Safety and tolerability of putaminal AADC gene therapy for Parkinson disease von CHRISTINE, C. W, STARR, P. A, LARSON, P. S, EBERLING, J. L, JAGUST, W. J, HAWKINS, R. A, VANBROCKLIN, H. F, WRIGHT, J. F, BANKIEWICZ, K. S, AMINOFF, M. J

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Validated assays for the quantification of C9orf72 human pathology von Salomonsson, S. E., Maltos, A. M., Gill, K., Aladesuyi Arogundade, O., Brown, K. A., Sachdev, A., Sckaff, M., Lam, K. J. K., Fisher, I. J., Chouhan, R. S., Van Laar, V. S., Marley, C. B., McLaughlin, I., Bankiewicz, K. S., Tsai, Y.-C., Conklin, B. R., Clelland, C. D.

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Axonal transport of adeno-associated viral vectors is serotype-dependent von Salegio, E A, Samaranch, L, Kells, A P, Mittermeyer, G, San Sebastian, W, Zhou, S, Beyer, J, Forsayeth, J, Bankiewicz, K S

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Results from a phase I safety trial of hAADC gene therapy for Parkinson disease von EBERLING, J. L, JAGUST, W. J, CHRISTINE, C. W, STARR, P, LARSON, P, BANKIEWICZ, K. S, AMINOFF, M. J

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Axonal transport of AAV9 in nonhuman primate brain von Green, F, Samaranch, L, Zhang, H S, Manning-Bog, A, Meyer, K, Forsayeth, J, Bankiewicz, K S

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Adeno-associated virus type 6 is retrogradely transported in the non-human primate brain von San Sebastian, W, Samaranch, L, Heller, G, Kells, A P, Bringas, J, Pivirotto, P, Forsayeth, J, Bankiewicz, K S

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MR-guided parenchymal delivery of adeno-associated viral vector serotype 5 in non-human primate brain von Samaranch, L, Blits, B, San Sebastian, W, Hadaczek, P, Bringas, J, Sudhakar, V, Macayan, M, