Evaluation of TCR Gene Editing Achieved by TALENs, CRISPR/Cas9, and megaTAL Nucleases von Osborn, Mark J, Webber, Beau R, Knipping, Friederike, Lonetree, Cara-lin, Tennis, Nicole, DeFeo, Anthony P, McElroy, Amber N, Starker, Colby G, Lee, Catherine, Merkel, Sarah, Lund, Troy C, Kelly-Spratt, Karen S, Jensen, Michael C, Voytas, Daniel F, von Kalle, Christof, Schmidt, Manfred, Gabriel, Richard, Hippen, Keli L, Miller, Jeffrey S, Scharenberg, Andrew M, Tolar, Jakub, Blazar, Bruce R

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CRISPR/Cas9-based genetic correction for recessive dystrophic epidermolysis bullosa von Webber, Beau R, Osborn, Mark J, McElroy, Amber N, Twaroski, Kirk, Lonetree, Cara-lin, DeFeo, Anthony P, Xia, Lily, Eide, Cindy, Lees, Christopher J, McElmurry, Ron T, Riddle, Megan J, Kim, Chong Jai, Patel, Dharmeshkumar D, Blazar, Bruce R, Tolar, Jakub

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TALEN-based Gene Correction for Epidermolysis Bullosa von Osborn, Mark J, Starker, Colby G, McElroy, Amber N, Webber, Beau R, Riddle, Megan J, Xia, Lily, DeFeo, Anthony P, Gabriel, Richard, Schmidt, Manfred, Von Kalle, Christof, Carlson, Daniel F, Maeder, Morgan L, Joung, J Keith, Wagner, John E, Voytas, Daniel F, Blazar, Bruce R, Tolar, Jakub

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Synthetic Zinc Finger Nuclease Design and Rapid Assembly von OSBORN, Mark J, DEFEO, Anthony P, BLAZAR, Bruce R, TOLAR, Jakub

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Fanconi anemia gene editing by the CRISPR/Cas9 system von Osborn, Mark J, Gabriel, Richard, Webber, Beau R, DeFeo, Anthony P, McElroy, Amber N, Jarjour, Jordan, Starker, Colby G, Wagner, John E, Joung, J Keith, Voytas, Daniel F, von Kalle, Christof, Schmidt, Manfred, Blazar, Bruce R, Tolar, Jakub

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CRISPR/Cas9-Mediated Correction of the FANCD1 Gene in Primary Patient Cells von Skvarova Kramarzova, Karolina, Osborn, Mark J, Webber, Beau R, DeFeo, Anthony P, McElroy, Amber N, Kim, Chong Jai, Tolar, Jakub

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Correction of Fanconi Anemia Mutations Using Digital Genome Engineering von Sipe, Christopher J, Kluesner, Mitchell G, Bingea, Samuel P, Lahr, Walker S, Andrew, Aneesha A, Wang, Minjing, DeFeo, Anthony P, Hinkel, Timothy L, Laoharawee, Kanut, Wagner, John E, MacMillan, Margaret L, Vercellotti, Gregory M, Tolar, Jakub, Osborn, Mark J, McIvor, R Scott, Webber, Beau R, Moriarity, Branden S

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Minicircle DNA-based Gene Therapy Coupled With Immune Modulation Permits Long-term Expression of α-L-Iduronidase in Mice With Mucopolysaccharidosis Type I von Osborn, Mark J, McElmurry, Ron T, Lees, Christopher J, DeFeo, Anthony P, Chen, Zhi-Ying, Kay, Mark A, Naldini, Luigi, Freeman, Gordon, Tolar, Jakub, Blazar, Bruce R

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Cas9-induced targeted integration of large DNA payloads in primary human T cells via homology-mediated end-joining DNA repair von Webber, Beau R., Johnson, Matthew J., Skeate, Joseph G., Slipek, Nicholas J., Lahr, Walker S., DeFeo, Anthony P., Mills, Lauren J., Qiu, Xiaohong, Rathmann, Blaine, Diers, Miechaleen D., Wick, Bryce, Henley, Tom, Choudhry, Modassir, Starr, Timothy K., McIvor, R. Scott, Moriarity, Branden S.

