, Francois, Imwong, Mallika, White, Nicholas J., Sanders, Mandy, Anastasi, Elisa, Alcock, Dan, Drury, Eleanor, Oyola, Samuel, Quail, Michael A., Turner, Daniel J., Ruano-Rubio, Valentin, Jyothi, Dushyanth, Amenga-Etego, Lucas, Hubbart, Christina, Jeffreys, Anna, Rowlands, Kate, Sutherland, Colin, Roper, Cally, Mangano, Valentina, Modiano, David, Tan, John C., Ferdig, Michael T., Amambua-Ngwa, Alfred, Conway, David J., Takala-Harrison, Shannon, Plowe, Christopher V., Rayner, Julian C., Rockett, Kirk A., Clark, Taane G., Newbold, Chris I., Berriman, Matthew, MacInnis, Bronwyn, Kwiatkowski, Dominic P.

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Spatially resolved imaging of the inner Fomalhaut disk using JWST/MIRI von Gáspár, András, Wolff, Schuyler Grace, Rieke, George H., Leisenring, Jarron M., Morrison, Jane, Su, Kate Y. L., Ward-Duong, Kimberly, Aguilar, Jonathan, Ygouf, Marie, Beichman, Charles, Llop-Sayson, Jorge, Bryden, Geoffrey

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The nature of lexico-semantic processing deficits in mild cognitive impairment von Duong, Anh, Whitehead, Victor, Hanratty, Kate, Chertkow, Howard

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Muscle Biopsy Findings in Combination With Myositis‐Specific Autoantibodies Aid Prediction of Outcomes in Juvenile Dermatomyositis von Deakin, Claire T., Simou, Stefania, Arnold, Katie A., Tansley, Sarah L., Betteridge, Zoe E., McHugh, Neil J., Varsani, Hemlata, Holton, Janice L., Jacques, Thomas S., Pilkington, Clarissa A., Nistala, Kiran, Wedderburn, Lucy R., Armon, Kate, Ellis‐Gage, Joe, Roper, Holly, Briggs, Vanja, Watts, Joanna, McCann, Liza, Roberts, Ian, Baildam, Eileen, Hanna, Louise, Lloyd, Olivia, Wadeson, Susan, Riley, Phil, McGovern, Ann, Ryder, Clive, Scott, Janis, Thomas, Beverley, Southwood, Taunton, Al‐Abadi, Eslam, Wyatt, Sue, Jackson, Gillian, Amin, Tania, Wood, Mark, VanRooyen, Vanessa, Burton, Deborah, Davidson, Joyce, Gardner‐Medwin, Janet, Martin, Neil, Ferguson, Sue, Waxman, Liz, Browne, Michael, Friswell, Mark, Swift, Alison, Stevenson, Vicky, Wade, Debbie, Sen, Ethan, Smith, Eve, Qiao, Lisa, Watson, Stuart, Duong, Claire, Venning, Helen, Satyapal, Rangaraj, Stretton, Elizabeth, Jordan, Mary, Mosley, Ellen, Frost, Anna, Crate, Lindsay, Warrier, Kishore, Stafford, Stefanie, Hasson, Nathan, Maillard, Sue, Halkon, Elizabeth, Brown, Virginia, Juggins, Audrey, Smith, Sally, Lunt, Sian, Enayat, Elli, Kassoumeri, Laura, Beard, Laura, Almeida, Beverley, Marques, Raquel, Dowle, Stefanie, Papadopoulou, Charis, Suffield, Linda, Al‐Obaidi, Muthana, Lee, Helen, Leach, Sam, Smith, Helen, McMahon, Anne‐Marie, Chisem, Heather, Kingshott, Ruth, Wilkinson, Nick, Inness, Emma, Kendall, Eunice, Mayers, David, Etherton, Ruth, Bailey, Kathryn, Clinch, Jacqui, Fineman, Natalie, Pluess‐Hall, Helen, Vallance, Lindsay, Akeroyd, Louise, Leahy, Alice, Collier, Amy, Cutts, Rebecca, De Graaf, Hans, Davidson, Brian, Hartfree, Sarah, Pratt, Danny

