P3.11 Antisense oligomer mediated retention of SMN2 intron and exon 7 leads to a novel SMN transcript and increased functional SMN protein in Spinal Muscular Atrophy fibroblasts von Mitrpant, C, Price, L, Johnsen, R.D, Burghes, A.H, Fletcher, S, Wilton, S.D

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P3.32 Exon/intron 7 inclusion: an alternative mode of splice intervention in spinal muscular atrophy fibroblasts von Mitrpant, C, Fragall, C.T, Johnsen, R, Burghes, A.H, Fletcher, S, Wilton, S.D

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T.P.1.08 The use of antisense oligomer for splice switching in spinal muscular atrophy fibroblasts von Mitrpant, C, Fragall, C, Johnsen, R, Burghes, A.H, Fletcher, S, Wilton, S.D

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