The Transcriptional and Functional Properties of Mouse Epiblast Stem Cells Resemble the Anterior Primitive Streak von Kojima, Yoji, Kaufman-Francis, Keren, Studdert, Joshua B., Steiner, Kirsten A., Power, Melinda D., Loebel, David A.F., Jones, Vanessa, Hor, Angelyn, de Alencastro, Gustavo, Logan, Grant J., Teber, Erdahl T., Tam, Oliver H., Stutz, Michael D., Alexander, Ian E., Pickett, Hilda A., Tam, Patrick P.L.

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Improved Genome Editing through Inhibition of FANCM and Members of the BTR Dissolvase Complex von de Alencastro, Gustavo, Puzzo, Francesco, Pavel-Dinu, Mara, Zhang, Feijie, Pillay, Sirika, Majzoub, Karim, Tiffany, Matthew, Jang, Hagoon, Sheikali, Adam, Cromer, M. Kyle, Meetei, Ruhikanta, Carette, Jan E., Porteus, Matthew H., Pekrun, Katja, Kay, Mark A.

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Modeling correction of severe urea cycle defects in the growing murine liver using a hybrid recombinant adeno‐associated virus/piggyBac transposase gene delivery system von Cunningham, Sharon C., Siew, Susan M., Hallwirth, Claus V., Bolitho, Christine, Sasaki, Natsuki, Garg, Gagan, Michael, Iacovos P., Hetherington, Nicola A., Carpenter, Kevin, de Alencastro, Gustavo, Nagy, Andras, Alexander, Ian E.

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Tracking Adeno-Associated Virus Capsid Evolution by High-Throughput Sequencing von de Alencastro, Gustavo, Pekrun, Katja, Valdmanis, Paul, Tiffany, Matthew, Xu, Jianpeng, Kay, Mark A

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Fludarabine increases nuclease-free AAV- and CRISPR/Cas9-mediated homologous recombination in mice von Tsuji, Shinnosuke, Stephens, Calvin J., Bortolussi, Giulia, Zhang, Feijie, Baj, Gabriele, Jang, Hagoon, de Alencastro, Gustavo, Muro, Andrés F., Pekrun, Katja, Kay, Mark A.

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539. Screening for Recombinant Adeno-Associated Viral Vectors That Selectively Transduce Hepatitis B Virus Infected Cells von de Alencastro, Gustavo, Pekrun, Katja, Kay, Mark

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Collybistin and gephyrin are novel components of the eukaryotic translation initiation factor 3 complex von Sertie, Andrea L, de Alencastro, Gustavo, De Paula, Vanessa J, Passos-Bueno, Maria Rita

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Using a barcoded AAV capsid library to select for clinically relevant gene therapy vectors von Pekrun, Katja, De Alencastro, Gustavo, Luo, Qing-Jun, Liu, Jun, Kim, Youngjin, Nygaard, Sean, Galivo, Feorillo, Zhang, Feijie, Song, Ren, Tiffany, Matthew R, Xu, Jianpeng, Hebrok, Matthias, Grompe, Markus, Kay, Mark A

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305. A Screening Strategy for Selecting Recombinant Adeno-Associated Viral Vectors That Selectively Transduce Viral Infected Cells von de Alencastro, Gustavo, Paulk, Nicole K., Pekrun, Katja, Kay, Mark A.

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Exploiting the unique regenerative capacity of the liver to underpin cell and gene therapy strategies for genetic and acquired liver disease von Logan, Grant J., de Alencastro, Gustavo, Alexander, Ian E., Yeoh, George C.

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335. Toward a Cellular Therapy for Metabolic Liver Disease: Gene Targeting of the Ornithine Transcarbamylase (Otc) Locus in Bipotential Murine Oval Liver Cells (BMOL) Using Adeno-A... von Logan, Grant J., Woo, Ken H., Smyth, Christine M., Cunningham, Sharon C., Trippit, Jessica R., de Alencastro, Gustavo, Yeoh, George C.T., Alexander, Ian E.

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700. Stable Correction of Severe Metabolic Liver Disease Phenotypes in the Growing Murine Liver Using a Hybrid rAAV/piggyBac Transposon Gene Delivery System von Cunningham, Sharon C., Siew, Susan M., Hallwirth, Claus V., Bolitho, Christine, Sasaki, Natsuki, Garg, Gagan, Michael, Iacovos P., Hetherington, Nicola A., de Alencastro, Gustavo, Nagy, Andras, Alexander, Ian E.

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METHODS AND COMPOSITIONS FOR EXPRESSING PHENYLALANINE HYDROXYLASE von de Alencastro, Gustavo

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ZINC FINGER NUCLEASE VARIANTS FOR TREATING OR PREVENTING LYSOSOMAL STORAGE DISEASES von Huston, Marshall, De Alencastro, Gustavo, Shivak, David

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ZINC FINGER NUCLEASE VARIANTS FOR TREATING OR PREVENTING LYSOSOMAL STORAGE DISEASES von DE ALENCASTRO, Gustavo, HUSTON, Marshall, SHIVAK, David

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METHODS AND COMPOSITIONS FOR FACILITATING HOMOLOGOUS RECOMBINATION von De Alencastro, Gustavo, Kay, Mark A

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METHODS AND COMPOSITIONS FOR EXPRESSING PHENYLALANINE HYDROXYLASE von DE ALENCASTRO, Gustavo

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METHODS AND COMPOSITIONS FOR EXPRESSING PHENYLALANINE HYDROXYLASE von DE ALENCASTRO, Gustavo

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AAV VARIANTS FOR THE TREATMENT OF DRY AMD von GRISHANIN, Ruslan, DE ALENCASTRO, Gustavo, RILEY, Brigit

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AAV VARIANTS FOR THE TREATMENT OF DRY AMD von GRISHANIN, Ruslan, DE ALENCASTRO, Gustavo, RILEY, Brigit

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