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Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy: A 30-Month Nonrandomized Controlled Open-Label Extension Trial von Mah, Jean K, Clemens, Paula R, Guglieri, Michela, Smith, Edward C, Finkel, Richard S, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M, Webster, Richard, Castro, Diana, Kuntz, Nancy L, McDonald, Craig M, Damsker, Jesse M, Schwartz, Benjamin D, Mengle-Gaw, Laurel J, Jackowski, Stefan, Stimpson, Georgia, Ridout, Deborah A, Ayyar-Gupta, Vandana, Baranello, Giovanni, Manzur, Adnan Y, Muntoni, Francesco, Gordish-Dressman, Heather, Leinonen, Mika, Ward, Leanne M, Hoffman, Eric P, Dang, Utkarsh J

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THE PECULIAR DEBRIS DISK OF HD 111520 AS RESOLVED BY THE GEMINI PLANET IMAGER von Draper, Zachary H., Duchêne, Gaspard, Millar-Blanchaer, Maxwell A., Matthews, Brenda C., Wang, Jason J., Kalas, Paul, Graham, James R., Padgett, Deborah, Ammons, S. Mark, Bulger, Joanna, Chen, Christine, Chilcote, Jeffrey K., Doyon, René, Fitzgerald, Michael P., Follette, Kate B., Gerard, Benjamin, Greenbaum, Alexandra Z., Hibon, Pascale, Hinkley, Sasha, Macintosh, Bruce, Ingraham, Patrick, Lafrenière, David, Marchis, Franck, Marois, Christian, Nielsen, Eric L., Oppenheimer, Rebecca, Patel, Rahul, Patience, Jenny, Perrin, Marshall, Pueyo, Laurent, Rajan, Abhijith, Rameau, Julien, Sivaramakrishnan, Anand, Vega, David, Ward-Duong, Kimberly, Wolff, Schuyler G.

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Association Between Dietary Intake and Function in Amyotrophic Lateral Sclerosis von Nieves, Jeri W, Gennings, Chris, Factor-Litvak, Pam, Hupf, Jonathan, Singleton, Jessica, Sharf, Valerie, Oskarsson, Björn, Fernandes Filho, J. Americo M, Sorenson, Eric J, D’Amico, Emanuele, Goetz, Ray, Mitsumoto, Hiroshi

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Successful introgression of wMel Wolbachia into Aedes aegypti populations in Fiji, Vanuatu and Kiribati von Simmons, Cameron P, Donald, Wesley, Tagavi, Lekon, Tarivonda, Len, Quai, Timothy, Tavoa, Raynelyn, Noran, Tebikau, Manikaoti, Erirau, Kareaua, Lavinia, Abwai, Tabomoa Tinte, Chand, Dip, Rama, Vineshwaran, Deo, Vimal, Deo, Kharishma Karti, Tavuii, Aminiasi, Valentine, Wame, Prasad, Ravi, Seru, Eremasi, Naituku, Leikitah, Ratu, Anaseini, Hesketh, Mark, Kenny, Nichola, Beebe, Sarah C, Goundar, Anjali A, McCaw, Andrew, Buntine, Molly, Green, Ben, Frossard, Tibor, Gilles, Jeremie R L, Joubert, D Albert, Wilson, Geoff, Duong, Le Quyen, Bouvier, Jean B, Stanford, Darren, Forder, Carolyn, Duyvestyn, Johanna M, Pacidônio, Etiene C, Flores, Heather A, Wittmeier, Natalie, Retzki, Kate, Ryan, Peter A, Denton, Jai A, Smithyman, Ruth, Tanamas, Stephanie K, Kyrylos, Peter, Dong, Yi, Khalid, Anam, Hodgson, Lauren, Anders, Katherine L, O'Neill, Scott L

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