Intracerebroventricular delivery of glucocerebrosidase reduces substrates and increases lifespan in a mouse model of neuronopathic Gaucher disease von Cabrera-Salazar, M.A., Bercury, S.D., Ziegler, R.J., Marshall, J., Hodges, B.L., Chuang, W.-L., Pacheco, J., Li, L., Cheng, S.H., Scheule, R.K.

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289 Beyond SION-638: a novel series of highly potent stabilizers of the first nucleotide binding domain enables full correction of ΔF508-CFTR in a dual combination with Sionna CFTR... von Hurlbut, G., Altmann, S., Barrague, M., Bercury, S., Duguid, M., Foley, J., Gao, Z., Hunnicutt, A., Hurlbut-Lesk, O., Liao, J., Munson, M., Stepp, D., Macor, J.

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EPS3.10 Novel CFTR modulator combinations directly address the ΔF508-CFTR NBD1 stability defect and enable full CFTR correction von Hurlbut, G., Altmann, S., Barrague, M., Bercury, S., Duguid, M., Easter, A., Foley, J., Gao, Z., Hewitt, M., Hunnicutt, A., Hurlbut-Lesk, O., Stepp, D., Liao, J., Maharoof, U., McKee, C., Munson, M., Macor, J.

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662 Novel cystic fibrosis transmembrane conductance regulator modulator combinations that address the first nucleotide binding domain defect central to ΔF508 dysfunction enable ful... von Hurlbut, G., Altmann, S., Barrague, M., Bercury, S., Duguid, M., Easter, A., Foley, J., Fretland, J., Gao, Z., Hewitt, M., Hunnicutt, A., Liao, J., Maharoof, U., McKee, C., Munson, M., Macor, J.

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M.P.5.10 Efforts to enhance AAV8-mediated gene therapy of Pompe disease von Ziegler, R, Bercury, S, Zhu, Y, Foley, J, Gumlaw, N, Koeberl, D, Scheule, R, Cheng, S

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Ability of Adeno-Associated Virus Serotype 8-Mediated Hepatic Expression of Acid α-Glucosidase to Correct the Biochemical and Motor Function Deficits of Presymptomatic and Symptoma... von ZIEGLER, Robin J, BERCURY, Scott D, CHENG, Seng H, FIDLER, Jonathan, ZHAO, Michael A, FOLEY, Joseph, TAKSIR, Tatyana V, RYAN, Susan, HODGES, Bradley L, SCHEULE, Ronald K, SHIHABUDDIN, Lamya S

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Molecular analysis of the Doppia transposable element of maize von Bercury, S D, Panavas, T, Irenze, K, Walker, E L

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Inhibition of Pulmonary Fibrosis by the Chemokine IP-10/CXCL10 von Tager, Andrew M, Kradin, Richard L, LaCamera, Peter, Bercury, Scott D, Campanella, Gabriele S. V, Leary, Carol P, Polosukhin, Vasiliy, Zhao, Long-Hai, Sakamoto, Hideo, Blackwell, Timothy S, Luster, Andrew D

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Leukotriene B sub(4) receptor BLT1 mediates early effector T cell recruitment von Tager, A M, Bromley, S K, Medoff, B D, Islam, SA, Bercury, S D, Friedrich, E B, Carafone, AD, Gerszten, R E, Luster, AD

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BLTR mediates leukotriene B(4)-induced chemotaxis and adhesion and plays a dominant role in eosinophil accumulation in a murine model of peritonitis von Tager, A M, Dufour, J H, Goodarzi, K, Bercury, S D, von Andrian, U H, Luster, A D

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BLTR Mediates Leukotriene B sub(4)-induced Chemotaxis and Adhesion and Plays a Dominant Role in Eosinophil Accumulation in a Murine Model of Peritonitis von Tager, A M, Dufour, J H, Goodarzi, K, Bercury, S D, von Andrian, UH, Luster, AD

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Dynamics and Mechanisms of CNS Myelination von Bercury, Kathryn K., Macklin, Wendy B.

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Systemic delivery of a glucosylceramide synthase inhibitor reduces CNS substrates and increases lifespan in a mouse model of type 2 Gaucher disease von Cabrera-Salazar, Mario A, Deriso, Matthew, Bercury, Scott D, Li, Lingyun, Lydon, John T, Weber, William, Pande, Nilesh, Cromwell, Mandy A, Copeland, Diane, Leonard, John, Cheng, Seng H, Scheule, Ronald K

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Mammalian target of rapamycin promotes oligodendrocyte differentiation, initiation and extent of CNS myelination von Wahl, Stacey E, McLane, Lauren E, Bercury, Kathryn K, Macklin, Wendy B, Wood, Teresa L

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Olig1 function is required for oligodendrocyte differentiation in the mouse brain von Dai, Jinxiang, Bercury, Kathryn K, Ahrendsen, Jared T, Macklin, Wendy B

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Conditional ablation of raptor or rictor has differential impact on oligodendrocyte differentiation and CNS myelination von Bercury, Kathryn K, Dai, JinXiang, Sachs, Hilary H, Ahrendsen, Jared T, Wood, Teresa L, Macklin, Wendy B

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Olig1 Acetylation and Nuclear Export Mediate Oligodendrocyte Development von Dai, Jinxiang, Bercury, Kathryn K, Jin, Weilin, Macklin, Wendy B

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Interaction of mTOR and Erk1/2 signaling to regulate oligodendrocyte differentiation von Dai, JinXiang, Bercury, Kathryn K., Macklin, Wendy B.

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Iminosugar-based inhibitors of glucosylceramide synthase increase brain glycosphingolipids and survival in a mouse model of Sandhoff disease von Ashe, Karen M, Bangari, Dinesh, Li, Lingyun, Cabrera-Salazar, Mario A, Bercury, Scott D, Nietupski, Jennifer B, Cooper, Christopher G F, Aerts, Johannes M F G, Lee, Edward R, Copeland, Diane P, Cheng, Seng H, Scheule, Ronald K, Marshall, John

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A New Model of Cuprizone-Mediated Demyelination/Remyelination von Sachs, Hilary H., Bercury, Kathryn K., Popescu, Daniela C., Narayanan, S. Priya, Macklin, Wendy B.

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