Monobac System–A Single Baculovirus for the Production of rAAV von Galibert, Lionel, Jacob, Aurélien, Savy, Adrien, Dickx, Yohann, Bonnin, Delphine, Lecomte, Christophe, Rivollet, Lise, Sanatine, Peggy, Boutin Fontaine, Marjorie, Le Bec, Christine, Merten, Otto-Wilhelm

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CUG-BP1/CELF1 requires UGU-rich sequences for high-affinity binding von Marquis, Julien, Paillard, Luc, Audic, Yann, Cosson, Bertrand, Danos, Olivier, Le Bec, Christine, Osborne, H Beverley

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Systemic AAV8-Mediated Gene Therapy Drives Whole-Body Correction of Myotubular Myopathy in Dogs von Mack, David L., Poulard, Karine, Goddard, Melissa A., Latournerie, Virginie, Snyder, Jessica M., Grange, Robert W., Elverman, Matthew R., Denard, Jérôme, Veron, Philippe, Buscara, Laurine, Le Bec, Christine, Hogrel, Jean-Yves, Brezovec, Annie G., Meng, Hui, Yang, Lin, Liu, Fujun, O’Callaghan, Michael, Gopal, Nikhil, Kelly, Valerie E., Smith, Barbara K., Strande, Jennifer L., Mavilio, Fulvio, Beggs, Alan H., Mingozzi, Federico, Lawlor, Michael W., Buj-Bello, Ana, Childers, Martin K.

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Practical utilization of recombinant AAV vector reference standards: focus on vector genomes titration by free ITR qPCR von D'Costa, Susan, Blouin, Veronique, Broucque, Frederic, Penaud-Budloo, Magalie, François, Achille, Perez, Irene C, Le Bec, Christine, Moullier, Philippe, Snyder, Richard O, Ayuso, Eduard

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Preclinical Development of an AAV8-hUGT1A1 Vector for the Treatment of Crigler-Najjar Syndrome von Collaud, Fanny, Bortolussi, Giulia, Guianvarc'h, Laurence, Aronson, Sem J, Bordet, Thierry, Veron, Philippe, Charles, Severine, Vidal, Patrice, Sola, Marcelo Simon, Rundwasser, Stephanie, Dufour, Delphine G, Lacoste, Florence, Luc, Cyril, Wittenberghe, Laetitia V, Martin, Samia, Le Bec, Christine, Bosma, Piter J, Muro, Andres F, Ronzitti, Giuseppe, Hebben, Matthias, Mingozzi, Federico

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Internal Ribosome Entry Site Structural Motifs Conserved among Mammalian Fibroblast Growth Factor 1 Alternatively Spliced mRNAs von Martineau, Yvan, Le Bec, Christine, Monbrun, Laurent, Allo, Valérie, Chiu, Ing-Ming, Danos, Olivier, Moine, Hervé, Prats, Hervé, Prats, Anne-Catherine

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MyD88 signaling in B cells regulates the production of Th1-dependent antibodies to AAV von Sudres, Muriel, Ciré, Séverine, Vasseur, Virginie, Brault, Léa, Da Rocha, Sylvie, Boisgérault, Florence, Le Bec, Christine, Gross, David Alexandre, Blouin, Véronique, Ryffel, Bernard, Galy, Anne

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498. Prolonged Benefit from Systemic rAAV8 in a Canine Model of Myotubular Myopathy von Elverman, Matthew, Mack, David, Goddard, Melissa, Snyder, Jessica, Grange, Robert, Poulard, Karine, Latournerie, Virginie, Veron, Philippe, Buscara, Laurine, Bec, Christine Le, Martin, Samia, Mavilio, Fulvio, Mingozzi, Federico, Meng, Hui, Lawlor, Michael, Beggs, Alan, Buj-Bello, Anna, Childers, Martin

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Systemic AAV8-Mediated Gene Therapy Drives Whole-Body Correction of Myotubular Myopathy in Dogs von Mack, David, Poulard, Karine, Goddard, Melissa, Latournerie, Virginie, Snyder, Jessica, Grange, Robert, Elverman, Matthew, Denard, Jérôme, Veron, Philippe, Buscara, Laurine, Le Bec, Christine, Hogrel, Jean-Yves, Brezovec, Annie, Meng, Hui, Yang, Lin, Liu, Fujun, O’callaghan, Michael, Gopal, Nikhil, Kelly, Valerie, Smith, Barbara, Strande, Jennifer, Mavilio, Fulvio, Beggs, Alan, Mingozzi, Federico, Lawlor, Michael, Buj-Bello, Ana, Childers, Martin

