Molecular evolution of a novel hyperactive Sleeping Beauty transposase enables robust stable gene transfer in vertebrates von Chuah, Marinee K L, Ma, Ling, VandenDriessche, Thierry, Manoj, Namitha, Samara-Kuko, Ermira, Grzela, Dawid P, Schmitt, Andrea, Pryputniewicz, Diana, Fletcher, Bradley, Jerchow, Boris, Mátés, Lajos, Matrai, Janka, Gysemans, Conny, Becker, Katja, Miskey, Csaba, Belay, Eyayu, Acosta-Sanchez, Abel, Ivics, Zoltán, Izsvák, Zsuzsanna

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Hepatocyte‐targeted expression by integrase‐defective lentiviral vectors induces antigen‐specific tolerance in mice with low genotoxic risk von Mátrai, Janka, Cantore, Alessio, Bartholomae, Cynthia C., Annoni, Andrea, Wang, Wei, Acosta‐Sanchez, Abel, Samara‐Kuko, Ermira, De Waele, Liesbeth, Ma, Ling, Genovese, Pietro, Damo, Martina, Arens, Anne, Goudy, Kevin, Nichols, Timothy C., von Kalle, Christof, L. Chuah, Marinee K., Roncarolo, Maria Grazia, Schmidt, Manfred, VandenDriessche, Thierry, Naldini, Luigi

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Codon optimization of human factor VIII cDNAs leads to high-level expression von Ward, Natalie J., Buckley, Suzanne M.K., Waddington, Simon N., VandenDriessche, Thierry, Chuah, Marinee K.L., Nathwani, Amit C., McIntosh, Jenny, Tuddenham, Edward G.D., Kinnon, Christine, Thrasher, Adrian J., McVey, John H.

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Emerging potential of transposons for gene therapy and generation of induced pluripotent stem cells von VandenDriessche, Thierry, Ivics, Zoltán, Izsvák, Zsuzsanna, Chuah, Marinee K.L.

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Hyperactive PiggyBac Transposons for Sustained and Robust Liver-targeted Gene Therapy von Di Matteo, Mario, Samara-Kuko, Emira, Ward, Natalie J, Waddingon, Simon N, McVey, John H, Chuah, Marinee KL, VandenDriessche, Thierry

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Recent Advances in Lentiviral Vector Development and Applications von Mátrai, Janka, Chuah, Marinee KL, VandenDriessche, Thierry

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Intrinsic cell memory reinforces myogenic commitment of pericyte-derived iPSCs von Quattrocelli, Mattia, Palazzolo, Giacomo, Floris, Giuseppe, Schöffski, Patrick, Anastasia, Luigi, Orlacchio, Aldo, Vandendriessche, Thierry, Chuah, Marinee KL, Cossu, Giulio, Verfaillie, Catherine, Sampaolesi, Maurilio

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Preclinical and clinical progress in hemophilia gene therapy von Mátrai, Janka, Chuah, Marinee KL, VandenDriessche, Thierry

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Efficient stable gene transfer into human cells by the Sleeping Beauty transposon vectors von Izsvák, Zsuzsanna, Chuah, Marinee K.L., VandenDriessche, Thierry, Ivics, Zoltán

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Nanoparticles for the delivery of genes and drugs to human hepatocytes von Kuroda, Shun'ichi, Yamada, Tadanori, Iwasaki, Yasushi, Tada, Hiroko, Iwabuki, Hidehiko, Chuah, Marinee KL, VandenDriessche, Thierry, Fukuda, Hideki, Kondo, Akihiko, Ueda, Masakazu, Seno, Masaharu, Tanizawa, Katsuyuki

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Restoration of Plasma von Willebrand Factor Deficiency Is Sufficient to Correct Thrombus Formation After Gene Therapy for Severe von Willebrand Disease von De Meyer, Simon F, Vandeputte, Nele, Pareyn, Inge, Petrus, Inge, Lenting, Peter J, Chuah, Marinee K.L, VandenDriessche, Thierry, Deckmyn, Hans, Vanhoorelbeke, Karen

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Lentiviral vectors containing the human immunodeficiency virus type-1 central polypurine tract can efficiently transduce nondividing hepatocytes and antigen-presenting cells in viv... von VandenDriessche, Thierry, Thorrez, Lieven, Naldini, Luigi, Follenzi, Antonia, Moons, Lieve, Berneman, Zwi, Collen, Desire, Chuah, Marinee K.L.

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Efficient Lentiviral Transduction and Improved Engraftment of Human Bone Marrow Mesenchymal Cells von Van Damme, An, Thorrez, Lieven, Ma, Ling, Vandenburgh, Herman, Eyckmans, Jeroen, Dell'Accio, Francesco, De Bari, Cosimo, Luyten, Frank, Lillicrap, David, Collen, Désiré, VandenDriessche, Thierry, Chuah, Marinee K.L.

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Therapeutic factor VIII levels and negligible toxicity in mouse and dog models of hemophilia A following gene therapy with high-capacity adenoviral vectors von Chuah, Marinee K.L., Schiedner, Gudrun, Thorrez, Lieven, Brown, Brian, Johnston, Marion, Gillijns, Veerle, Hertel, Sabine, Van Rooijen, Nico, Lillicrap, David, Collen, Désiré, VandenDriessche, Thierry, Kochanek, Stefan

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Comparative Analysis of Transposable Element Vector Systems in Human Cells von Grabundzija, Ivana, Irgang, Markus, Mátés, Lajos, Belay, Eyayu, Matrai, Janka, Gogol-Döring, Andreas, Kawakami, Koichi, Chen, Wei, Ruiz, Patricia, Chuah, Marinee K.L., VandenDriessche, Thierry, Izsvák, Zsuzsanna, Ivics, Zoltán

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Novel Hyperactive Transposons for Genetic Modification of Induced Pluripotent and Adult Stem Cells: A Nonviral Paradigm for Coaxed Differentiation von Belay, Eyayu, Mátrai, Janka, Acosta‐Sanchez, Abel, Ma, Ling, Quattrocelli, Mattia, Mátés, Lajos, Sancho‐Bru, Pau, Geraerts, Martine, Yan, Bing, Vermeesch, Joris, Rincón, Melvin Yesid, Samara‐Kuko, Ermira, Ivics, Zoltán, Verfaillie, Catherine, Sampaolesi, Maurilio, Izsvák, Zsuzsanna, VandenDriessche, Thierry, Chuah, Marinee K. L.

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Gene therapy for hemophilia von Chuah, Marinee K. L., Collen, Desire, VandenDriessche, Thierry

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Moving gene therapy forward with mobile DNA von VandenDriessche, Thierry, Chuah, Marinee K L

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Xenogeneic liver models for gene therapy von Vandendriessche, Thierry, Chuah, Marinee K L

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PiggyBac Toolbox von Di Matteo, Mario, Mátrai, Janka, Belay, Eyayu, Firdissa, Tewodros, VandenDriessche, Thierry, Chuah, Marinee K. L.

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