Evaluation of TCR Gene Editing Achieved by TALENs, CRISPR/Cas9, and megaTAL Nucleases von Osborn, Mark J, Webber, Beau R, Knipping, Friederike, Lonetree, Cara-lin, Tennis, Nicole, DeFeo, Anthony P, McElroy, Amber N, Starker, Colby G, Lee, Catherine, Merkel, Sarah, Lund, Troy C, Kelly-Spratt, Karen S, Jensen, Michael C, Voytas, Daniel F, von Kalle, Christof, Schmidt, Manfred, Gabriel, Richard, Hippen, Keli L, Miller, Jeffrey S, Scharenberg, Andrew M, Tolar, Jakub, Blazar, Bruce R

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CRISPR/Cas9-Mediated Correction of the FANCD1 Gene in Primary Patient Cells von Skvarova Kramarzova, Karolina, Osborn, Mark J, Webber, Beau R, DeFeo, Anthony P, McElroy, Amber N, Kim, Chong Jai, Tolar, Jakub

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TALEN-based Gene Correction for Epidermolysis Bullosa von Osborn, Mark J, Starker, Colby G, McElroy, Amber N, Webber, Beau R, Riddle, Megan J, Xia, Lily, DeFeo, Anthony P, Gabriel, Richard, Schmidt, Manfred, Von Kalle, Christof, Carlson, Daniel F, Maeder, Morgan L, Joung, J Keith, Wagner, John E, Voytas, Daniel F, Blazar, Bruce R, Tolar, Jakub

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Fanconi anemia gene editing by the CRISPR/Cas9 system von Osborn, Mark J, Gabriel, Richard, Webber, Beau R, DeFeo, Anthony P, McElroy, Amber N, Jarjour, Jordan, Starker, Colby G, Wagner, John E, Joung, J Keith, Voytas, Daniel F, von Kalle, Christof, Schmidt, Manfred, Blazar, Bruce R, Tolar, Jakub

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Correction of Fanconi Anemia Mutations Using Digital Genome Engineering von Sipe, Christopher J, Kluesner, Mitchell G, Bingea, Samuel P, Lahr, Walker S, Andrew, Aneesha A, Wang, Minjing, DeFeo, Anthony P, Hinkel, Timothy L, Laoharawee, Kanut, Wagner, John E, MacMillan, Margaret L, Vercellotti, Gregory M, Tolar, Jakub, Osborn, Mark J, McIvor, R Scott, Webber, Beau R, Moriarity, Branden S

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CRISPR/Cas9-based genetic correction for recessive dystrophic epidermolysis bullosa von Webber, Beau R, Osborn, Mark J, McElroy, Amber N, Twaroski, Kirk, Lonetree, Cara-lin, DeFeo, Anthony P, Xia, Lily, Eide, Cindy, Lees, Christopher J, McElmurry, Ron T, Riddle, Megan J, Kim, Chong Jai, Patel, Dharmeshkumar D, Blazar, Bruce R, Tolar, Jakub

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Minicircle DNA-based Gene Therapy Coupled With Immune Modulation Permits Long-term Expression of α-L-Iduronidase in Mice With Mucopolysaccharidosis Type I von Osborn, Mark J, McElmurry, Ron T, Lees, Christopher J, DeFeo, Anthony P, Chen, Zhi-Ying, Kay, Mark A, Naldini, Luigi, Freeman, Gordon, Tolar, Jakub, Blazar, Bruce R

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CRISPR/Cas9 Targeted Gene Editing and Cellular Engineering in Fanconi Anemia von Osborn, Mark J., Lonetree, Cara-lin, Webber, Beau R., Patel, Dharmeshkumar, Dunmire, Samantha, DeFeo, Anthony P., McElroy, Amber N., MacMillan, Margaret L., Wagner, John E., Blazar, Bruce R., Tolar, Jakub

