ESkine, a Novel β-Chemokine, Is Differentially Spliced to Produce Secretable and Nuclear Targeted Isoforms von Baird, Janet W., Nibbs, Robert J.B., Komai-Koma, Mousa, Connolly, Julie Anne, Ottersbach, Katrin, Clark-Lewis, Ian, Liew, Foo Y., Graham, Gerard J.

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ESkine, a Novel β-Chemokine, Is Differentially Spliced to Produce Secretable and Nuclear Targeted Isoforms von Janet W. Baird, Robert J. B. Nibbs, Mousa Komai-Koma, Julie Anne Connolly, Katrin Ottersbach, Ian Clark-Lewis, Foo Y. Liew, Gerard J. Graham

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Medical management of muscle weakness in Duchenne muscular dystrophy von Rivera, Sarah R, Jhamb, Sumit K, Abdel-Hamid, Hoda Z, Acsadi, Gyula, Brandsema, John, Ciafaloni, Emma, Darras, Basil T, Iannaccone, Susan T, Konersman, Chamindra G, Kuntz, Nancy L, McDonald, Craig M, Parsons, Julie A, Tesi Rocha, Carolina, Zaidman, Craig M, Butterfield, Russell J, Connolly, Anne M, Mathews, Katherine D

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TBCRC 022: A Phase II Trial of Neratinib and Capecitabine for Patients With Human Epidermal Growth Factor Receptor 2-Positive Breast Cancer and Brain Metastases von Freedman, Rachel A, Gelman, Rebecca S, Anders, Carey K, Melisko, Michelle E, Parsons, Heather A, Cropp, Anne M, Silvestri, Kelly, Cotter, Christine M, Componeschi, Kathryn P, Marte, Juan M, Connolly, Roisin M, Moy, Beverly, Van Poznak, Catherine H, Blackwell, Kimberly L, Puhalla, Shannon L, Jankowitz, Rachel C, Smith, Karen L, Ibrahim, Nuhad, Moynihan, Timothy J, O'Sullivan, Ciara C, Nangia, Julie, Niravath, Polly, Tung, Nadine, Pohlmann, Paula R, Burns, Robyn, Rimawi, Mothaffar F, Krop, Ian E, Wolff, Antonio C, Winer, Eric P, Lin, Nancy U

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Mutations in sphingosine-1-phosphate lyase cause nephrosis with ichthyosis and adrenal insufficiency von Lovric, Svjetlana, Goncalves, Sara, Gee, Heon Yung, Oskouian, Babak, Srinivas, Honnappa, Choi, Won-Il, Shril, Shirlee, Ashraf, Shazia, Tan, Weizhen, Rao, Jia, Airik, Merlin, Schapiro, David, Braun, Daniela A, Sadowski, Carolin E, Widmeier, Eugen, Jobst-Schwan, Tilman, Schmidt, Johanna Magdalena, Girik, Vladimir, Capitani, Guido, Suh, Jung H, Lachaussée, Noëlle, Arrondel, Christelle, Patat, Julie, Gribouval, Olivier, Furlano, Monica, Boyer, Olivia, Schmitt, Alain, Vuiblet, Vincent, Hashmi, Seema, Wilcken, Rainer, Bernier, Francois P, Innes, A Micheil, Parboosingh, Jillian S, Lamont, Ryan E, Midgley, Julian P, Wright, Nicola, Majewski, Jacek, Zenker, Martin, Schaefer, Franz, Kuss, Navina, Greil, Johann, Giese, Thomas, Schwarz, Klaus, Catheline, Vilain, Schanze, Denny, Franke, Ingolf, Sznajer, Yves, Truant, Anne S, Adams, Brigitte, Désir, Julie, Biemann, Ronald, Pei, York, Ars, Elisabet, Lloberas, Nuria, Madrid, Alvaro, Dharnidharka, Vikas R, Connolly, Anne M, Willing, Marcia C, Cooper, Megan A, Lifton, Richard P, Simons, Matias, Riezman, Howard, Antignac, Corinne, Saba, Julie D, Hildebrandt, Friedhelm

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The care of patients with Duchenne, Becker, and other muscular dystrophies in the COVID‐19 pandemic von Veerapandiyan, Aravindhan, Wagner, Kathryn R., Apkon, Susan, McDonald, Craig M., Mathews, Katherine D., Parsons, Julie A., Wong, Brenda L., Eichinger, Katy, Shieh, Perry B., Butterfield, Russell J., Rao, Vamshi K., Smith, Edward C., Proud, Crystal M., Connolly, Anne M., Ciafaloni, Emma

