The long terminal repeat negative control region is a critical element for insertional oncogenesis after gene transfer into hematopoietic progenitors with Moloney murine leukemia v... von Ikawa, Y, Uchiyama, T, Jagadeesh, G J, Candotti, F

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OP0007 Blood Interferon Signature as a Screening For Type I Interferonopathies in Children With Early-Onset SLE and Vasculopathy von Volpi, S., Santori, E., Picco, P., Rice, G., Caorsi, R., Martini, A., Crow, Y., Gattorno, M., Candotti, F.

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A-153 Primary cutaneous T-cell lymphoma not otherwise specified (NOS) uncovering a novel RAB27A variant in Griscelli syndrome type 2 von Blanchard, G., Atallah, I., Fehrenbacher, B., Schaller, M., Candotti, F., Guenova, E.

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Development of IgA nephropathy-like glomerulonephritis associated with Wiskott–Aldrich syndrome protein deficiency von Shimizu, M, Nikolov, N.P, Ueno, K, Ohta, K, Siegel, R.M, Yachie, A, Candotti, F

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Identification of type I interferonopathies using blood interferon signature: the experience of a pediatric rheumatology center von Volpi, S, Santori, E, Picco, P, Rice, G, Caorsi, R, Martini, A, Crow, Y, Candotti, F, Gattorno, M

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Somatic Mosaicism Caused by Monoallelic Reversion of a Mutation in T Cells of a Patient with ADA‐SCID and the Effects of Enzyme Replacement Therapy on the Revertant Phenotype von Moncada‐Vélez, M., Vélez‐Ortega, A., Orrego, J., Santisteban, I., Jagadeesh, J., Olivares, M., Olaya, N., Hershfield, M., Candotti, F., Franco, J.

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Clinical efficacy of SARS‐CoV‐2 Omicron‐neutralizing antibodies in immunoglobulin preparations for the treatment of agammaglobulinemia in patients with primary antibody deficiency... von Karbiener, Michael, Kindle, Gerhard, Meyts, Isabelle, Seppänen, Mikko R. J., Candotti, Fabio, Kamieniak, Marta, Ilk, Reinhard, Kreil, Thomas R., Seidel, Markus G.

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Lentiviral-mediated gene transfer into human lymphocytes: role of HIV-1 accessory proteins von Chinnasamy, Dhanalakshmi, Chinnasamy, Nachimuthu, Enriquez, Melissa J., Otsu, Makoto, Morgan, Richard A., Candotti, Fabio

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Efficient gene transfer to human peripheral blood monocyte-derived dendritic cells using human immunodeficiency virus type 1-based lentiviral vectors von CHINNASAMY, Nachimuthu, CHINNASAMY, Dhanalakshmi, TOSO, John F, LAPOINTE, Rejean, CANDOTTI, Fabio, MORGAN, Richard A, HWU, Patrick

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Signaling networks in B cell development and related therapeutic strategies von Ren, Anwen, Sun, Jianxuan, Yin, Wei, Westerberg, Lisa S., Miller, Heather, Lee, Pamela, Candotti, Fabio, Guan, Fei, Lei, Jiahui, Gong, Quan, Chen, Yan, Liu, Chaohong

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Immunodeficiencies: Injecting some safety into SCID gene therapy? von Candotti, F, Roifman, C, Puck, J M

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Engraftment potential of human amnion and chorion cells derived from term placenta von Bailo, Marco, Soncini, Maddalena, Vertua, Elsa, Signoroni, Patrizia Bonassi, Sanzone, Silvia, Lombardi, Guerino, Arienti, Davide, Calamani, Francesca, Zatti, Daniela, Paul, Petra, Albertini, Alberto, Zorzi, Fausto, Cavagnini, Angelo, Candotti, Fabio, Wengler, Georg S, Parolini, Ornella

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Novel Discoveries in Immune Dysregulation in Inborn Errors of Immunity von Ren, Anwen, Yin, Wei, Miller, Heather, Westerberg, Lisa S, Candotti, Fabio, Park, Chan-Sik, Lee, Pamela, Gong, Quan, Chen, Yan, Liu, Chaohong

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Retrovirus-mediated WASP gene transfer corrects defective actin polymerization in B cell lines from Wiskott-Aldrich syndrome patients carrying 'null' mutations von CANDOTTI, F, FACCHETTI, F, BLANZUOLI, L, STEWART, D. M, NELSON, D. I, BLAESE, R. M

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Somatic mosaicism in primary immune deficiencies von Wada, Taizo, Candotti, Fabio

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Reconstitution of lymphoid development and function in ZAP-70–deficient mice following gene transfer into bone marrow cells von Otsu, Makoto, Steinberg, Marcos, Ferrand, Christophe, Merida, Peggy, Rebouissou, Cosette, Tiberghien, Pierre, Taylor, Naomi, Candotti, Fabio, Noraz, Nelly

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N-WASP is required for B-cell–mediated autoimmunity in Wiskott-Aldrich syndrome von Volpi, Stefano, Santori, Elettra, Abernethy, Katrina, Mizui, Masayuki, Dahlberg, Carin I.M., Recher, Mike, Capuder, Kelly, Csizmadia, Eva, Ryan, Douglas, Mathew, Divij, Tsokos, George C., Snapper, Scott, Westerberg, Lisa S., Thrasher, Adrian J., Candotti, Fabio, Notarangelo, Luigi D.

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Gene therapy for immunodeficiency von Candotti, F

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Jak3, severe combined immunodeficiency, and a new class of immunosuppressive drugs von Pesu, Marko, Candotti, Fabio, Husa, Matthew, Hofmann, Sigrun R., Notarangelo, Luigi D., O'Shea, John J.

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Expansion of Hepatic and Hematopoietic Stem Cells Utilizing Mouse Embryonic Liver Explants von Monga, Satdarshan P. S., Tang, Yi, Candotti, Fabio, Rashid, Asif, Wildner, Oliver, Mishra, Bibhuti, Iqbal, Shareen, Mishra, Lopa

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