Safety, tolerability, and preliminary efficacy of an IGF-1 mimetic in patients with spinal and bulbar muscular atrophy: a randomised, placebo-controlled trial von Grunseich, Christopher, Miller, Ram, Swan, Therese, Glass, David J, El Mouelhi, Mohamed, Fornaro, Mara, Petricoul, Olivier, Vostiar, Igor, Roubenoff, Ronenn, Meriggioli, Matthew N, Kokkinis, Angela, Guber, Robert D, Budron, Maher S, Vissing, John, Soraru, Gianni, Mozaffar, Tahseen, Ludolph, Albert, Kissel, John T, Fischbeck, Kenneth H, Grunseich, Christopher, Miller, Ram, Swan, Therese, Glass, David J, Mouelhi, Mohamed El, Fornaro, Mara, Petricoul, Olivier, Vostiar, Igor, Roubenoff, Ronenn, Meriggioli, Matthew N, Dahlqvist, Julia, Witting, Nanna, Vissing, John, Martinelli, Ilaria, Querin, Giorgia, Soraru, Gianni, Goyal, Namita A, Cash, Tiyonnoh M, Minton, Brian, Mozaffar, Tahseen, Rosenbohm, Angela, Weiland, Ulrike, Weydt, Patrick, Ludolph, Albert, Chelnick, Sharon, Iyadurai, Stanley, King, Wendy, Kissel, John T, Budron, Maher S, Guber, Robert D, Kokkinis, Angela, Fischbeck, Kenneth H

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Nucleocytoplasmic transport defect in a North American patient with ALS8 von Guber, Robert D., Schindler, Alice B., Budron, Maher S., Chen, Ke‐lian, Li, Yuebing, Fischbeck, Kenneth H., Grunseich, Christopher

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Nucleocytoplasmic transport defect in a North American patient with ALS 8 von Guber, Robert D., Schindler, Alice B., Budron, Maher S., Chen, Ke‐lian, Li, Yuebing, Fischbeck, Kenneth H., Grunseich, Christopher

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A randomized, placebo-controlled study to evaluate the safety, tolerability, and preliminary efficacy of an IGF-1 mimetic in patients with spinal and bulbar muscular atrophy von Grunseich, Christopher, Miller, Ram, Swan, Therese, Glass, David J, El Mouelhi, Mohamed, Fornaro, Mara, Petricoul, Olivier, Vostiar, Igor, Roubenoff, Ronenn, Meriggioli, Matthew N, Kokkinis, Angela, Guber, Robert D, Budron, Maher S, Vissing, John, Soraru, Gianni, Mozaffar, Tahseen, Ludolph, Albert, Kissel, John T, Fischbeck, Kenneth H

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