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Natural history of infantile‐onset spinal muscular atrophy von Kolb, Stephen J., Coffey, Christopher S., Yankey, Jon W., Krosschell, Kristin, Arnold, W. David, Rutkove, Seward B., Swoboda, Kathryn J., Reyna, Sandra P., Sakonju, Ai, Darras, Basil T., Shell, Richard, Kuntz, Nancy, Castro, Diana, Parsons, Julie, Connolly, Anne M., Chiriboga, Claudia A., McDonald, Craig, Burnette, W. Bryan, Werner, Klaus, Thangarajh, Mathula, Shieh, Perry B., Finanger, Erika, Cudkowicz, Merit E., McGovern, Michelle M., McNeil, D. Elizabeth, Finkel, Richard, Iannaccone, Susan T., Kaye, Edward, Kingsley, Allison, Renusch, Samantha R., McGovern, Vicki L., Wang, Xueqian, Zaworski, Phillip G., Prior, Thomas W., Burghes, Arthur H.M., Bartlett, Amy, Kissel, John T.

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Spinal muscular atrophy care in the COVID‐19 pandemic era von Veerapandiyan, Aravindhan, Connolly, Anne M., Finkel, Richard S., Arya, Kapil, Mathews, Katherine D., Smith, Edward C., Castro, Diana, Butterfield, Russell J., Parsons, Julie A., Servais, Laurent, Kuntz, Nancy, Rao, Vamshi K., Brandsema, John F., Mercuri, Eugenio, Ciafaloni, Emma

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Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy von Finkel, Richard S, Mercuri, Eugenio, Darras, Basil T, Connolly, Anne M, Kuntz, Nancy L, Kirschner, Janbernd, Chiriboga, Claudia A, Saito, Kayoko, Servais, Laurent, Tizzano, Eduardo, Topaloglu, Haluk, Tulinius, Már, Montes, Jacqueline, Glanzman, Allan M, Bishop, Kathie, Zhong, Z. John, Gheuens, Sarah, Bennett, C. Frank, Schneider, Eugene, Farwell, Wildon, De Vivo, Darryl C

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Ataluren treatment of patients with nonsense mutation dystrophinopathy von Bushby, Katharine, Finkel, Richard, Wong, Brenda, Barohn, Richard, Campbell, Craig, Comi, Giacomo P., Connolly, Anne M., Day, John W., Flanigan, Kevin M., Goemans, Nathalie, Jones, Kristi J., Mercuri, Eugenio, Quinlivan, Ros, Renfroe, James B., Russman, Barry, Ryan, Monique M., Tulinius, Mar, Voit, Thomas, Moore, Steven A., Lee Sweeney, H., Abresch, Richard T., Coleman, Kim L., Eagle, Michelle, Florence, Julaine, Gappmaier, Eduard, Glanzman, Allan M., Henricson, Erik, Barth, Jay, Elfring, Gary L., Reha, Allen, Spiegel, Robert J., O'donnell, Michael W., Peltz, Stuart W., Mcdonald, Craig M.

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Repeated intravenous cardiosphere-derived cell therapy in late-stage Duchenne muscular dystrophy (HOPE-2): a multicentre, randomised, double-blind, placebo-controlled, phase 2 tria... von McDonald, Craig M, Marbán, Eduardo, Hendrix, Suzanne, Hogan, Nathaniel, Ruckdeschel Smith, Rachel, Eagle, Michelle, Finkel, Richard S, Tian, Cuixia, Janas, Joanne, Harmelink, Matthew M, Varadhachary, Arun S, Taylor, Michael D, Hor, Kan N, Mayer, Oscar H, Henricson, Erik K, Furlong, Pat, Ascheim, Deborah D, Rogy, Siegfried, Williams, Paula, Marbán, Linda, Butterfield, Russell, Connolly, Anne, Muntoni, Francesco, Joyce, Nanette C., Evans, Maya, Abedi, Mehrdad, Surampudi, Prasanth, Jhawar, Sanjay, Dayan, Jonathan G., Anthonisen, Colleen, Goude, Erica, Nicorici, Alina, Sarwary, Omaid, Prasad, Poonam, Baek, Jayoon, Newton, Andrew, Johnson, Hannah, Kusmik, Kyle, Filar, Lauri, Edmondson, Angie, Rybalsky, Irina, Chouteau, Wendy, Giordano, Anthony F., Rodriguez, Aixa, Anderson, Kristan, Wezel, Germaine, Vega, Melisa, Duke, Julie, Collado, Jorge, Civitello, Matthew, Wells, Julie, Pyzik, Erika, Rehborg, Rebecca, Brown, Michelle, Van Eyk, Jennifer, Rogers, Russell G.

