615 Antisense oligonucleotide-based drug development for people with cystic fibrosis carrying the 2789+5 G-to-A splicing mutation von Oren, Y., Barchad, O. Avizur, Galai, E. Ozeri, Elgrabli, R., Mordechai, T., Blinder, T., Stanleigh, N., Kerem, E., Kerem, B.

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P029 Antisense oligonucleotide-based drug development for cystic fibrosis patients carrying the 2789+5 G-to-A splicing mutation von Oren, Y.S., Barchad, O. Avizur, Galai, E. Ozeri, Elgrabli, R., Mordechai, T., Blinder, T., Stanleigh, N., Kerem, E., Kerem, B.

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620 Antisense oligonucleotide splicing modulation as a novel cystic fibrosis therapeutic approach for the N1303 K nonsense mutation von Oren, Y., Barchad-Avizur, O., Galai, E. Ozeri, Schirelman, M., Blinder, T., Ordan, M., Mordechai, T., Stampfer, C., Cymberknoh, M. Cohen, Kerem, E., Kerem, B.

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618 SPL84-23-1 antisense oligonucleotide modulating the 3849+10 kb C-T splicing defect, has an additive effect with elexacaftor/tezacaftor/ivacaftor in primary human bronchial epit... von Barchad-Avizur, O., Oren, Y., Golec, A., Hatton, A., Ozeri Galai, E., Stampfer, C., Dahan, S., Sermet-Gaudelus, I., Kerem, B.

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601: Antisense-oligonucleotide-splicing modulation as a novel CF therapeutic approach for W1282X mutation von Kerem, B., Oren, Y., Avizur-Barchad, O., Ozeri-Galai, E., Elgrabli, R., Schirelman, M., Fogel, T., Ordan, M., Laselva, O., Kerem, E., Bear, C.

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619 Antisense oligonucleotide splicing modulation as a novel cystic fibrosis therapeutic approach for the W1282X nonsense mutation von Avizur Barchad, O., Oren, Y., Ozeri Galai, E., Elgrabli, R., Schirelman, M., Blinder, T., Stampfer, C., Ordan, M., Laselvab, O., Cohen Cymberknoh, M., Kerem, E., Bear, C., Kerem, B.

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P028 Antisense oligonucleotide splicing modulation as a novel cystic fibrosis (CF) therapeutic approach for the W1282X nonsense mutation von Barchad, O. Avizur, Oren, Y.S., Galai, E. Ozeri, Elgrabli, R., Schirelman, M.R., Blinder, T., Stampfer, C.D., Ordan, M., Laselvab, O., Cymberknoh, M. Cohen, Kerem, E., Bear, C.E., Kerem, B.

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P034 Novel insights into the therapeutic potential of antisense oligonucleotides as splicing modulators in respiratory and intestinal patient-derived model systems von Stanleigh, N., Irony-Tur Sinai, M., Oren, Y., Golec, A., Hatton, A., Avizur-Barchad, O., Ozeri-Galai, E., Wilschanski, M., Kerem, E., Sermet-Gaudelus, I., Kerem, B.

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