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Stereospecific Grignard-Activated Solid Phase Synthesis of DNA Methylphosphonate Dimers von Le Bec, Christine, Wickstrom, Eric

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503. Adeno-Associated Virus Vector (AAV) Microdystrophin Gene Therapy Prolongs Survival and Restores Muscle Function in the Canine Model of Duchenne Muscular Dystrophy (DMD) von Guiner, Caroline Le, Servais, Laurent, Montus, Marie, Larcher, Thibaut, Fraysse, Bodvael, Moullec, Sophie, Koo, Taeyoung, Malerba, Alberto, Bec, Christine Le, Hebben, Matthias, Masurier, Carole, Mingozzi, Federico, Adjali, Oumeya, Carlier, Pierre, Hogrel, Jean-Yves, Gjata, Bernard, Cherel, Yan, Athanasopoulos, Takis, Mavilio, Fulvio, Voit, Thomas, Moullier, Philippe, Dickson, George

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704. Long-Term Correction of Crigler-Najjar Syndrome and Scale-Up Production of an Optimized AAV8 Vector Expressing the UGT1A1 Transgene von Bortolussi, Giulia, Collaud, Fanny, van Dijk, Remco, Ronzitti, Giuseppe, Charles, Severine, Martin, Samia, Vignaud, Alban, Lacoste, Florence, Le Bec, Christine, Hebben, Matthias, Mavilio, Fulvio, Bosma, Piter, Muro, Andres F., Mingozzi, Federico

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503. Minimally Effective Dose of Systemic AAV8-MTM1 Needed To Prolong Survival and Correct Severe Muscle Pathology in a Canine Model of X-Linked Myotubular Myopathy von Mack, David L., Poulard, Karine, Goddard, Melissa, Snyder, Jessica M., Grange, Robert W., Doering, Jon, Czerniecki, Stefan, Strande, Jennifer L., Latournerie, Virginie, Veron, Philippe, Meng, Hui, Yang, Lin, Liu, Fujun, Le Bec, Christine, Buscara, Laurine, Martin, Samia, Moullier, Philippe, O'Callaghan, Michael, Mingozzi, Federico, Beggs, Alan H., Lawlor, Michael W., Buj-Bello, Anna, Mavilio, Fulvio, Childers, Martin K.

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Epigenetic gene expression noise and phenotypic diversification of clonal cell populations von Neildez-Nguyen, Thi My Anh, Parisot, Aurélie, Vignal, Céline, Rameau, Philippe, Stockholm, Daniel, Picot, Julien, Allo, Valérie, Le Bec, Christine, Laplace, Corinne, Paldi, Andras

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Preclinical Development of an AAV8-hUGT1A1 Vector for the Treatment of Crigler-Najjar Syndrome von Collaud, Fanny, Bortolussi, Giulia, Guianvarc’h, Laurence, Aronson, Sem, Bordet, Thierry, Veron, Philippe, Charles, Severine, Vidal, Patrice, Sola, Marcelo Simon, Rundwasser, Stephanie, Dufour, Delphine, Lacoste, Florence, Luc, Cyril, Wittenberghe, Laetitia, Martin, Samia, Le Bec, Christine, Bosma, Piter, Muro, Andres, Ronzitti, Giuseppe, Hebben, Matthias, Mingozzi, Federico

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Efficient gene transfer in skeletal muscle with AAV-derived bicistronic vector using the FGF-1 IRES von Delluc-Clavières, A, Le Bec, C, Van den Berghe, L, Conte, C, Allo, V, Danos, O, Prats, A-C

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CUG-BP1/CELF1 requires UGU-rich sequences for high-affinity binding von Marquis, Julien, Paillard, Luc, Audic, Yann, Cosson, Bertrand, Danos, Olivier, Le Bec, Christine, Osborne, Howard Beverley

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Stereospecific grignard activated coupling of a deoxynucleoside von Le Bec, Christine, Wickstrom, Eric

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Stereospecific grignard activated coupling of a deoxynucleoside : Methylphosphonate on a polyethylene glycol support von Le Bec, Christine, Wickstrom, Eric

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Derivatives of Imidazole-4-carboxamide as Substrates for Various DNA Polymerases von Le Bec, Christine, Roux, Pascal, Buc, Henri, Pochet, Sylvie

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