Real-world outcomes from a series of patients with late onset Pompe disease who switched from alglucosidase alfa to avalglucosidase alfa von Carter, Chris, Boggs, Tracy, Case, Laura E, Kishnani, Priya

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Development of high sustained anti-drug antibody titers and corresponding clinical decline in a late-onset Pompe disease patient after 11+ years on enzyme replacement therapy von Kim, Katherine H., Desai, Ankit K., Vucko, Erika R., Boggs, Tracy, Kishnani, Priya S., Burton, Barbara K.

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A retrospective longitudinal study and comprehensive review of adult patients with glycogen storage disease type III von Hijazi, Ghada, Paschall, Anna, Young, Sarah P., Smith, Brian, Case, Laura E., Boggs, Tracy, Amarasekara, Sathya, Austin, Stephanie L., Pendyal, Surekha, El-Gharbawy, Areeg, Deak, Kristen L., Muir, Andrew J., Kishnani, Priya S.

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Randomized controlled trial of brief cognitive-behavioural interventions among regular users of amphetamine von Baker, Amanda, Boggs, Tracy G., Lewin, Terry J.

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Whole‐body magnetic resonance imaging in late‐onset Pompe disease: Clinical utility and correlation with functional measures von Khan, Aleena A., Boggs, Tracy, Bowling, Michael, Austin, Stephanie, Stefanescu, Mihaela, Case, Laura, Kishnani, Priya S.

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Whole-body MRI in late-onset Pompe disease: Clinical utility and correlation with functional measures von Khan, Aleena A., Boggs, Tracy, Bowling, Michael, Austin, Stephanie, Stefanescu, Mihaela, Case, Laura, Kishnani, Priya S.

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Physical therapy assessment and whole-body magnetic resonance imaging findings in children with glycogen storage disease type IIIa: A clinical study and review of the literature von Paschall, Anna, Khan, Aleena A., Enam, Syed Faaiz, Boggs, Tracy, Hijazi, Ghada, Bowling, Michael, Austin, Stephanie, Case, Laura E., Kishnani, Priya

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A RETROSPECTIVE LONGITUDINAL STUDY AND COMPREHENSIVE REVIEW OF ADULT PATIENTS WITH GLYCOGEN STORAGE DISEASE TYPE III von Hijazi, Ghada, Paschall, Anna, Young, Sarah P., Smith, Brian, Case, Laura E., Boggs, Tracy, Amarasekara, Sathya, Austin, Stephanie L., Pendyal, Surekha, El-Gharbawy, Areeg, Deak, Kristen L., Muir, Andrew J., Kishnani, Priya S.

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Quantitative whole‐body magnetic resonance imaging in children with Pompe disease: Clinical tools to evaluate severity of muscle disease von Fernandes, Samuela A., Khan, Aleena A., Boggs, Tracy, Bowling, Michael, Austin, Stephanie, Stefanescu, Mihaela, Case, Laura, Kishnani, Priya S.

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Characteristics of regular amphetamine users and implications for treatment von Baker, Tracy G. Boggs, Terry J. Lewin, Amanda

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Characteristics of regular amphetamine users and implications for treatment von Baker, Amanda, Boggs, Tracy G., Lewin, Terry J.

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Randomized Controlled Trial of Brief Cognitive-Behavioural Interventions among Regular Users of Amphetamine von Baker, Amanda, Boggs, Tracy G, Lewin, Terry J

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Making them believe von Boggs, Tracy

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Development of high sustained anti-drug antibody titers and corresponding clinical decline in a late-onset Pompe disease patient after 11+ years on enzyme replacement therapy von Kim, Katherine H, Desai, Ankit K, Vucko, Erika R, Boggs, Tracy, Kishnani, Priya S, Burton, Barbara K

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Making them believe: consumers know lower-sodium products to be better for them, but how can manufacturers convince them on taste? von Boggs, Tracy

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Nine-year prospective efficacy and safety of brain-responsive neurostimulation for focal epilepsy von Nair, Dileep R., Laxer, Kenneth D., Weber, Peter B., Murro, Anthony M., Park, Yong D., Barkley, Gregory L., Smith, Brien J., Gwinn, Ryder P., Doherty, Michael J., Noe, Katherine H., Zimmerman, Richard S., Bergey, Gregory K., Anderson, William S., Heck, Christianne, Liu, Charles Y., Lee, Ricky W., Sadler, Toni, Duckrow, Robert B., Hirsch, Lawrence J., Wharen, Robert E., Tatum, William, Srinivasan, Shraddha, McKhann, Guy M., Agostini, Mark A., Alexopoulos, Andreas V., Jobst, Barbara C., Roberts, David W., Salanova, Vicenta, Witt, Thomas C., Cash, Sydney S., Cole, Andrew J., Worrell, Gregory A., Lundstrom, Brian N., Edwards, Jonathan C., Halford, Jonathan J., Spencer, David C., Ernst, Lia, Skidmore, Christopher T., Sperling, Michael R., Miller, Ian, Geller, Eric B., Berg, Michel J., Fessler, A. James, Rutecki, Paul, Goldman, Alica M., Mizrahi, Eli M., Gross, Robert E., Shields, Donald C., Schwartz, Theodore H., Labar, Douglas R., Fountain, Nathan B., Elias, W. Jeff, Olejniczak, Piotr W., Villemarette-Pittman, Nicole R., Eisenschenk, Stephan, Roper, Steven N., Boggs, Jane G., Courtney, Tracy A., Sun, Felice T., Seale, Cairn G., Miller, Kathy L., Skarpaas, Tara L., Morrell, Martha J.