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In Vivo Mononuclear Cell Tracking Using Superparamagnetic Particles of Iron Oxide Feasibility and Safety in Humans von RICHARDS, Jennifer M. J, SHAW, Catherine A, FORREST, Elaine K, BIENEK, Carol, MILLS, Nicholas L, BURDESS, Anne, DHALIWAL, Kev, SIMPSON, A. John, WALLACE, William A, HILL, Adam T, RODDIE, P. Huw, MCKILLOP, Graham, LANG, Ninian N, CONNOLLY, Thomas A, FEUERSTEIN, Giora Z, BARCLAY, G. Robin, TURNER, Marc L, NEWBY, David E, WILLIAMS, Michelle C, SEMPLE, Scott I. K, MACGILLIVRAY, Thomas J, GRAY, Calum, CRAWFORD, Julie H, ALAM, Shirjel R, ATKINSON, Anne P. M

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Electrical impedance myography in duchenne muscular dystrophy and healthy controls: A multicenter study of reliability and validity von Zaidman, Craig M., Wang, Lucy L., Connolly, Anne M., Florence, Julaine, Wong, Brenda L., Parsons, Julie A., Apkon, Susan, Goyal, Namita, Williams, Eugene, Escolar, Diana, Rutkove, Seward B., Bohorquez, Jose L.

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Safeguarding Female Reproductive Health against Endocrine Disrupting Chemicals-The FREIA Project von Duursen, Majorie B M van, Boberg, Julie, Christiansen, Sofie, Connolly, Lisa, Damdimopoulou, Pauliina, Filis, Panagiotis, Fowler, Paul A, Gadella, Bart M, Holte, Jan, Jääger, Kersti, Johansson, Hanna K L, Li, Tianyi, Mazaud-Guittot, Séverine, Parent, Anne-Simone, Salumets, Andres, Soto, Ana M, Svingen, Terje, Velthut-Meikas, Agne, Wedebye, Eva Bay, Xie, Yuling, Berg, Martin van den

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Clinical Follow-Up for Duchenne Muscular Dystrophy Newborn Screening: A Proposal von Kwon, Jennifer M., Abdel-Hamid, Hoda Z., Al-Zaidy, Samiah A., Mendell, Jerry R., Kennedy, Annie, Kinnett, Kathi, Cwik, Valerie A., Street, Natalie, Bolen, Julie, Day, John W., Connolly, Anne M.

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Longitudinal natural history in young boys with Duchenne muscular dystrophy von Coratti, Giorgia, Brogna, Claudia, Norcia, Giulia, Ricotti, Valeria, Abbott, Lianne, D'Amico, Adele, Berardinelli, Angela, Vita, Gian Luca, Lucibello, Simona, Messina, Sonia, Sansone, Valeria, Albamonte, Emilio, Colia, Giulia, Salmin, Francesca, Gardani, Alice, Manzur, Adnan, Main, Marion, Baranello, Giovanni, Arnoldi, Maria Teresa, Parsons, Julie, Carry, Terri, Connolly, Anne M., Bertini, Enrico, Muntoni, Francesco, Pane, Marika, Mercuri, Eugenio

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Putative adverse outcome pathways for female reproductive disorders to improve testing and regulation of chemicals von Johansson, Hanna K. L., Damdimopoulou, Pauliina, van Duursen, Majorie B. M., Boberg, Julie, Franssen, Delphine, de Cock, Marijke, Jääger, Kersti, Wagner, Magdalena, Velthut-Meikas, Agne, Xie, Yuling, Connolly, Lisa, Lelandais, Pauline, Mazaud-Guittot, Severine, Salumets, Andres, Draskau, Monica Kam, Filis, Panagiotis, Fowler, Paul A., Christiansen, Sofie, Parent, Anne-Simone, Svingen, Terje

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THE 6-minute walk test and other endpoints in Duchenne muscular dystrophy: Longitudinal natural history observations over 48 weeks from a multicenter study von Mcdonald, Craig M., Henricson, Erik K., Abresch, R. Ted, Florence, Julaine M., Eagle, Michelle, Gappmaier, Eduard, Glanzman, Allan M., Spiegel, Robert, Barth, Jay, Elfring, Gary, Reha, Allen, Peltz, Stuart

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The 6-minute walk test and other clinical endpoints in duchenne muscular dystrophy: Reliability, concurrent validity, and minimal clinically important differences from a multicente... von McDonald, Craig M., Henricson, Erik K., Abresch, R. Ted, Florence, Julaine, Eagle, Michelle, Gappmaier, Eduard, Glanzman, Allan M., Spiegel, Robert, Barth, Jay, Elfring, Gary, Reha, Allen, Peltz, Stuart W.

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A multinational study on motor function in early-onset FSHD von Mah, Jean K, Feng, Jia, Jacobs, Marni B, Duong, Tina, Carroll, Kate, de Valle, Katy, Carty, Cara L, Morgenroth, Lauren P, Guglieri, Michela, Ryan, Monique M, Clemens, Paula R, Thangarajh, Mathula, Webster, Richard, Smith, Edward, Connolly, Anne M, McDonald, Craig M, Karachunski, Peter, Tulinius, Mar, Harper, Amy, Cnaan, Avital, Chen, Yi-Wen

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