Effect of Genome Size on AAV Vector Packaging von Wu, Zhijian, Yang, Hongyan, Colosi, Peter

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Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis: Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery von Cukras, Catherine, Wiley, Henry E., Jeffrey, Brett G., Sen, H. Nida, Turriff, Amy, Zeng, Yong, Vijayasarathy, Camasamudram, Marangoni, Dario, Ziccardi, Lucia, Kjellstrom, Sten, Park, Tae Kwon, Hiriyanna, Suja, Wright, J. Fraser, Colosi, Peter, Wu, Zhijian, Bush, Ronald A., Wei, Lisa L., Sieving, Paul A.

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Christian Personalism versus Utilitarianism: An Analysis of Their Approaches to Love and Suffering von Colosi, Peter J.

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Bill of Rights for Children: Linacre Quarterly, 81:4, 298–301 von Colosi and, Peter J., Williams, William V.

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A long-term efficacy study of gene replacement therapy for RPGR-associated retinal degeneration von Wu, Zhijian, Hiriyanna, Suja, Qian, Haohua, Mookherjee, Suddhasil, Campos, Maria M, Gao, Chun, Fariss, Robert, Sieving, Paul A, Li, Tiansen, Colosi, Peter, Swaroop, Anand

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Preclinical Dose-Escalation Study of Intravitreal AAV-RS1 Gene Therapy in a Mouse Model of X-linked Retinoschisis: Dose-Dependent Expression and Improved Retinal Structure and Func... von Bush, Ronald A, Zeng, Yong, Colosi, Peter, Kjellstrom, Sten, Hiriyanna, Suja, Vijayasarathy, Camasamudram, Santos, Maria, Li, Jinbo, Wu, Zhijian, Sieving, Paul A

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A CEP290 C-Terminal Domain Complements the Mutant CEP290 of Rd16 Mice In Trans and Rescues Retinal Degeneration von Mookherjee, Suddhasil, Chen, Holly Yu, Isgrig, Kevin, Yu, Wenhan, Hiriyanna, Suja, Levron, Rivka, Li, Tiansen, Colosi, Peter, Chien, Wade, Swaroop, Anand, Wu, Zhijian

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Long-term rescue of cone photoreceptor degeneration in retinitis pigmentosa 2 (RP2)-knockout mice by gene replacement therapy von Mookherjee, Suddhasil, Hiriyanna, Suja, Kaneshiro, Kayleigh, Li, Linjing, Li, Yichao, Li, Wei, Qian, Haohua, Li, Tiansen, Khanna, Hemant, Colosi, Peter, Swaroop, Anand, Wu, Zhijian

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Mutations on the External Surfaces of Adeno-Associated Virus Type 2 Capsids That Affect Transduction and Neutralization von Lochrie, Michael A, Tatsuno, Gwen P, Christie, Brian, McDonnell, Jennifer Wellman, Zhou, Shangzhen, Surosky, Richard, Pierce, Glenn F, Colosi, Peter

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Rd9 is a naturally occurring mouse model of a common form of retinitis pigmentosa caused by mutations in RPGR-ORF15 von Thompson, Debra A, Khan, Naheed W, Othman, Mohammad I, Chang, Bo, Jia, Lin, Grahek, Garrett, Wu, Zhijian, Hiriyanna, Suja, Nellissery, Jacob, Li, Tiansen, Khanna, Hemant, Colosi, Peter, Swaroop, Anand, Heckenlively, John R

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PDGF-CC blockade inhibits pathological angiogenesis by acting on multiple cellular and molecular targets von Hou, Xu, Kumar, Anil, Lee, Chunsik, Wang, Bin, Arjunan, Pachiappan, Dong, Lijin, Maminishkis, Arvydas, Tang, Zhongshu, Li, Yang, Zhang, Fan, Zhang, Shi-Zhuang, Wardega, Piotr, Chakrabarty, Sagarika, Liu, Baoying, Wu, Zhijian, Colosi, Peter, Fariss, Robert N., Lennartsson, Johan, Nussenblatt, Robert, Gutkind, J. Silvio, Cao, Yihai, Li, Xuri, Langer, Robert

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Application of in-vitro-cultured primary hepatocytes to evaluate species translatability and AAV transduction mechanisms of action von Liu, Su, Razon, Lisa, Ritchie, Olivia, Sihn, Choong-Ryoul, Handyside, Britta, Berguig, Geoffrey, Woloszynek, Jill, Zhang, Lening, Batty, Paul, Lillicrap, David, Agrawal, Vishal, Cortesio, Christa, Gebretsadik, Kahsay, Akeefe, Hassibullah, Colosi, Peter, Kim, Benjamin, Bunting, Stuart, Fong, Sylvia

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Gene Delivery to Skeletal Muscle Results in Sustained Expression and Systemic Delivery of a Therapeutic Protein von Kessler, Paul D., Podsakoff, Gregory M., Chen, Xiaojuan, McQuiston, Susan A., Colosi, Peter C., Matelis, Laura A., Kurtzman, Gary J., Byrne, Barry J.

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Separation of adeno-associated virus type 2 empty particles from genome containing vectors by anion-exchange column chromatography von Qu, Guang, Bahr-Davidson, Jennifer, Prado, Joseph, Tai, Alex, Cataniag, Floro, McDonnell, Jennifer, Zhou, Jingmin, Hauck, Bernd, Luna, Jac, Sommer, Jurg M., Smith, Peter, Zhou, Shangzhen, Colosi, Peter, High, Katherine A., Pierce, Glenn F., Wright, J. Fraser

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Ocular and systemic safety of a recombinant AAV8 vector for X-linked retinoschisis gene therapy: GLP studies in rabbits and Rs1-KO mice von Marangoni, Dario, Bush, Ronald A, Zeng, Yong, Wei, Lisa L, Ziccardi, Lucia, Vijayasarathy, Camasamudram, Bartoe, Joshua T, Palyada, Kiran, Santos, Maria, Hiriyanna, Suja, Wu, Zhijian, Colosi, Peter, Sieving, Paul A

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Let’s Make Rhode Island a State Where the Vulnerable are Loved von Colosi, Peter J.

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Suggestion Is Coercion When It Comes to Death von Colosi, Peter J.

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Novel Caprine Adeno-Associated Virus (AAV) Capsid (AAV-Go.1) Is Closely Related to the Primate AAV-5 and Has Unique Tropism and Neutralization Properties von Arbetman, Alejandra E, Lochrie, Michael, Zhou, Shangzhen, Wellman, Jennifer, Scallan, Ciaran, Doroudchi, Mohammad M, Randlev, Britta, Patarroyo-White, Susannah, Liu, Tongyao, Smith, Peter, Lehmkuhl, Howard, Hobbs, Lea Ann, Pierce, Glenn F, Colosi, Peter

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Bill of rights for children von Colosi, Peter J, Williams, William V

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Dietrich von Hildebrand, The Encyclical Humanae Vitae: A Sign of Contradiction. An Essay on Birth Control and Catholic Conscience von Colosi, Peter J.

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