Properties of the Narrative Scoring Scheme Using Narrative Retells in Young School-Age Children von Heilmann, John, Miller, Jon F, Nockerts, Ann, Dunaway, Claudia

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Six-minute walk test is reliable and valid in spinal muscular atrophy von Dunaway Young, Sally, Montes, Jacqueline, Kramer, Samantha S., Marra, Jonathan, Salazar, Rachel, Cruz, Rosangel, Chiriboga, Claudia A., Garber, Carol Ewing, De Vivo, Darryl C.

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Altered dopaminergic pathways and therapeutic effects of intranasal dopamine in two distinct mouse models of autism von Chao, Owen Y, Pathak, Salil S, Zhang, Hao, Dunaway, Nathan, Li, Jay-Shake, Mattern, Claudia, Nikolaus, Susanne, Huston, Joseph P, Yang, Yi-Mei

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HDAC1 inhibition promotes pathogenic Th17 cell expansion in the context of high salt von Edell, Claudia J., Molina, Patrick A., Dunaway, Luke, Pollock, Jennifer S.

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Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy von Finkel, Richard S, Mercuri, Eugenio, Darras, Basil T, Connolly, Anne M, Kuntz, Nancy L, Kirschner, Janbernd, Chiriboga, Claudia A, Saito, Kayoko, Servais, Laurent, Tizzano, Eduardo, Topaloglu, Haluk, Tulinius, Már, Montes, Jacqueline, Glanzman, Allan M, Bishop, Kathie, Zhong, Z. John, Gheuens, Sarah, Bennett, C. Frank, Schneider, Eugene, Farwell, Wildon, De Vivo, Darryl C

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Endothelial histone deacetylase 1 activity impairs kidney microvascular NO signaling in rats fed a high‐salt diet von Dunaway, Luke S., Cook, Anthony K., Kellum, Cailin E., Edell, Claudia, Botta, Davide, Molina, Patrick A., Sedaka, Randee S., d'Uscio, Livius V., Katusic, Zvonimir S., Pollock, David M., Inscho, Edward W., Pollock, Jennifer S.

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Lack of effect on ambulation of dalfampridine-ER (4-AP) treatment in adult SMA patients von Chiriboga, Claudia A., Marra, Jonathan, LaMarca, Nicole M., Young, Sally Dunaway, Weimer, Louis H., Levin, Bruce, McCabe, Brian

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Divide and conquer: two stem cell populations in squamous epithelia, reserves and the active duty forces von Dunaway, Spencer, Rothaus, Alexandra, Zhang, Yuhang, Luisa Kadekaro, Ana, Andl, Thomas, Andl, Claudia D.

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Safety and efficacy of leriglitazone for preventing disease progression in men with adrenomyeloneuropathy (ADVANCE): a randomised, double-blind, multi-centre, placebo-controlled ph... von Köhler, Wolfgang, Engelen, Marc, Eichler, Florian, Lachmann, Robin, Fatemi, Ali, Sampson, Jacinda, Salsano, Ettore, Gamez, Josep, Molnar, Maria Judit, Pascual, Sílvia, Rovira, Maria, Vilà, Anna, Pina, Guillem, Martín-Ugarte, Itziar, Mantilla, Adriana, Pizcueta, Pilar, Rodríguez-Pascau, Laura, Traver, Estefania, Vilalta, Anna, Pascual, María, Martinell, Marc, Meya, Uwe, Mochel, Fanny, Mc Govern, Eavan, Yazbeck, Elise, Barbier, Magali, Luton, Marie-Pierre, Pousset, Françoise, Hogrel, Jean-Yves, Adanyeguh, Isaac, Then Bergh, Florian, Bergner, Caroline, Unterlauft, Astrid, Roicke, Hannes, Hoffmann, Karl-Titus, Scherlach, Cordula, Kalb, Andrea, Meilick, Bianca, Reuschel, Mandy, Fenu, Silvia, Mauro, Elena, Murphy, Elaine, Krishna, Gauri, Beyene, Tiggy, Sierra, Alba, Quiñoa, Sara, Belen Canovas, Anna, Grosz, Zoltan, Györgyi, Báthori, van de Stadt, S.I., Huffnagel, I.C., van Ballegoij, W.J.C., Voermans, M.M.C., Seyedsadjadi, Reza, Corre, Camille, Godbole, Neha, Grant, Natalie Rose, Brito Pires, Claudia Maria, Trovato, Melissa, Yeh, Nancy, Goodman, Jordan, Keller, Jennifer, Joseph, Chris, Van Haren, Keith, Sakamuri, Sarada, Duong, Tina, Perrone, Lila, Tran, Stephanie, Dunaway Young, Sally, Hashmi, Syed

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Bulbar function in spinal muscular atrophy (SMA): State of art and new challenges. 21st July 2023, Rome, Italy von McGrattan, Katlyn, Cerchiari, Antonella, Conway, Eleanor, Berti, Beatrice, Finkel, Richard, Muntoni, Francesco, Mercuri, Eugenio, Fanelli, Lavinia, Coratti, Giorgia, Sansone, Valeria, Albamonte, Emilio, Trucco, Federica, Latini, Sofia, Bertini, Enrico, d'Amico, Adele, Doglio, Luca, Stimpson, Georgia, Baranello, Giovanni, Scoto, Mariacristina, Rohwer, Annemarie, Edel, Lisa, Lofra, Robert Muni, Bettolo, Chiara Marini, Young, Sally Dunaway, Day, John, Duong, Tina, Darras, Basil, Pasternak, Amy, Montes, Jacqueline, Rodriguez-Torres, Ralph, Chiriboga, Claudia A., Hirano, Michio, Civitello, Matthew, Cunningham, Zarazuela Zolkipli, Brandsema, John, Mayer, Hank, Glanzmann, Allan, Karagiannis, Joannis, Baldinetti, Francesca, Khader, Leila, Costa, Patrizia, Lovato, Valeria, Rastelletti, Irene

