Prebiotics enhance persistence of fermented-food associated bacteria in in vitro cultivated fecal microbial communities von Christensen, Chloe M., Kok, Car Reen, Auchtung, Jennifer M., Hutkins, Robert

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Generation of an infantile GM1 gangliosidosis induced pluripotent stem cell line (CHOCi005-A) for disease modeling and therapeutic testing von Rha, Allisandra K., Christensen, Chloe L., Kan, Shih-Hsin, Harb, Jerry F., Andrade-Heckman, Perla, Wang, Raymond Y.

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Base editing of the GLB1 gene is therapeutic in GM1 gangliosidosis patient-derived cells von Rha, Allisandra K., Kan, Shih-Hsin, Andrade-Heckman, Perla, Christensen, Chloe L., Harb, Jerry F., Wang, Raymond Y.

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Base editing rescues acid α-glucosidase function in infantile-onset Pompe disease patient-derived cells von Christensen, Chloe L., Kan, Shih-Hsin, Andrade-Heckman, Perla, Rha, Allisandra K., Harb, Jerry F., Wang, Raymond Y.

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CRISPR-mediated generation and characterization of a Gaa homozygous c.1935C>A (p.D645E) Pompe disease knock-in mouse model recapitulating human infantile onset-Pompe disease von Kan, Shih-hsin, Huang, Jeffrey Y., Harb, Jerry, Rha, Allisandra, Dalton, Nancy D., Christensen, Chloe, Chan, Yunghang, Davis-Turak, Jeremy, Neumann, Jonathan, Wang, Raymond Y.

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Base editing corrects the common Salla disease SLC17A5 c.115C>T variant von Harb, Jerry F., Christensen, Chloe L., Kan, Shih-Hsin, Rha, Allisandra K., Andrade-Heckman, Perla, Pollard, Laura, Steet, Richard, Huang, Jeffrey Y., Wang, Raymond Y.

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Generation of two induced pluripotent stem cell lines (CHOCi002-A and CHOCi003-A) from Pompe disease patients with compound heterozygous mutations in the GAA gene von Christensen, Chloe, Heckman, Perla, Rha, Allisandra, Kan, Shih-Hsin, Harb, Jerry, Wang, Raymond

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Kombucha tea as an anti-hyperglycemic agent in humans with diabetes – a randomized controlled pilot investigation von Mendelson, Chagai, Sparkes, Sabrina, Merenstein, Daniel J., Christensen, Chloe, Sharma, Varun, Desale, Sameer, Auchtung, Jennifer M., Kok, Car Reen, Hallen-Adams, Heather E., Hutkins, Robert

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Cell and Gene Therapies for Mucopolysaccharidoses: Base Editing and Therapeutic Delivery to the CNS von Christensen, Chloe L, Ashmead, Rhea E, Choy, Francis Y M

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Microbiota, metabolic profiles and immune biomarkers in infants receiving formula with added bovine milk fat globule membrane: a randomized, controlled trial von Christensen, Chloe, Kok, Car Reen, Harris, Cheryl L, Moore, Nancy, Wampler, Jennifer L, Zhuang, Weihong, Wu, Steven S, Hutkins, Robert, Izard, Jacques, Auchtung, Jennifer M

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Complete genome sequence of the probiotic Bifidobacterium adolescentis strain iVS-1 von Chacón-Vargas, Katherine, Van Haute, Mallory J, Kessinger, Isabella M K, McClain, Kaylee A, Yumul, Shara R P, Christensen, Chloe M, Lewis, Zachery T, Auchtung, Thomas A

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A Prospective Treatment Option for Lysosomal Storage Diseases: CRISPR/Cas9 Gene Editing Technology for Mutation Correction in Induced Pluripotent Stem Cells von Christensen, Chloe L, Choy, Francis Y M

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Progranulin as a Novel Factor in Gaucher Disease von Choy, Francis Y.M., Christensen, Chloe L.

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Enhancing cell culture conditions for MPS IIIB induced pluripotent stem cells: The impact of dysregulated heparan sulfate turnover on FGF2 signalling von Christensen, Chloe L., Choy, Francis

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Restoration of acid-alpha glucosidase expression and function through efficient adenine base editing of Pompe disease variants von Christensen, Chloe L., Kan, Shih-hsin, Andrade-Heckman, Perla, Rha, Allisandra, Harb, Jerry, Wang, Raymond Y.

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Prime editing corrects the c.1935C > A pathogenic variant in infantile-onset Pompe disease mouse myoblasts von Rha, Allisandra, Kan, Shih-hsin, Christensen, Chloe, Harb, Jerry F., Andrade-Heckman, Perla, Wang, Raymond Y.

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Prime editing corrects the Gaa c.1935C > A pathogenic variant in infantile-onset Pompe disease mouse myoblasts von Rha, Allisandra, Kan, Shih-hsin, Christensen, Chloe, Harb, Jerry F., Andrade-Heckman, Perla, Wang, Raymond Y.

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Prime editing corrects the c.1826dupA mutation in infantile-onset Pompe disease von Rha, Allisandra K., Huang, Jeffrey Y., Kan, Shih-hsin, Harb, Jerry, Christensen, Chloe, Wang, Raymond Y.

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Crossing biological membranes using PTD4: Implications for treatment of MPS IIIB through enzyme replacement therapy von Ashmead, Rhea E., Christensen, Chloe L., Choy, Francis Y.M.

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Base editing of the N370S mutation in Gaucher disease skin fibroblasts von Christensen, Chloe, Wells-Durand, Emma, Hilton, Anna-Maria, Thompson, Jenna, Chu, Samuel, Choy, Francis

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