An Engineered Adeno-Associated Virus Capsid Mediates Efficient Transduction of Pericytes and Smooth Muscle Cells of the Brain Vasculature von Ramirez, Servio H, Hale, Jonathan F, McCarthy, Siobhan, Cardenas, Christian L, Dona, Kalpani N Udeni Galpayage, Hanlon, Killian S, Hudry, Eloise, Cruz, Demitri De La, Ng, Carrie, Das, Sabyasachi, Nguyen, Diane M, Nammour, Josette, Bennett, Rachel E, Andrews, Allison M, Musolino, Patricia L, Maguire, Casey A

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An AAV capsid increases transduction of striatum and a ChAT promoter allows selective cholinergic neuron transduction von Santoscoy, Miguel C., Espinoza, Paula, De La Cruz, Demitri, Mahamdeh, Mohammed, Starr, Jacqueline R., Patel, Nikita, Maguire, Casey A.

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In vivo selection in non-human primates identifies AAV capsids for on-target CSF delivery to spinal cord von Hanlon, Killian S., Cheng, Ming, Ferrer, Roberto Montoro, Ryu, Jae Ryun, Lee, Boram, De La Cruz, Demitri, Patel, Nikita, Espinoza, Paula, Santoscoy, Miguel C., Gong, Yi, Ng, Carrie, Nguyen, Diane M., Nammour, Josette, Clark, Sean W., Heine, Vivi M., Sun, Woong, Kozarsky, Karen, Maguire, Casey A.

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Optimization of base editors for the functional correction of SMN2 as a treatment for spinal muscular atrophy von Alves, Christiano R. R., Ha, Leillani L., Yaworski, Rebecca, Sutton, Emma R., Lazzarotto, Cicera R., Christie, Kathleen A., Reilly, Aoife, Beauvais, Ariane, Doll, Roman M., de la Cruz, Demitri, Maguire, Casey A., Swoboda, Kathryn J., Tsai, Shengdar Q., Kothary, Rashmi, Kleinstiver, Benjamin P.

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AAV CAPSIDS FOR ON-TARGET DELIVERY TO SPINAL CORD von CHENG, Mingjie, DE LA CRUZ, Demitri Alexander, HANLON, Killian S, SANTOSCOY, Miguel Israel Chavez, MAGUIRE, Casey A

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