Hematopoietic stem cell transplantation gene therapy for hemophilia a using non-genotoxic ANTI-CD117 immunotoxin conditioning von Russell, A.L, Prince, C, Zoine, J, Sheilds, J, Lytle, A, Spencer, H, Chandrakasan, S, Doering, C.B

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EVALUATION OF A HIGH-EXPRESSION FVIII TRANSGENE AND LENTIVIRAL VECTOR-TRANSDUCED AUTOLOGOUS CD34+ HEMATOPOIETIC STEM CELLS IN A PHASE 1 CLINICAL TRIAL OF GENE THERAPY FOR HEMOPHILI... von Srivastava, A., Abraham, A., Aboobacker, F., Singh, G., Geevar, T., Kulkarni, U., Selvarajan, S., Korula, A., Dave, R., A M, M., Velayudhan, S., Nair, S., Denning, G., Lollar, J., Doering, C.B., Spencer, H.T.

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Generation of an optimized lentiviral vector encoding a high-expression factor VIII transgene for gene therapy of hemophilia A von Johnston, J M, Denning, G, Doering, C B, Spencer, H T

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Expanding the ortholog approach for hemophilia treatment complicated by factor VIII inhibitors von Zakas, P. M., Vanijcharoenkarn, K., Markovitz, R. C., Meeks, S. L., Doering, C. B.

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High-throughput screening identifies compounds that enhance lentiviral transduction von Johnston, J M, Denning, G, Moot, R, Whitehead, D, Shields, J, Le Doux, J M, Doering, C B, Spencer, H T

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Identifying the risk of obstructive sleep apnea in metabolic syndrome patients: Diagnostic accuracy of the Berlin Questionnaire von Cepeda, Felipe X, Virmondes, Leslie, Rodrigues, Sara, Dutra-Marques, Akothirene C B, Toschi-Dias, Edgar, Ferreira-Camargo, Fernanda C, Hussid, Maria Fernanda, Rondon, Maria Urbana Pb, Alves, Maria Janieire N N, Trombetta, Ivani C

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Deconstructing pathological tau by biological process in early stages of Alzheimer disease: a method for quantifying tau spatial spread in neuroimagingResearch in context von Stephanie Doering, Austin McCullough, Brian A. Gordon, Charles D. Chen, Nicole McKay, Diana Hobbs, Sarah Keefe, Shaney Flores, Jalen Scott, Hunter Smith, Stephen Jarman, Kelley Jackson, Russ C. Hornbeck, Beau M. Ances, Chengjie Xiong, Andrew J. Aschenbrenner, Jason Hassenstab, Carlos Cruchaga, Alisha Daniels, Randall J. Bateman, John C. Morris, Tammie L.S. Benzinger, James M. Noble, Gregory S. Day, Neill R. Graff-Radford, Jonathan Voglein, Johannes Levin, Ricardo F. Allegri, Patricio Chrem Mendez, Ezequiel Surace, Sarah B. Berman, Snezana Ikonomovic, Neelesh K. Nadkarni, Francisco Lopera, Laura Ramirez, David Aguillon, Yudy Leon, Claudia Ramos, Diana Alzate, Ana Baena, Natalia Londono, Sonia Moreno, Mathias Jucker, Christoph Laske, Elke Kuder-Buletta, Susanne Graber-Sultan, Oliver Preische, Anna Hofmann, Takeshi Ikeuchi, Kensaku Kasuga, Yoshiki Niimi, Kenji Ishii, Michio Senda, Raquel Sanchez-Valle, Pedro Rosa-Neto, Nick C. Fox, Dave Cash, Jae-Hong Lee, Jee Hoon Roh, Stephen Salloway, Meghan C. Riddle, William Menard, Courtney Bodge, Mustafa Surti, Leonel Tadao Takada, Martin Farlow, Jasmeer P. Chhatwal, V.J. Sanchez-Gonzalez, Maribel Orozco-Barajas, Alison M. Goate, Alan E. Renton, Bianca T. Esposito, Celeste M. Karch, Jacob Marsh, Carlos Cruchaga, Victoria Fernanadez, Brian A. Gordon, Anne M. Fagan, Gina Jerome, Elizabeth Herries, Jorge Llibre-Guerra, Allan I. Levey, Erik C.B. Johnson, Nicholas T. Seyfried, Peter R. Schofield, William S. Brooks, Jacob A. Bechara, Randall Bateman, Eric McDade, Jason Hassenstab, Richard J. Perrin, Erin E. Franklin, Tammie Benzinger, Allison Chen, Charles Chen, Shaney Flores, Nelly Friedrichsen, Brian Gordon, Nancy Hantler, Russ Hornbeck

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