Long-Term Preservation of Cones and Improvement in Visual Function Following Gene Therapy in a Mouse Model of Leber Congenital Amaurosis Caused by Guanylate Cyclase-1 Deficiency von MIHELEC, Marija, PEARSON, Rachael A, ROBBIE, Scott J, BUCH, Prateek K, AZAM, Selina A, BAINBRIDGE, James W. B, SMITH, Alexander J, ALI, Robin R

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In contrast to AAV-mediated Cntf expression, AAV-mediated Gdnf expression enhances gene replacement therapy in rodent models of retinal degeneration von Buch, Prateek K, MacLaren, Robert E, Durán, Yanaí, Balaggan, Kamaljit S, MacNeil, Angus, Schlichtenbrede, Frank C, Smith, Alexander J, Ali, Robin R

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Dominant cone-rod dystrophy: a mouse model generated by gene targeting of the GCAP1/Guca1a gene von Buch, Prateek K, Mihelec, Marija, Cottrill, Phillippa, Wilkie, Susan E, Pearson, Rachael A, Duran, Yanai, West, Emma L, Michaelides, Michel, Ali, Robin R, Hunt, David M

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Gene Replacement Therapy Rescues Photoreceptor Degeneration in a Murine Model of Leber Congenital Amaurosis Lacking RPGRIP von Pawlyk, Basil S, Smith, Alexander J, Buch, Prateek K, Adamian, Michael, Hong, Dong-Hyun, Sandberg, Michael A, Ali, Robin R, Li, Tiansen

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CNTF gene transfer protects ganglion cells in rat retinae undergoing focal injury and branch vessel occlusion von MacLaren, Robert E., Buch, Prateek K., Smith, Alexander J., Balaggan, Kamaljit S., MacNeil, Angus, Taylor, Jeremy S., Osborne, Neville N., Ali, Robin R.

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Local administration of an adeno-associated viral vector expressing IL-10 reduces monocyte infiltration and subsequent photoreceptor damage during experimental autoimmune uveitis von Broderick, Cathryn A, Smith, Alexander J, Balaggan, Kam S, Georgiadis, Anastasios, Georgarias, Anastasios, Buch, Prateek K, Trittibach, Peter C, Barker, Susie E, Sarra, Gian-Marco, Thrasher, Adrian J, Dick, Andrew D, Ali, Robin R

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Corrigendum to "Local Administration of an Adeno-Associated Viral Vector Expressing IL-10 Reduces Monocyte Infiltration and Subsequent Photoreceptor Damage During Experimental Auto... von Broderick, Cathryn A, Smith, Alexander J, Balaggan, Kam S, Georgiadis, Anastasios, Buch, Prateek K, Trittibach, Peter C, Barker, Susie E, Sarra, Gian-Marco, Thrasher, Adrian J, Dick, Andrew D, Ali, Robin R

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Gene replacement therapy rescues photoreceptor degeneration in a murine model of Leber congenital amaurosis lacking RPGRIP von Pawlyk, Basil S, Smith, Alexander J, Buch, Prateek K, Adamian, Michael, Hong, Dong-Hyun, Sandberg, Michael A, Ali, Robin R, Li, Tiansen

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Long-term preservation of cones and improvement in visual function following gene therapy in a mouse model of Leber congenital amaurosis caused by guanylate cyclase-1 deficiency von Mihelec, Marija, Pearson, Rachael A, Robbie, Scott J, Buch, Prateek K, Azam, Selina A, Bainbridge, James W.B, Smith, Alexander J, Ali, Robin R

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Effective gene therapy with nonintegrating lentiviral vectors von Yáñez-Muñoz, Rafael J, Balaggan, Kamaljit S, MacNeil, Angus, Howe, Steven J, Schmidt, Manfred, Smith, Alexander J, Buch, Prateek, MacLaren, Robert E, Anderson, Patrick N, Barker, Susie E, Duran, Yanai, Bartholomae, Cynthia, von Kalle, Christof, Heckenlively, John R, Kinnon, Christine, Ali, Robin R, Thrasher, Adrian J

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