Strategy to assess the effect of duvoglustat co-administered with alglucosidase alfa infusion on the immune response to enzyme replacement therapy for Pompe disease von Benjamin, Elfrida R., Wu, Xiaoyang, Valle, M. Cecilia Della, Sjoberg, Eric, Sitaraman, Sheela, Stevens, Anthony, Gomez, Nestor, Katz, Evan, Pruthi, Farhana, Kelley, Jeffry S., Wustman, Brandon, Valenzano, Kenneth J., Byrne, Barry J., Barlow, Carrolee, Lockhart, David J.

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A pharmacogenetic analysis of Fabry patient responses to pharmacological chaperone treatment with AT1001 (migalastat hydrochloride) von Benjamin, Elfrida, Wu, Xiaoyang, Della Valle, M. Cecilia, Katz, Evan, Schiffmann, Raphael, Castelli, Jeffrey P., Greene, Douglas S., Adera, Mathews, Boudes, Pol, Lockhart, David J., Valenzano, Kenneth J.

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Blood biomarkers recommended for diagnosing and monitoring IgG4-related disease. Considerations from the ERN ReCONNET and collaborating partners von Iaccarino, Luca, Talarico, Rosaria, Bozzalla-Cassione, Emanuele, Burmester, Gerd R, Culver, Emma L, Doria, Andrea, Ebbo, Mikael, van Hagen, P Martin, Hachulla, Eric, van Laar, Jan A M, Lanzillotta, Marco, Martinez-Valle, Fernando, Montecucco, Carlomaurizio, Monti, Sara, Nalli, Cecilia, Schleinitz, Nicolas, Tincani, Angela, Della-Torre, Emanuel, Alexander, Tobias

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EVIDENCE FOR TYPE Ia SUPERNOVA DIVERSITY FROM ULTRAVIOLET OBSERVATIONS WITH THE HUBBLE SPACE TELESCOPE von XIAOFENG WANG, LIFAN WANG, BAADE, Dietrich, BARRIS, Brian J, BENETTI, Stefano, BOUCHET, Patrice, BURROWS, Adam S, CANAL, Ramon, CAPPELLARO, Enrico, CARLBERG, Raymond G, DI CARLO, Elisa, CHALLIS, Peter J, FILIPPENKO, Alexei V, CROTTS, Arlin P. S, DANZIGER, John I, DELLA VALLE, Massimo, FINK, Michael, FOLEY, Ryan J, FRANSSON, Claes, GAL-YAM, Avishay, GARNAVICH, Peter M, GERARDY, Chris L, GOLDHABER, Gerson, BARON, Eddie, HAMUY, Mario, HILLEBRANDT, Wolfgang, HÖFLICH, Peter, HOLLAND, Stephen T, HOLZ, Daniel E, HUGHES, John P, JEFFERY, David J, JHA, Saurabh W, KASEN, Dan, KHOKHLOV, Alexei M, KROMER, Markus, KIRSHNER, Robert P, KNOP, Robert A, KOZMA, Cecilia, KRISCIUNAS, Kevin, LEE, Brian C, LEIBUNDGUT, Bruno, LENTZ, Eric J, LEONARD, Douglas C, LEWIN, Walter H. G, WEIDONG LI, JACK, Dennis, LIVIO, Mario, LUNDQVIST, Peter, MAOZ, Dan, MATHESON, Thomas, MAZZALI, Paolo A, MEIKLE, Peter, MIKNAITIS, Gajus, MILNE, Peter A, MOCHNACKI, Stefan W, NOMOTO, Ken'ichi, TIANMENG ZHANG, ALDERING, Greg, ANTILOGUS, Pierre, DAVID ARNETT, W

