B-Cell Depletion is Protective Against Anti-AAV Capsid Immune Response: A Human Subject Case Study von Corti, M, Elder, Me, Falk, Dj, Lawson, L, Smith, Bk, Nayak, S, Conlon, Tj, Clément, N, Erger, K, Lavassani, E, Green, M, Doerfler, Pa, Herzog, Rw, Byrne, Bj

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Copackaged AAV9 Vectors Promote Simultaneous Immune Tolerance and Phenotypic Correction of Pompe Disease von Doerfler, Phillip A, Todd, Adrian G, Clément, Nathalie, Falk, Darin J, Nayak, Sushrusha, Herzog, Roland W, Byrne, Barry J

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Immune responses and hypercoagulation in ERT for Pompe disease are mutation and rhGAA dose dependent von Nayak, Sushrusha, Doerfler, Phillip A, Porvasnik, Stacy L, Cloutier, Denise D, Khanna, Richie, Valenzano, Ken J, Herzog, Roland W, Byrne, Barry J

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BAFF blockade prevents anti-drug antibody formation in a mouse model of Pompe disease von Doerfler, Phillip A, Nayak, Sushrusha, Herzog, Roland W, Morel, Laurence, Byrne, Barry J

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Targeted approaches to induce immune tolerance for Pompe disease therapy von Doerfler, Phillip A, Nayak, Sushrusha, Corti, Manuela, Morel, Laurence, Herzog, Roland W, Byrne, Barry J

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Pharmacological chaperones prevent the precipitation of rhGAA by anti-GM antibodies during enzyme replacement therapy von Doerfler, PA, Kelley, JS, Nayak, S, Lawson, LA, Byrne, BJ

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B & T Cell Immunomodulation Attenuates Anaphylaxis in a Novel Mouse Model of Pompe Disease von Doerfler, PA, Nayak, S, Herzog, RW, Byrne, BJ

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Chromothripsis as an on-target consequence of CRISPR-Cas9 genome editing von Leibowitz, ML, Papathanasiou, S, Doerfler, PA, Blaine, LJ, Sun, L, Yao, Y, Zhang, CZ, Weiss, MJ, Pellman, D

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Epigenetic and genotype-specific effects on the stability of de novo imposed methylation patterns in transgenic mice von Schumacher, A, Koetsier, P A, Hertz, J, Doerfler, W

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Stability of transgene methylation patterns in mice : position effects, strain specificity and cellular mosaicism von KOETSIER, P. A, MANGEL, L, SCHMITZ, B, DOERFLER, W

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A simple device to prevent contamination during spin-column gel filtration von KOETSIER, P. A, DOERFLER, W

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Software package to collect and process radiogas chromatographic data von Campbell, I. M, Doerfler, D. L, Donahey, S. A, Kadlec, R, McGandy, E. L, Naworal, J. D, Nulton, C. P, Venza-Raczka, M, Wimberly, F

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