Ribitol restores functionally glycosylated α-dystroglycan and improves muscle function in dystrophic FKRP-mutant mice von Cataldi, Marcela P., Lu, Peijuan, Blaeser, Anthony, Lu, Qi Long

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ISPD Overexpression Enhances Ribitol-Induced Glycosylation of α-Dystroglycan in Dystrophic FKRP Mutant Mice von Cataldi, Marcela P., Blaeser, Anthony, Lu, Peijuan, Leroy, Victoria, Lu, Qi Long

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Differential Effects of DNA Double-Strand Break Repair Pathways on Single-Strand and Self-Complementary Adeno-Associated Virus Vector Genomes von Cataldi, Marcela P, McCarty, Douglas M

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Functional correction of neurological and somatic disorders at later stages of disease in MPS IIIA mice by systemic scAAV9-hSGSH gene delivery von Fu, Haiyan, Cataldi, Marcela P, Ware, Tierra A, Zaraspe, Kimberly, Meadows, Aaron S, Murrey, Darren A, McCarty, Douglas M

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Improved efficacy of FKRP AAV gene therapy by combination with ribitol treatment for LGMD2I von Cataldi, Marcela P, Vannoy, Charles H, Blaeser, Anthony, Tucker, Jason D, Leroy, Victoria, Rawls, Raegan, Killilee, Jessalyn, Holbrook, Molly C, Lu, Qi Long

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Break Down of the Complexity and Inconsistency Between Levels of Matriglycan and Disease Phenotype in FKRP-Related Dystroglycanopathies: A Review and Model of Interpretation von Lu, Qi L., Holbrook, Molly C., Cataldi, Marcela P., Blaeser, Anthony

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Hairpin-end conformation of adeno-associated virus genome determines interactions with DNA-repair pathways von Cataldi, M P, McCarty, D M

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