Correction of Neurological Disease of Mucopolysaccharidosis IIIB in Adult Mice by rAAV9 Trans-Blood–Brain Barrier Gene Delivery von Fu, Haiyan, DiRosario, Julianne, Killedar, Smruti, Zaraspe, Kimberly, McCarty, Douglas M

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Ribonuclease 7 is a potent antimicrobial peptide within the human urinary tract von Spencer, John D., Schwaderer, Andrew L., DiRosario, Julianne D., McHugh, Kirk M., McGillivary, Glen, Justice, Sheryl S., Carpenter, Ashley R., Baker, Peter B., Harder, Jürgen, Hains, David S.

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Human alpha defensin 5 expression in the human kidney and urinary tract von Spencer, John David, Hains, David S, Porter, Edith, Bevins, Charles L, DiRosario, Julianne, Becknell, Brian, Wang, Huanyu, Schwaderer, Andrew L

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Innate and adaptive immune activation in the brain of MPS IIIB mouse model von DiRosario, Julianne, Divers, Erin, Wang, Chuansong, Etter, Jonathan, Charrier, Alyssa, Jukkola, Peter, Auer, Herbert, Best, Victoria, Newsom, David L., McCarty, Douglas M., Fu, Haiyan

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Mucopolysaccharidosis IIIB, a lysosomal storage disease, triggers a pathogenic CNS autoimmune response von Killedar, Smruti, Dirosario, Julianne, Divers, Erin, Popovich, Phillip G, McCarty, Douglas M, Fu, Haiyan

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Restoration of central nervous system α-N-acetylglucosaminidase activity and therapeutic benefits in mucopolysaccharidosis IIIB mice by a single intracisternal recombinant adeno-as... von Fu, Haiyan, DiRosario, Julianne, Kang, Lu, Muenzer, Joseph, McCarty, Douglas M.

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Mucopolysaccharidosis IIIB, a lysosomal storage disease, triggers a pathogenic neuroautoimmune response (93.19) von Fu, Haiyan, Killedar, Smruti, DiRosario, Julianne, Popovich, Phillip, McCarty, Douglas

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Correction of neurological disease of Mucopolysaccharidosis IIIB in adult mice by rAAV9 trans-blood-brain-barrier gene delivery von Fu, Haiyan, DiRosario, Julianne, Killedar, Smruti, Zaraspe, Kimberly, McCarty, Douglas

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Restoration of central nervous system [alpha]-N-acetylglucosaminidase activity and therapeutic benefits in mucopolysaccharidosis IIIB mice by a single intracisternal recombinant ad... von Fu, Haiyan, DiRosario, Julianne, Kang, Lu, Muenzer, Joseph, McCarty, Douglas M

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Chronic autoimmune activation in patients with mucopolysaccharidosis III (93.22) von Fu, Haiyan, Killedar, Smruti, al-Dahhak, Roula, Rankin, Chelsea, Wu, Yee-Ling, Zhou, Bi, Yu, Chack-Yung, DiRosario, Julianne, McCarty, Douglas

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Differential distribution of heparan sulfate glycoforms and elevated expression of heparan sulfate biosynthetic enzyme genes in the brain of mucopolysaccharidosis IIIB mice von McCarty, Douglas M., DiRosario, Julianne, Gulaid, Kadra, Killedar, Smruti, Oosterhof, Arie, van Kuppevelt, Toin H., Martin, Paul T., Fu, Haiyan

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494. Optimizing the Mannitol-Facilitated CNS Entry of Peripherally-Delivered AAV2 Vector von Fu, Haiyan, DiRosario, Julianne, McCarty, Douglas M.

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