Hematopoietic Stem Cell Transplantation for Mucopolysaccharidoses: Past, Present, and Future von Taylor, Madeleine, Khan, Shaukat, Stapleton, Molly, Wang, Jianmin, Chen, Jing, Wynn, Robert, Yabe, Hiromasa, Chinen, Yasutsugu, Boelens, Jaap Jan, Mason, Robert W., Kubaski, Francyne, Horovitz, Dafne D.G., Barth, Anneliese L., Serafini, Marta, Bernardo, Maria Ester, Kobayashi, Hironori, Orii, Kenji E., Suzuki, Yasuyuki, Orii, Tadao, Tomatsu, Shunji

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Early hematopoietic stem cell transplantation in a patient with severe mucopolysaccharidosis II: A 7 years follow-up von Barth, Anneliese L., de Magalhães, Tatiana S.P.C., Reis, Ana Beatriz R., de Oliveira, Maria Lucia, Scalco, Fernanda B., Cavalcanti, Nicolette C., Silva, Daniel S. e, Torres, Danielle A., Costa, Alessandra A.P., Bonfim, Carmem, Giugliani, Roberto, Llerena, Juan C., Horovitz, Dafne D.G.

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Long-term impact of early initiation of enzyme replacement therapy in 34 MPS VI patients: A resurvey study von Horovitz, Dafne D.G., Leão, Emília K.E.A., Ribeiro, Erlane M., Martins, Ana M., Barth, Anneliese L., Neri, João I.C.F., Kerstenetzky, Marcelo, Siqueira, Ana C.M., Ribeiro, Bethania F.R., Kim, Chong A., Santos, Francisca C., Franco, José F.S., Lichtvan, Leniza C.L., Giuliani, Liane R., Rodrigues, Maria Do C.S., Bonatti, Renata C.F., Teixeira, Thaís B., Gonçalves, Alexandra, Lourenço, Charles M., Pereira, Ane S.S., Acosta, Angelina X.

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Hematopoietic Stem Cell Transplantation in Mucopolysaccharidosis Type II von Barth, Anneliese L, Horovitz, Dafne D

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Transition to home infusion in Pompe disease in Brazil: Safety of the regimen during the COVID-19 pandemic and thereafter von Horovitz, Dafne D.G., Barth, Anneliese L., Alves, Welton C., Llerena, Juan C.

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Hematopoietic Stem Cell Transplantation in Mucopolysaccharidosis Type II: A Literature Review and Critical Analysis von Barth, Anneliese L., Horovitz, Dafne D. G.

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Mucopolysaccharidoses and laryngeal, tracheal and bronchial disease: Type-specific abnormalities and long-term implications von Horovitz, Dafne D., de Mello, Paulo Pires, de Mello Valente, Mariana Pires, Torres, Danielle, Barth, Anneliese L.

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Bone/joint abnormalities in children/adolescents: A screening protocol for mucopolysaccharidosis von Horovitz, Dafne D.G., Barth, Anneliese L., Barros Mendes, Pedro H., Gonzaga, Mariana Q.G., Chisté, Yuri L., Medeiros, Rommel B., Oliveira, Maria L., Scalco, Fernanda B.

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Enzyme replacement therapy in mucopolysaccharidosis type II with alternative dosing 1mg/kg idursulfase in every other week infusions von Horovitz, Dafne D., Barth, Anneliese L., Souza, Carolina F., Canossa, Sueli G., Curiati, Marco A., Kyosen, Sandra O., Oliveira, Maria L., Scalco, Fernanda B., Martins, Ana M.

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Early hematopoietic stem cell transplantation in a patient with severe mucopolysaccharidosis II: A 7 years follow-up von Barth, Anneliese L, de Magalhães, Tatiana S P C, Reis, Ana Beatriz R, de Oliveira, Maria Lucia, Scalco, Fernanda B, Cavalcanti, Nicolette C, Silva, Daniel S E, Torres, Danielle A, Costa, Alessandra A P, Bonfim, Carmem, Giugliani, Roberto, Llerena, Juan C, Horovitz, Dafne D G

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Variability in STEM Summer Bridge Programs: Associations with Belonging and STEM Self-Efficacy von Barth, Joan M., Dunlap, Sarah T., Bolland, Anneliese C., McCallum, Debra Moehle, Acoff, Viola L.

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