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Identification of red flags for IgG4-related disease: an international European Reference Network for Rare Connective Tissue Diseases framework von Della-Torre, Emanuel, Talarico, Rosaria, Ballarin, Jose, Bozzalla-Cassione, Emanuele, Cardamone, Chiara, Cigolini, Cosimo, Ferro, Francesco, Fonseca, Tomas, Fragoulis, George E, Galetti, Ilaria, Gerosa, Maria, Hernández-Rodríguez, José, Lanzillotta, Marco, Marinello, Diana, Martin, Thierry, Martinez-Valle, Fernando, Maślińska, Maria, Moretti, Michele, Mosca, Marta, Müller-Ladner, Ulf, Nalli, Cecilia, Orsolini, Giovanni, Pamfil, Cristina, Perez-Garcia, Guillermo, Priori, Roberta, Quattrocchio, Giacomo, Ramming, Andreas, Regola, Francesca, Romão, Vasco C, Silva, Augusto, van Laar, Jan A M, Vicente-Edo, Maria Jose, Vinker, Shlomo, Alexander, Tobias

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Ageing of patients on chronic dialysis: Effects on mortality—A 12-year study von Tazza, Luigi, Di Napoli, Anteo, Bossola, Maurizio, Valle, Sabrina, Pezzotti, Patrizio, Luciani, Giovanna, Di Lallo, Domenico

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Survey of determinants and effects of timing of referral to a nephrologist: the patient's point of view von Di Napoli, Anteo, Valle, Sabrina, d'Adamo, Gianna, Pezzotti, Patrizio, Chicca, Serena, Pignocco, Marco, Spinelli, Cosimo, Di Giulio, Salvatore, Di Lallo, Domenico

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Relationship between structure and neutralizing activity of rabbit tetanus antibodies elicited by acellular and whole-cell pertussis DTP vaccines von Dokmetjian, José, Valle, Cecilia Della, Lavigne, Victoria, Eriksson, Patricia V., Manghi, Marcela A.

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Evidence for Type Ia Supernova Diversity from Ultraviolet Observations with the Hubble Space Telescope von Wang, Xiaofeng, Wang, Lifan, Filippenko, Alexei V, Baron, Eddie, Kromer, Markus, Dennis, Jack, Zhang, Tianmeng, Aldering, Greg, Antilogus, Pierre, Arnett, David, Baade, Dietrich, Barris, Brian J, Benetti, Stefano, Bouchet, Patrice, Burrows, Adam S, Canal, Ramon, Cappellaro, Enrico, Carlberg, Raymond, Elisa di Carlo, Challis, Peter, Crotts, Arlin, Danziger, John I, Massimo Della Valle, Fink, Michael, Foley, Ryan J, Fransson, Claes, Gal-Yam, Avishay, Garnavich, Peter, Gerardy, Chris L, Goldhaber, Gerson, Hamuy, Mario, Hillebrandt, Wolfgang, Hoeflich, Peter A, Holland, Stephen T, Holz, Daniel E, Hughes, John P, Jeffery, David J, Jha, Saurabh W, Kasen, Dan, Khokhlov, Alexei M, Kirshner, Robert P, Knop, Robert, Kozma, Cecilia, Krisciunas, Kevin, Lee, Brian C, Leibundgut, Bruno, Lentz, Eric J, Leonard, Douglas C, Lewin, Walter H G, Li, Weidong, Livio, Mario, Lundqvist, Peter, Maoz, Dan, Matheson, Thomas, Mazzali, Paolo, Meikle, Peter, Miknaitis, Gajus, Milne, Peter, Mochnacki, Stefan, Nomoto, Ken'Ichi, Nugent, Peter E, Oran, Elaine, Panagia, Nino, Perlmutter, Saul, Phillips, Mark M, Pinto, Philip, Poznanski, Dovi, Pritchet, Christopher J, Reinecke, Martin, Riess, Adam, Ruiz-Lapuente, Pilar, Scalzo, Richard, Schlegel, Eric M, Schmidt, Brian, Siegrist, James, Soderberg, Alicia M, Sollerman, Jesper, Sonneborn, George, Spadafora, Anthony, Spyromilio, Jason, Sramek, Richard A, Starrfield, Sumner G, Strolger, Louis G, Suntzeff, Nicholas B, Rollin, Thomas, Tonry, John L, Tornambe, Amedeo, Truran, James W, Turatto, Massimo, Turner, Michael, Van Dyk, Schuyler D, Weiler, Kurt, Wheeler, J Craig, Wood-Vasey, Michael, Woosley, Stan, Yamaoka, Hitoshi

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