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CRISPR/Cas9 Targeted Gene Editing and Cellular Engineering in Fanconi Anemia von Osborn, Mark J., Lonetree, Cara-lin, Webber, Beau R., Patel, Dharmeshkumar, Dunmire, Samantha, DeFeo, Anthony P., McElroy, Amber N., MacMillan, Margaret L., Wagner, John E., Blazar, Bruce R., Tolar, Jakub

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Angiotensin receptor blockade mediated amelioration of mucopolysaccharidosis type I cardiac and craniofacial pathology von Osborn, Mark J., Webber, Beau R., McElmurry, Ronald T., Rudser, Kyle D., DeFeo, Anthony P., Muradian, Michael, Petryk, Anna, Hallgrimsson, Benedikt, Blazar, Bruce R., Tolar, Jakub, Braunlin, Elizabeth A.

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TALEN-based Individualized Gene Medicine for Epidermolysis Bullosa von Osborn, Mark J, Starker, Colby G, McElroy, Amber N, Webber, Beau R, DeFeo, Anthony P, Gabriel, Richard, Schmidt, Manfred, von Kalle, Christof, Carlson, Daniel F, Maeder, Morgan L, Joung, J Keith, Wagner, John E, Voytas, Daniel F, Blazar, Bruce R, Tolar, Jakub

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Minicircle DNA-based Gene Therapy Coupled With Immune Modulation Permits Long-term Expression of alpha -L-lduronidase in Mice With Mucopolysaccharidosis Type I von Osborn, Mark J, McElmurry, Ron T, Lees, Christopher J, DeFeo, Anthony P, Chen, Zhi-Ying, Kay, Mark A, Naldini, Luigi, Freeman, Gordon, Tolar, Jakub, Blazar, Bruce R

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Minicircle DNA-based Gene Therapy Coupled With Immune Modulation Permits Long-term Expression of [alpha]-L-Iduronidase in Mice With Mucopolysaccharidosis Type I von Osborn, Mark J, Mcelmurry, Ron T, Lees, Christopher J, Defeo, Anthony P, Chen, Zhi-ying, Kay, Mark A, Naldini, Luigi, Freeman, Gordon, Tolar, Jakub, Blazar, Bruce R

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Minicircle DNA-based Gene Therapy Coupled With Immune Modulation Permits Long-term Expression of α- -Iduronidase in Mice With Mucopolysaccharidosis Type I von Osborn, Mark J, McElmurry, Ron T, Lees, Christopher J, DeFeo, Anthony P, Chen, Zhi-Ying, Kay, Mark A, Naldini, Luigi, Freeman, Gordon, Tolar, Jakub, Blazar, Bruce R

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A global horizon scan of issues impacting marine and coastal biodiversity conservation von Herbert-Read, James E., Thornton, Ann, Amon, Diva J., Birchenough, Silvana N. R., Côté, Isabelle M., Dias, Maria P., Godley, Brendan J., Keith, Sally A., McKinley, Emma, Peck, Lloyd S., Calado, Ricardo, Defeo, Omar, Degraer, Steven, Johnston, Emma L., Kaartokallio, Hermanni, Macreadie, Peter I., Metaxas, Anna, Muthumbi, Agnes W. N., Obura, David O., Paterson, David M., Piola, Alberto R., Richardson, Anthony J., Schloss, Irene R., Snelgrove, Paul V. R., Stewart, Bryce D., Thompson, Paul M., Watson, Gordon J., Worthington, Thomas A., Yasuhara, Moriaki, Sutherland, William J.

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A global horizon scan of issues impacting marine and coastal biodiversity conservation von Herbert-Read, James E, Thornton, Ann, Amon, Diva J, Birchenough, Silvana NR, Côté, Isabelle M, Dias, Maria P, Godley, Brendan J, Keith, Sally A, McKinley, Emma, Peck, Lloyd S, Calado, Ricardo, Defeo, Omar, Degraer, Steven, Johnston, Emma L, Kaartokallio, Hermanni, Macreadie, Peter I, Metaxas, Anna, Muthumbi, Agnes WN, Obura, David O, Paterson, David M, Piola, Alberto R, Richardson, Anthony J, Schloss, Irene R, Snelgrove, Paul VR, Stewart, Bryce D, Thompson, Paul M, Watson, Gordon J, Worthington, Thomas A, Yasuhara, Moriaki, Sutherland, William J

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