Long-term expression and repeated administration of AAV type 1, 2 and 5 vectors in skeletal muscle of immunocompetent adult mice von RIVIERE, C, DANOS, O, DOUAR, A. M

Volltext

AAV vectors for RNA-based modulation of gene expression von Danos, O

Volltext

Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients von CHARRIER, S, DUPRE, L, RONCAROLO, M. Grazia, GALY, A, SCARAMUZZA, S, JEANSON-LEH, L, BLUNDELL, M. P, DANOS, O, CATTANEO, F, AIUTI, A, ECKENBERG, R, THRASHER, A. J

Volltext

Intracellular Trafficking of Adeno-Associated Virus Vectors: Routing to the Late Endosomal Compartment and Proteasome Degradation von Douar, A M, Poulard, K, Stockholm, D, Danos, O

Volltext

A lentiviral vector encoding the human Wiskott-Aldrich syndrome protein corrects immune and cytoskeletal defects in WASP knockout mice von CHARRIER, S, STOCKHOLM, D, GALY, A, SEYE, K, OPOLON, P, TAVEAU, M, GROSS, D.-A, BUCHER-LAURENT, S, DELENDA, C, VAINCHENKER, W, DANOS, O

Volltext

Lentiviral protein delivery of meganucleases in human cells mediates gene targeting and alleviates toxicity von He, C, Gouble, A, Bourdel, A, Manchev, V, Poirot, L, Paques, F, Duchateau, P, Edelman, A, Danos, O

Volltext

Genetic correction of canine dystrophic epidermolysis bullosa mediated by retroviral vectors von Baldeschi, Christine, Gache, Yannick, Rattenholl, Anke, Bouillé, Pascale, Danos, Olivier, Ortonne, Jean-Paul, Bruckner-Tuderman, Leena, Meneguzzi, Guerrino

Volltext

Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors von Snyder, Richard O, Miao, Carol H, Patijn, Gijsbert A, Spratt, S. Kaye, Danos, Olivier, Nagy, Dea, Gown, Allen M, Winther, Brian, Meuse, Leonard, Cohen, Lawrence K, Thompson, Arthur R, Kay, Mark A

Volltext

AAV-mediated delivery of a mutated myostatin propeptide ameliorates calpain 3 but not α-sarcoglycan deficiency von BARTOLI, M, POUPIOT, J, RICHARD, I, VULIN, A, FOUGEROUSSE, F, ARANDEL, L, DANIELE, N, ROUDAUT, C, NOULET, F, GARCIA, L, DANOS, O

Volltext

Safe and Efficient Generation of Recombinant Retroviruses with Amphotropic and Ecotropic Host Ranges von Danos, Olivier, Mulligan, Richard C.

Volltext

Successful Interference with Cellular Immune Responses to Immunogenic Proteins Encoded by Recombinant Viral Vectors von Sarukhan, A, Camugli, S, Gjata, B, von Boehmer, H, Danos, O, Jooss, K

Volltext

Linear Topology Confers in Vivo Gene Transfer Activity to Polyethylenimines von Brissault, B, Leborgne, C, Guis, C, Danos, O, Cheradame, H, Kichler, A

Volltext

Human immunodeficiency virus type 1 Nef increases the efficiency of reverse transcription in the infected cell von Schwartz, O, Maréchal, V, Danos, O, Heard, J M

Volltext

HLA-A0201-restricted Cytolytic Responses to the rtTA Transactivator Dominant and Cryptic Epitopes Compromise Transgene Expression Induced by the Tetracycline on System von Ginhoux, F, Turbant, S, Gross, D A, Poupiot, J, Marais, T, Lone, Y, Lemonnier, F A, Firat, H, Perez, N, Danos, O, Davoust, J

Volltext

Canine Adenovirus Type 2 Attachment and Internalization: Coxsackievirus-Adenovirus Receptor, Alternative Receptors, and an RGD-Independent Pathway von Soudais, C, Boutin, S, Hong, S S, Chillon, M, Danos, O, Bergelson, J M, Boulanger, P, Kremer, E J

Volltext

Synthesis, Characterization, and Gene Transfer Application of Poly(ethylene glycol-b-ethylenimine) with High Molar Mass Polyamine Block von Brissault, B, Kichler, A, Leborgne, C, Danos, O, Cheradame, H, Gau, J, Auvray, L, Guis, C

Volltext

P.130 RGX-202: An investigational AAV8 gene therapy coding for a novel microdystrophin as a treatment for Duchenne muscular dystrophy von Dastgir, J., Falabella, P., Qiao, C., Kim, S., Buss, N., Fiscella, M., Pakola, S., Danos, O.

Volltext

DNA compaction into new DNA vectors based on cyclodextrin polymer: Surface enhanced Raman spectroscopy characterization von Burckbuchler, V., Wintgens, V., Lecomte, S., Percot, A., Leborgne, C., Danos, O., Kichler, A., Amiel, C.

Volltext

Adeno-associated virus pseudotype 5 vector improves gene transfer in arthritic joints von APPARAILLY, F, KHOURY, M, DOUAR, A.-M, TAK, P. P, JORGENSEN, C, VERVOORDELDONK, M. J. B, ADRIAANSEN, J, GICQUEL, E, PEREZ, N, RIVIERE, C, LOUIS-PLENCE, P, NOEL, D, DANOS, O

Volltext

Noninvasive monitoring of therapeutic gene transfer in animal models of muscular dystrophies von BARTOLI, M, POUPIOT, J, GOYENVALLE, A, PEREZ, N, GARCIA, L, DANOS, O, RICHARD, I

Volltext