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Cas9-induced targeted integration of large DNA payloads in primary human T cells via homology-mediated end-joining DNA repair von Webber, Beau R, Johnson, Matthew J, Skeate, Joseph G, Slipek, Nicholas J, Lahr, Walker S, DeFeo, Anthony P, Mills, Lauren J, Qiu, Xiaohong, Rathmann, Blaine, Diers, Miechaleen D, Wick, Bryce, Henley, Tom, Choudhry, Modassir, Starr, Timothy K, McIvor, R Scott, Moriarity, Branden S

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Angiotensin receptor blockade mediated amelioration of mucopolysaccharidosis type I cardiac and craniofacial pathology von Osborn, Mark J., Webber, Beau R., McElmurry, Ronald T., Rudser, Kyle D., DeFeo, Anthony P., Muradian, Michael, Petryk, Anna, Hallgrimsson, Benedikt, Blazar, Bruce R., Tolar, Jakub, Braunlin, Elizabeth A.

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Synthetic Zinc Finger Nuclease Design and Rapid Assembly von OSBORN, Mark J, DEFEO, Anthony P, BLAZAR, Bruce R, TOLAR, Jakub

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Abstract 1611: Temporal recapitulation of genome instability in an iPSC model of osteosarcoma von Becklin, Kelsie Lynn, Madden, Rebecca, Mills, Lauren, Thue, Nicole, Carroll, Nathan, DeFeo, Anthony, Moriarity, Branden, Webber, Beau

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Megatal, Crispr/Cas9, and Talen T-Cell Receptor Gene Editing von Osborn, Mark J., Webber, Beau R, Knipping, Friederike, Lonetree, Cara-lin, DeFeo, Anthony, McElroy, Amber, Starker, Colby, Gabriel, Richard, Merkel, Sarah, Hippen, Keli L., Voytas, Daniel, von Kalle, Christof, Schmidt, Manfred, Miller, Jeffrey S., Jarjour, Jordan, Astrakhan, Alexander, Scharenberg, Andrew M, Tolar, Jakub, Blazar, Bruce R.

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TALEN-based Individualized Gene Medicine for Epidermolysis Bullosa von Osborn, Mark J, Starker, Colby G, McElroy, Amber N, Webber, Beau R, DeFeo, Anthony P, Gabriel, Richard, Schmidt, Manfred, von Kalle, Christof, Carlson, Daniel F, Maeder, Morgan L, Joung, J Keith, Wagner, John E, Voytas, Daniel F, Blazar, Bruce R, Tolar, Jakub

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Minicircle DNA-based Gene Therapy Coupled With Immune Modulation Permits Long-term Expression of alpha -L-lduronidase in Mice With Mucopolysaccharidosis Type I von Osborn, Mark J, McElmurry, Ron T, Lees, Christopher J, DeFeo, Anthony P, Chen, Zhi-Ying, Kay, Mark A, Naldini, Luigi, Freeman, Gordon, Tolar, Jakub, Blazar, Bruce R

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Minicircle DNA-based Gene Therapy Coupled With Immune Modulation Permits Long-term Expression of α- -Iduronidase in Mice With Mucopolysaccharidosis Type I von Osborn, Mark J, McElmurry, Ron T, Lees, Christopher J, DeFeo, Anthony P, Chen, Zhi-Ying, Kay, Mark A, Naldini, Luigi, Freeman, Gordon, Tolar, Jakub, Blazar, Bruce R

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Minicircle DNA-based Gene Therapy Coupled With Immune Modulation Permits Long-term Expression of [alpha]-L-Iduronidase in Mice With Mucopolysaccharidosis Type I von Osborn, Mark J, Mcelmurry, Ron T, Lees, Christopher J, Defeo, Anthony P, Chen, Zhi-ying, Kay, Mark A, Naldini, Luigi, Freeman, Gordon, Tolar, Jakub, Blazar, Bruce R

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Carrier and Sun Gear Set for use in a Transmission von Nesser, Austin, Defeo, Anthony

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Systems and methods for enhanced gaming servers von DeFeo, Anthony Peter, Pratt, Cory Allan, Witt, Christopher Russell, Kamner, David James

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SYSTEMS AND METHODS FOR ENHANCED GAMING SERVERS von DeFeo, Anthony Peter, Pratt, Cory Allan, Witt, Christopher Russell, Kamner, David James

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