Apc inhibition of Wnt signaling regulates supernumerary tooth formation during embryogenesis and throughout adulthood von Wang, Xiu-Ping, O'Connell, Daniel J, Lund, Jennifer J, Saadi, Irfan, Kuraguchi, Mari, Turbe-Doan, Annick, Cavallesco, Resy, Kim, Hyunsoo, Park, Peter J, Harada, Hidemitsu, Kucherlapati, Raju, Maas, Richard L

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Mutations in the RNA Granule Component TDRD7 Cause Cataract and Glaucoma von Lachke, Salil A., Alkuraya, Fowzan S., Kneeland, Stephen C., Ohn, Takbum, Aboukhalil, Anton, Howell, Gareth R., Saadi, Irfan, Cavallesco, Resy, Yue, Yingzi, Tsai, Anne C-H., Nair, K. Saidas, Cosma, Mihai I., Smith, Richard S., Hodges, Emily, AlFadhli, Suad M., Al-Hajeri, Amal, Shamseldin, Hanan E., Behbehani, AbdulMutalib, Hannon, Gregory J., Bulyk, Martha L., Drack, Arlene V., Anderson, Paul J., John, Simon W. M., Maas, Richard L.

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Deficiency of the Cytoskeletal Protein SPECC1L Leads to Oblique Facial Clefting von Saadi, Irfan, Alkuraya, Fowzan S., Gisselbrecht, Stephen S., Goessling, Wolfram, Cavallesco, Resy, Turbe-Doan, Annick, Petrin, Aline L., Harris, James, Siddiqui, Ursela, Grix, Arthur W., Hove, Hanne D., Leboulch, Philippe, Glover, Thomas W., Morton, Cynthia C., Richieri-Costa, Antonio, Murray, Jeffrey C., Erickson, Robert P., Maas, Richard L.

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Pax6- and Six3-mediated induction of lens cell fate in mouse and human ES cells von Anchan, Raymond M, Lachke, Salil A, Gerami-Naini, Behzad, Lindsey, Jennifer, Ng, Nicholas, Naber, Catherine, Nickerson, Michael, Cavallesco, Resy, Rowan, Sheldon, Eaton, Jennifer L, Xi, Qiongchao, Maas, Richard L

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Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia von Cavazzana-Calvo, Marina, Payen, Emmanuel, Negre, Olivier, Wang, Gary, Hehir, Kathleen, Fusil, Floriane, Down, Julian, Denaro, Maria, Brady, Troy, Westerman, Karen, Cavallesco, Resy, Gillet-Legrand, Beatrix, Caccavelli, Laure, Sgarra, Riccardo, Maouche-Chrétien, Leila, Bernaudin, Françoise, Girot, Robert, Dorazio, Ronald, Mulder, Geert-Jan, Polack, Axel, Bank, Arthur, Soulier, Jean, Larghero, Jérôme, Kabbara, Nabil, Dalle, Bruno, Gourmel, Bernard, Socie, Gérard, Chrétien, Stany, Cartier, Nathalie, Aubourg, Patrick, Fischer, Alain, Cornetta, Kenneth, Galacteros, Frédéric, Beuzard, Yves, Gluckman, Eliane, Bushman, Frederick, Hacein-Bey-Abina, Salima, Leboulch, Philippe

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Outcomes of Gene Therapy for Severe Sickle Disease and Beta-Thalassemia Major Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral Beta A... von Cavazzana, Marina, Ribeil, Jean-Antoine, Payen, Emmanuel, Suarez, Felipe, Beuzard, Yves, Touzot, Fabien, Cavallesco, Resy, Lefrere, Francois, Chretien, Stany, Bourget, Philippe, Monpoux, Fabrice, Pondarre, Corinne, Neven, Benedicte, Schmidt, Manfred, von Kalle, Christof, Kuypers, Frans A., Sandler, Laura, Soni, Sandeep, Hermine, Olivier, Blanche, Stephane, De Montalembert, Mariane, Hacien-Bey-Abina, Salima, Leboulch, Philippe

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Pax6- and Six3-Mediated Induction of Lens Cell Fate in Mouse and Human ES Cells von Anchan, Raymond M, Lachke, Salil A, Gerami-Naini, Behzad, Lindsey, Jennifer, Ng, Nicholas, Naber, Catherine, Nickerson, Michael, Cavallesco, Resy, Rowan, Sheldon, Eaton, Jennifer L, Xi, Qiongchao, Maas, Richard L

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Study Hgb-205: Outcomes of Gene Therapy for Hemoglobinopathies Via Transplantation of Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral βΑ-T87Q-Globin Vector... von Cavazzana, Marina, Ribeil, Jean-Antoine, Payen, Emmanuel, Suarez, Felipe, Beuzard, Yves, Touzot, Fabien, Cavallesco, Resy, Lefrère, Francois, Chretien, Stany, Bourget, Phillipe, Monpoux, Fabrice, Pondarre, Corrine, Neven, Benedicte, Schmidt, Manfred, von Kalle, Christof, Sandler, Laura, Soni, Sandeep, Hermine, Olivier, Blanche, Stephanie, De Montalembert, Mariane, Hacein-Bey-Abina, Salima, Leboulch, Philippe

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Deficiency of the Cytoskeletal Protein SPECC1 L Leads to Oblique Facial Clefting von SAADI, Irfan, ALKURAYA, Fowzan S, HOVE, Hanne D, LEBOULCH, Philippe, GLOVER, Thomas W, MORTON, Cynthia C, RICHIERI-COSTA, Antonio, MURRAY, Jeffrey C, ERICKSON, Robert P, MAAS, Richard L, GISSELBRECHT, Stephen S, GOESSLING, Wolfram, CAVALLESCO, Resy, TURBE-DOAN, Annick, PETRIN, Aline L, HARRIS, James, SIDDIQUI, Ursela, GRIX, Arthur W

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Transfusion independence and HMGA2 activation after gene therapy of human -thalassaemia von Leboulch, Philippe, Cavazzana-Calvo, Marina, Payen, Emmanuel, Negre, Olivier, Wang, Gary, Hehir, Kathleen, Fusil, Floriane, Down, Julian, Denaro, Maria, Brady, Troy, Westerman, Karen, Cavallesco, Resy, Gillet-Legrand, Beatrix, Caccavelli, Laure, Sgarra, Riccardo, Maouche-Chrétien, Leila, Bernaudin, Françoise, Girot, Robert, Dorazio, Ronald, Mulder, Geert-Jan, Polack, Axel, Bank, Arthur, Soulier, Jean, Larghero, Jérôme, Kabbara, Nabil, Dalle, Bruno, Gourmel, Bernard, Socie, Gérard, Chrétien, Stany, Cartier, Nathalie, Aubourg, Patrick, Fischer, Alain, Cornetta, Kenneth, Galacteros, Frédéric, Beuzard, Yves, Gluckman, Eliane, Bushman, Frederick, Hacein-Bey-Abina, Salima

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Modulatory Subdomains of the HS2 Enhancer Differentially Regulate Enhancer Activity in Erythroid Cells at Different Developmental Stages von Cavallesco, Resy, Tuan, Dorothy

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