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Provider‐to‐provider telehealth for sepsis patients in a cohort of rural emergency departments von Mohr, Nicholas M., Young, Tracy, Vakkalanka, J. Priyanka, Carter, Knute D., Shane, Dan M., Ullrich, Fred, Schuette, Allison R., Mack, Luke J., DeJong, Katie, Bell, Amanda, Pals, Mark, Camargo, Carlos A., Zachrison, Kori S., Boggs, Krislyn M., Skibbe, Adam, Ward, Marcia M.

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Climate Litigation and Justice in Africa von Rebelo, Pia (City, University of London), Rebelo, Xavier, van Wyk, Sanita, Obani, Pedi (University of Bradford), Ekhator, Eghosa O. (University of Derby), Okumagba, Edward O. (Delta State University), Bouwer, Kim (University of Durham), Etemire, Uzuazo (University of Port Harcourt), Field, Tracy-Lynn (University of the Witwatersrand)

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Standardized practices for RNA diagnostics using clinically accessible specimens reclassifies 75% of putative splicing variants von Bommireddipalli, Shobhana, Ades, Lesley, Archibald, Alison D., Berman, Yemima, Bojadzieva, Jasmina, Brown, Natasha J., Bryen, Samantha J., Engel, Amanda, Ewans, Lisa J., Fennell, Andrew, Freckmann, Mary-Louise, Gear, Russell, Goel, Himanshu, Goh, Shuxiang, Harraway, James, Higgins, Megan, Ho, Gladys, Hunter, Matthew F., Joshi, Himanshu, Krzesinski, Emma, Leventer, Richard J., Macaskill, Steven, McCarthy, Hugh J., McLean, Alison, Patel, Chirag, Regan, Matthew, Schindler, Tim, Tantsis, Esther, Tchan, Michel C., van Spaendonck-Zwarts, Karin, White, Susan M., Williams, Mark G., Wright, Dale C., Yap, Patrick, Yeung, Alison, Jones, Kristi J., Cooper, Sandra T., Arts, Peer, Barnett, Christopher, Beshay, Victoria, Blombery, Piers, Boggs, Kirsten, Branford, Susan, Bryen, Samantha J., Canson, Daffodil, Chew, Edward, Chong, Belinda, Chung, Seo-Kyung, Clark, Mike, Compton, Alison, Corbett, Mark, Davis, Mark R., Dudding, Tracy, Ewans, Lisa J., Eyras, Eduardo, Fellowes, Andrew, Field, Michael, Freckmann, Mary-Louise, Gaff, Clara, Galea, Melanie, Hanna, Bernadette, Harraway, James, Hayashi, Rippei, Henderson, Alex, Jackson, Matilda, Jones, Kristi J., Wong, Justin Jong-Leong, Joshi, Himanshu, Krzesinski, Emma, Kumble, Smitha, Laing, Nigel, Lau, Chiyan, Lee, Eric, Lundie, Ben, Mallawaarachchi, Amali, McLean, Alison, Meldrum, Cliff, Mina, Kym, Mowat, David, Oshlack, Alicia, Parsons, Michael, Patel, Chirag, Pinner, Jason R., Quinn, Michael, Ravenscroft, Gina, Regan, Matthew, Ronan, Anne, Sadedin, Simon, Schreiber, Andreas, Scott, Rodney, Simons, Cas, Smyth, Renee, Thompson, Bryony A., Thorburn, David, Trent, Ronald, Tudini, Emma, Wallis, Mathew, Wilson, Meredith J., Winship, Ingrid, Yeung, Alison

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Initial Results from Summit: An On-going, 3-Part, Multi-Center, Randomized, Double-Blind, Placebo-Controlled Phase 2 Clinical Study of Bezuclastinib in Adult Patients with NonAdvan... von Modena, Brian, Rein, Lindsay A.M., Oh, Stephen, DeAngelo, Daniel, Hunter, Anthony, Akin, Cem, Castells, Mariana, Manning, Michael, Herrscher, Richard, Ustun, Celalettin, Kirshenbaum, Arnold, Livideanu, Cristina Bulai, Boggs, Nathan, Yi, Cecilia Arana, Siebenhaar, Frank, George, Tracy, Exter, Benjamin, Zhang, Jenna, Pilla, Amanda, Jolin, Hina, Easton, Rachael, Bose, Prithviraj

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