The ORTHO BC-SAT: A Satisfaction Questionnaire for Women Using Hormonal Contraceptives von Colwell, H. H., Mathias, S. D., Cimms, T. A., Rothman, M., Friedman, A. J., Patrick, D. L.

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Developing Outcomes Assessments as Endpoints for Registrational Clinical Trials of Antibacterial Drugs: 2015 Update From the Biomarkers Consortium of the Foundation for the Nationa... von Talbot, George H., Powers, John H., Hoffmann, Steven C.

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What are the important health-related quality of life issues in patients diagnosed with indolent lymphoma? von Mathias, S. D., Cimms, T. A., Colwell, H. H., Lubeck, D. P., Dawson, K. L., Huang, J. E.

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Enriching Media Data: A Special Report from the U.S. Coalition of Innovative Media Measurement: Quality Is Key Requisite for Maximizing Return on Advertising Investment von Broussard, Gerard

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Burosumab for the Treatment of Tumor‐Induced Osteomalacia von Jan de Beur, Suzanne M, Miller, Paul D, Weber, Thomas J, Peacock, Munro, Insogna, Karl, Kumar, Rajiv, Rauch, Frank, Luca, Diana, Cimms, Tricia, Roberts, Mary Scott, San Martin, Javier, Carpenter, Thomas O

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eP167: The impact of glycogen storage disease type III on children and adults: Results from an online survey von Mayhew, Jill, Evins, Ayla, Cimms, Tricia, Grimm, Andrew

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Qualitative evaluation of the symptoms and quality of life impacts of long-chain fatty acid oxidation disorders von Williams-Hall, Rebecca, Tinsley, Katie, Kruger, Eliza, Johnson, Chloe, Bowden, Alexandra, Cimms, Tricia, Gater, Adam

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PRO64 Psychometric Validation of the Brief Fatigue Inventory (BFI) and Brief Pain Inventory Short-Form (BPI-SF) in Tumor-Induced Osteomalacia (TIO) von Nixon, A., Nixon, M., Sun, W., Williams, A., Cimms, T.

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PRO56 Psychometric Validation of the Short-Form 36 (version 2) (SF-36) in Tumor-Induced Osteomalacia (TIO) von Cimms, T., Liu, J., Sun, W., Williams, A., Nixon, A.

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The efficacy and safety of burosumab in two patients with cutaneous skeletal hypophosphatemia syndrome von Sugarman, Jeffrey, Maruri, Ann, Hamilton, Dale J., Tabatabai, Laila, Luca, Diana, Cimms, Tricia, Krolczyk, Stan, Roberts, Mary Scott, Carpenter, Thomas O.

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Glycogen storage disease type III: a mixed-methods study to assess the burden of disease von Evins, Ayla, Mayhew, Jill, Cimms, Tricia, Whyte, Julie, Vong, Kathy, Hribal, Elizabeth, Evans, Christopher J, Grimm, Andrew

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Path to diagnosis and the caregiver’s perspective on the impact of creatine transporter deficiency von Rees, Linda, Evins, Ayla, Cimms, Tricia, Blair, Susan, Voorhees, Kristin, Brandabur, Melanie

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eP118 - Path to diagnosis and the caregiver’s perspective on the impact of creatine transporter deficiency von Rees, Linda, Evins, Ayla, Cimms, Tricia, Blair, Susan, Voorhees, Kristin, Brandabur, Melanie

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PRO39 Caregiver Perspectives on the Humanistic Burden of Creatine Transporter Deficiency von Evins, A., Cimms, T., Blair, S., Whyte, J., Paulich, M., Hribal, E., Estrada, A., Evans, C.

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Burosumab Improves Patient-Reported Outcomes in Adults With Tumor-Induced Osteomalacia: Mixed-Methods Analysis von Jan de Beur, Suzanne M, Cimms, Tricia, Nixon, Annabel, Theodore-Oklota, Christina, Luca, Diana, Roberts, Mary Scott, Egan, Shayna, Graham, Christina A, Hribal, Elizabeth, Evans, Christopher J, Wood, Sue, Williams, Angela

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Clinical Characteristics of Creatine Transporter Deficiency (CTD): Final Results of the Vigilan Observational Study (P8-8.002) von Brandabur, Melanie, Bianconi, Simona, Anselm, Irina, Barshop, Bruce A., Berry-Kravis, Elizabeth, Koeberl, Dwight D., Cecil, Kim M., Hannah-Shmouni, Fady, Longo, Nicola, Mercimek-Andrews, Saadet, Porter, Forbes D., Rahhal, Samar, Sutton, Reid, Blair, Susan, Cimms, Tricia, Zhang, Lin, PhD, Cristan Farmer, Thurm, Audrey, Miller, Judith

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PRO79 QUALITATIVE EXPLORATION OF THE PATIENT EXPERIENCE OF LONG-CHAIN FATTY ACID OXIDATION DISORDERS von Hall, R., Kruger, E., Bowden, A., Cimms, T., Skrinar, A., Tinsley, K., Gater, A.

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The MPS VII disease monitoring program (DMP) is a novel, longitudinal, cohort program with rigor beyond a traditional registry von Marsden, Deborah, Hostutler, Robert, Cimms, Tricia, Sansone, Ken, Ali, Qais Abu, Mansbach, Hank

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The long-term safety and efficacy of vestronidase alfa, rhGUS enzyme replacement therapy, in subjects with mucopolysaccharidosis VII von Wang, Raymond Y., da Silva Franco, José Francisco, López-Valdez, Jaime, Martins, Esmeralda, Sutton, Vernon Reid, Whitley, Chester B., Zhang, Lin, Cimms, Tricia, Marsden, Deborah, Jurecka, Agnieszka, Harmatz, Paul

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Reply to: Burosumab for Tumor‐Induced Osteomalacia: not Enough of a Good Thing von Jan de Beur, Suzanne M., Miller, Paul D., Weber, Thomas J., Peacock, Munro, Insogna, Karl, Kumar, Rajiv, Rauch, Frank, Luca, Diana, Cimms, Tricia, Roberts, Mary Scott, Martin, Javier San, Carpenter, Thomas O.

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