Cyclosporin A and Rapamycin Relieve Distinct Lentiviral Restriction Blocks in Hematopoietic Stem and Progenitor Cells von Petrillo, Carolina, Cesana, Daniela, Piras, Francesco, Bartolaccini, Sara, Naldini, Luigi, Montini, Eugenio, Kajaste-Rudnitski, Anna

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Lentiviral vectors escape innate sensing but trigger p53 in human hematopoietic stem and progenitor cells von Piras, Francesco, Riba, Michela, Petrillo, Carolina, Lazarevic, Dejan, Cuccovillo, Ivan, Bartolaccini, Sara, Stupka, Elia, Gentner, Bernhard, Cittaro, Davide, Naldini, Luigi, Kajaste‐Rudnitski, Anna

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Genome editing for scalable production of alloantigen‐free lentiviral vectors for in vivo gene therapy von Milani, Michela, Annoni, Andrea, Bartolaccini, Sara, Biffi, Mauro, Russo, Fabio, Di Tomaso, Tiziano, Raimondi, Andrea, Lengler, Johannes, Holmes, Michael C, Scheiflinger, Friedrich, Lombardo, Angelo, Cantore, Alessio, Naldini, Luigi

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Liver gene therapy by lentiviral vectors reverses anti‐factor IX pre‐existing immunity in haemophilic mice von Annoni, Andrea, Cantore, Alessio, Della Valle, Patrizia, Goudy, Kevin, Akbarpour, Mahzad, Russo, Fabio, Bartolaccini, Sara, D'Angelo, Armando, Roncarolo, Maria Grazia, Naldini, Luigi

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Liver-Directed Gene Therapy for Hemophilia B with Immune Stealth Lentiviral Vectors von Cantore, Alessio, Milani, Michela, Annoni, Andrea, Liu, Tongyao, Bartolaccini, Sara, Biffi, Mauro, Russo, Fabio, Peters, Robert, Lombardo, Angelo, Nichols, Timothy C., Ayuso, Eduard, Naldini, Luigi

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6. Targeted Genome Editing of Cell Lines for Improved and Scalable Production of Lentiviral Vectors for Human Gene Therapy von Cantore, Alessio, Milani, Michela, Lengler, Johannes, Bartolaccini, Sara, Di Tomaso, Tiziano, Gregory, Philip D., Scheiflinger, Friedrich, Lombardo, Angelo, Naldini, Luigi

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36. Genome-Wide Insight Into the Transcriptional Modulations Triggered By Lentiviral Transduction in Human Hematopoietic Stem Cells von Piras, Francesco, Riba, Michela, Lazarevic, Dejan, Bartolaccini, Sara, Stupka, Elia, Cittaro, Davide, Naldini, Luigi, Kajaste-Rudnitski, Anna

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286. Genome Editing of Inducible Cell Lines for Scalable Production of Improved Lentiviral Vectors for Human Gene Therapy von Cantore, Alessio, Milani, Michela, Annoni, Andrea, Lengler, Johannes, Bartolaccini, Sara, Di Tomaso, Tiziano, Holmes, Michael C., Scheiflinger, Friedrich, Lombardo, Angelo, Naldini, Luigi

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