Catalytic domain modification and viral gene delivery of activated factor VII confers hemostasis at reduced expression levels and vector doses in vivo von Margaritis, Paris, Roy, Elise, Faella, Armida, Downey, Harre D., Ivanciu, Lacramioara, Pavani, Giulia, Zhou, Shangzhen, Bunte, Ralph M., High, Katherine A.

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Host and Vector-dependent Effects on the Risk of Germline Transmission of AAV Vectors von Favaro, Patricia, Downey, Harre D, Zhou, J Shangzhen, Wright, J Fraser, Hauck, Bernd, Mingozzi, Federico, High, Katherine A, Arruda, Valder R

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Proteasome Inhibitors Decrease AAV2 Capsid derived Peptide Epitope Presentation on MHC Class I Following Transduction von Finn, Jonathan D, Hui, Daniel, Downey, Harre D, Dunn, Danielle, Pien, Gary C, Mingozzi, Federico, Zhou, Shangzhen, High, Katherine A

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In Vitro and In Vivo Characterization of a Murine Model of Suppressed Intrinsic Pathway Using a FX Variant: FXRoma von Roy, Elise, Margaritis, Paris, Downey, Harre D., High, Katherine A.

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The Development of Novel Hemostatic Bypassing Molecules von Camire, Rodney M., Bunce, Matthew, Ivanciu, Lacramioara, Toso, Raffaella, Downey, Harre D., Liu, Jian-Hua, Arruda, Valder R.

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Safety of Recombinant Adeno-Associated Viral Vectors in a Large Animal Model von Favaro, Patricia, Downey, Harre D., Mingozzi, Federico, Wright, Fraser, Hauck, Bernd, High, Katherine A., Arruda, Valder R.

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