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Leg muscle function and fatigue during walking in spinal muscular atrophy type 3 von Montes, Jacqueline, Dunaway, Sally, Garber, Carol Ewing, Chiriboga, Claudia A., De Vivo, Darryl C., Rao, Ashwini K.

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Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy von Mercuri, Eugenio, Darras, Basil T, Chiriboga, Claudia A, Day, John W, Campbell, Craig, Connolly, Anne M, Iannaccone, Susan T, Kirschner, Janbernd, Kuntz, Nancy L, Saito, Kayoko, Shieh, Perry B, Tulinius, Már, Mazzone, Elena S, Montes, Jacqueline, Bishop, Kathie M, Yang, Qingqing, Foster, Richard, Gheuens, Sarah, Bennett, C. Frank, Farwell, Wildon, Schneider, Eugene, De Vivo, Darryl C, Finkel, Richard S

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Quantitative Evaluation of Lower Extremity Joint Contractures in Spinal Muscular Atrophy: Implications for Motor Function von Salazar, Rachel, Montes, Jacqueline, Dunaway Young, Sally, McDermott, Michael P, Martens, William, Pasternak, Amy, Quigley, Janet, Mirek, Elizabeth, Glanzman, Allan M, Civitello, Matt, Gee, Richard, Duong, Tina, Mazzone, Elena S, Main, Marion, Mayhew, Anna, Ramsey, Danielle, Muni Lofra, Robert, Coratti, Giorgia, Fanelli, Lavinia, De Sanctis, Roberto, Forcina, Nicola, Chiriboga, Claudia, Darras, Basil T, Tennekoon, Gihan I, Scoto, Mariacristina, Day, John W, Finkel, Richard, Muntoni, Francesco, Mercuri, Eugenio, De Vivo, Darryl C

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Spinal muscular atrophy functional composite score: A functional measure in spinal muscular atrophy von Montes, Jacqueline, Glanzman, Allan M., Mazzone, Elena S., Martens, William B., Dunaway, Sally, Pasternak, Amy, Riley, Susan O, Quigley, Janet, Pandya, Shree, De Vivo, Darryl C, Kaufmann, Petra, Chiriboga, Claudia A., Finkel, Richard S., Tennekoon, Gihan I., Darras, Basil T., Pane, Marika, Mercuri, Eugenio, Mcdermott, Michael P.

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Weakness and Fatigue in Diverse Neuromuscular Diseases von Montes, Jacqueline, Blumenschine, Michelle, Dunaway, Sally, Alter, Aliza S., Engelstad, Kristin, Rao, Ashwini K., Chiriboga, Claudia A., Sproule, Douglas M., Vivo, Darryl C. De

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Divide and conquer: two stem cell populations in squamous epithelia, reserves and the active duty forces von Spencer Dunaway, Alexandra Rothaus, Yuhang Zhang, Ana Luisa Kadekaro, Thomas Andl, Claudia D. Andl

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Six-Minute Walk Test Is Reliable and Valid in Spinal Muscular Atrophy (P7.075) von Dunaway, Sally, Montes, Jacqueline, Kramer, Samantha, Marra, Jonathan, Salazar, Rachel, Chiriboga, Claudia, Garber, Carol, De Vivo, Darryl

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Six-minute walk test is reliable and valid in spinal muscular atrophy: 6MWT in SMA von Dunaway Young, Sally, Montes, Jacqueline, Kramer, Samantha S., Marra, Jonathan, Salazar, Rachel, Cruz, Rosangel, Chiriboga, Claudia A., Garber, Carol Ewing, De Vivo, Darryl C.

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Rasch analysis of the Pediatric Evaluation of Disability Inventory-computer adaptive test (PEDI-CAT) item bank for children and young adults with spinal muscular atrophy von Pasternak, Amy, Sideridis, Georgios, Fragala-Pinkham, Maria, Glanzman, Allan M., Montes, Jacqueline, Dunaway, Sally, Salazar, Rachel, Quigley, Janet, Pandya, Shree, O'Riley, Susan, Greenwood, Jonathan, Chiriboga, Claudia, Finkel, Richard, Tennekoon, Gihan, Martens, William B., McDermott, Michael P., Fournier, Heather (Szelag), Madabusi, Lavanya, Harrington, Timothy, Cruz, Rosangel E., LaMarca, Nicole M., Videon, Nancy M., Vivo, Darryl C. De, Darras, Basil T.

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Sensory-Motor Circuit Dysfunction In Adult Ambulatory SMA Type 3 Patients (P4.087) von Chiriboga, Claudia, Weimer, Louis, Marra, Jonathan, Holuba LaMarca, Nicole, Montes, Jacqueline, Dunaway, Sally, Mentis, George, McCabe, Brian, De Vivo, Darryl

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