rAAV2/5 gene-targeting to rods:dose-dependent efficiency and complications associated with different promoters von Beltran, W A, Boye, S L, Boye, S E, Chiodo, V A, Lewin, A S, Hauswirth, W W, Aguirre, G D

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Targeting gene expression to cones with human cone opsin promoters in recombinant AAV von Komáromy, A M, Alexander, J J, Cooper, A E, Chiodo, V A, Acland, G M, Hauswirth, W W, Aguirre, G D

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AAV8(Y733F)-mediated gene therapy in a Spata7 knockout mouse model of Leber congenital amaurosis and retinitis pigmentosa von Zhong, H, Eblimit, A, Moayedi, Y, Boye, S L, Chiodo, V A, Chen, Y, Li, Y, Nichols, R M, Hauswirth, W W, Chen, R, Mardon, G

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Cone Phosphodiesterase-6 ' Restores Rod Function and Confers Distinct Physiological Properties in the Rod Phosphodiesterase-6 -Deficient rd10 Mouse von Deng, W.-T., Sakurai, K., Kolandaivelu, S., Kolesnikov, A. V., Dinculescu, A., Li, J., Zhu, P., Liu, X., Pang, J., Chiodo, V. A., Boye, S. L., Chang, B., Ramamurthy, V., Kefalov, V. J., Hauswirth, W. W.

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Targeting gene expression to cones with human cone opsin promoters in recombinant AAV von Komaromy, A.M, Alexander, J.J, Cooper, A.E, Chiodo, V.A, Acland, G.M, Hauswirth, W.W, Aguirre, G.D

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Targeting gene expression to cones with human cone opsin promoters in recombinant AAV von Komaromy, A.M, Alexander, J.J, Cooper, A.E, Chiodo, V.A, Glushakova, L.G, Acland, G.M, Hauswirth, W.W, Aguirre, G.D

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Identification, genetic analysis and DNA sequence of a 7.8‐kb virulence region of the Salmonella typhimurium virulence plasmid von Gulig, Paul A., Caldwell, Allison L., Chiodo, Vince A.

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Genetic and DNA sequence analysis of the Salmonella typhimurium virulence plasmid gene encoding the 28,000-molecular-weight protein von GULIG, P. A, CHIODO, V. A

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RD3 gene delivery restores guanylate cyclase localization and rescues photoreceptors in the Rd3 mouse model of Leber congenital amaurosis 12 von Molday, Laurie L, Djajadi, Hidayat, Yan, Paul, Szczygiel, Lukasz, Boye, Sanford L, Chiodo, Vince A, Gregory-Evans, Kevin, Sarunic, Marinko V, Hauswirth, William W, Molday, Robert S

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The Human Rhodopsin Kinase Promoter in an AAV5 Vector Confers Rod- and Cone-Specific Expression in the Primate Retina von BOYE, Shannon E, ALEXANDER, John J, CLARK, Mark E, GIRKIN, Christopher A, HAUSWIRTH, William W, GAMLIN, Paul D, BOYE, Sanford L, WITHERSPOON, Clark D, SANDEFER, Kristen J, CONLON, Thomas J, ERGER, Kirsten, JINGFEN SUN, RYALS, Renee, CHIODO, Vince A

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Vitreal delivery of AAV vectored Cnga3 restores cone function in CNGA3-/-/Nrl-/- mice, an all-cone model of CNGA3 achromatopsia von Du, Wei, Tao, Ye, Deng, Wen-Tao, Zhu, Ping, Li, Jie, Dai, Xufeng, Zhang, Yuxin, Shi, Wei, Liu, Xuan, Chiodo, Vince A, Ding, Xi-Qin, Zhao, Chen, Michalakis, Stylianos, Biel, Martin, Zhang, Zuoming, Qu, Jia, Hauswirth, William W, Pang, Ji-Jing

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Urokinase: a chemotactic factor for polymorphonuclear leukocytes in vivo von Boyle, MD, Chiodo, VA, Lawman, MJ, Gee, AP, Young, M

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Gene Therapy for Retinitis Pigmentosa Caused by MFRP Mutations: Human Phenotype and Preliminary Proof of Concept von DINCULESCU, Astra, ESTREICHER, Jackie, MIN, Seok-Hong, CHIODO, Vince A, NEELEY, Andy, XUAN LIU, XINHUA SHU, MATIAS-FLORENTINO, Margarita, BUENTELLO-VOLANTE, Beatriz, BOYE, Sanford L, CIDECIYAN, Artur V, HAUSWIRTH, William W, ZENTENO, Juan C, JACOBSON, Samuel G, ALEMAN, Tomas S, SCHWARTZ, Sharon B, WEI CHIEH HUANG, ROMAN, Alejandro J, SUMAROKA, Alexander, QIUHONG LI, DENG, Wen-Tao

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Production and purification of serotype 1, 2, and 5 recombinant adeno-associated viral vectors von Zolotukhin, Sergei, Potter, Mark, Zolotukhin, Irene, Sakai, Yoshihisa, Loiler, Scott, Fraites, Thomas J, Chiodo, Vince A, Phillipsberg, Tina, Muzyczka, Nicholas, Hauswirth, William W, Flotte, Terance R, Byrne, Barry J, Snyder, Richard O

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Gene therapy restores vision-dependent behavior as well as retinal structure and function in a mouse model of RPE65 Leber congenital amaurosis von Pang, Ji-jing, Chang, Bo, Kumar, Ashok, Nusinowitz, Steven, Noorwez, Syed M, Li, Jie, Rani, Asha, Foster, Thomas C, Chiodo, Vince A, Doyle, Thomas, Li, Huashi, Malhotra, Ritu, Teusner, Jacqueline T, McDowell, J Hugh, Min, Seok-Hong, Li, Qiuhong, Kaushal, Shalesh, Hauswirth, William W

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Erratum: Targeting gene expression to cones with human cone opsin promoters in recombinant AAV von Komáromy, A M, Alexander, J J, Cooper, A E, Chiodo, V A, Acland, G M, Hauswirth, W W, Aguirre, G D

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Gene therapy rescues cone function in congenital achromatopsia von Komáromy, András M., Alexander, John J., Rowlan, Jessica S., Garcia, Monique M., Chiodo, Vince A., Kaya, Asli, Tanaka, Jacqueline C., Acland, Gregory M., Hauswirth, William W., Aguirre, Gustavo D.

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Erratum: Targeting gene expression to cones with human cone opsin promoters in recombinant AAV von Komáromy, A M, Alexander, J J, Cooper, A E, Chiodo, V A, Glushakova, L G, Acland, G M, Hauswirth, W W, Aguirre, G D

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Targeting gene expression to cones with human cone opsin promoters in recombinant AA V von KOMAROMY, A. M, ALEXANDER, J. J, COOPER, A. E, CHIODO, V. A, ACLAND, G. M, HAUSWIRTH, W. W, AGUIRRE, G. D

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Structural and Functional Protection of Photoreceptors from MNU-Induced Retinal Degeneration by the X-Linked Inhibitor of Apoptosis von Petrin, Dino, Baker, Adam, Coupland, Stuart G, Liston, Peter, Narang, Monica, Damji, Karim, Leonard, Brian, Chiodo, Vince A, Timmers, Adrian, Hauswirth, William, Korneluk, Robert G, Tsilfidis, Catherine

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