Correction of enzymatic and lysosomal storage defects in Fabry mice by adenovirus-mediated gene transfer von ZIEGLER, R. J, YEW, N. S, LI, C, CHERRY, M, BERTHELETTE, P, ROMANCZUK, H, IOANNOU, Y. A, ZEIDNER, K. M, DESNICK, R. J, CHENG, S. H

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Correction of the nonlinear dose response improves the viability of adenoviral vectors for gene therapy of Fabry disease von ZIEGLER, Robin J, LI, Chester, CHENG, Seng H, CHERRY, Maribeth, YUNXIANG ZHU, HEMPEL, Donna, VAN ROOIJEN, Nico, IOANNOU, Yiannis A, DESNICK, Robert J, GOLDBERG, Mark A, YEW, Nelson S

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Optimization of plasmid vectors for high-level expression in lung epithelial cells von Yew, N S, Wysokenski, D M, Wang, K X, Ziegler, R J, Marshall, J, McNeilly, D, Cherry, M, Osburn, W, Cheng, S H

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Correction of the Biochemical and Functional Deficits in Fabry Mice Following AAV8–mediated Hepatic Expression of α-galactosidase A von Ziegler, Robin J, Cherry, Maribeth, Barbon, Christine M, Li, Chester, Bercury, Scott D, Armentano, Donna, Desnick, Robert J, Cheng, Seng H

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AAV2 Vector Harboring a Liver-Restricted Promoter Facilitates Sustained Expression of Therapeutic Levels of α-Galactosidase A and the Induction of Immune Tolerance in Fabry Mice von Ziegler, Robin J, Lonning, Scott M, Armentano, Donna, Li, Chester, Souza, David W, Cherry, Maribeth, Ford, Christine, Barbon, Christine M, Desnick, Robert J, Gao, Guangping, Wilson, James M, Peluso, Richard, Godwin, Simon, Carter, Barrie J, Gregory, Richard J, Wadsworth, Samuel C, Cheng, Seng H

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AAV8-Mediated Hepatic Expression of Acid Sphingomyelinase Corrects the Metabolic Defect in the Visceral Organs of a Mouse Model of Niemann-Pick Disease von Barbon, Christine M, Ziegler, Robin J, Li, Chester, Armentano, Donna, Cherry, Maribeth, Desnick, Robert J, Schuchman, Edward H, Cheng, Seng H

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Correction of the Biochemical and Functional Deficits in Fabry Mice Following AAV8-mediated Hepatic Expression of -galactosidase A von Ziegler, Robin J, Cherry, Maribeth, Barbon, Christine M, Li, Chester, Bercury, Scott D, Armentano, Donna, Desnick, Robert J, Cheng, Seng H

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Adenovirus-Transduced Lung as a Portal for Delivering α-Galactosidase A into Systemic Circulation for Fabry Disease von Li, Chester, Ziegler, Robin J., Cherry, Maribeth, Lukason, Michael, Desnick, Robert J., Yew, Nelson S., Cheng, Seng H.

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A concentrated and stable aerosol formulation of cationic lipid:DNA complexes giving high-level gene expression in mouse lung von Eastman, S J, Lukason, M J, Tousignant, J D, Murray, H, Lane, M D, St George, J A, Akita, G Y, Cherry, M, Cheng, S H, Scheule, R K

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Adenovirus-Transduced Lung as a Portal for Delivering [alpha]-Galactosidase A into Systemic Circulation for Fabry Disease von Li, Chester, Ziegler, Robin J, Cherry, Maribeth, Lukason, Michael, Desnick, Robert J, Yew, Nelson S, Cheng, Seng H

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AAV2 Vector Harboring a Liver-Restricted Promoter Facilitates Sustained Expression of Therapeutic Levels of [alpha]-Galactosidase A and the Induction of Immune Tolerance in Fabry M... von Ziegler, Robin J, Lonning, Scott M, Armentano, Donna, Li, Chester, Souza, David W, Cherry, Maribeth, d, Christine, Barbon, Christine M, Desnick, Robert J, Gao, Guangping, Wilson, James M, Peluso, Richard, Godwin, Simon, Carter, Barrie J, Gregory, Richard J, Wadsworth, Samuel C, Cheng, Seng H

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Correction of the Biochemical and Functional Deficits in Fabry Mice Following AAV8-mediated Hepatic Expression of α-galactosidase A von Ziegler, Robin J, Cherry, Maribeth, Barbon, Christine M, Li, Chester, Bercury, Scott D, Armentano, Donna, Desnick, Robert J, Cheng, Seng H

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The Effectiveness of Using Gadgets on Students’ Learning Interests and Academic Performance von Madarcos, Cherry Ann, De Vera, Mercy Grace, Manlavi, Maribeth

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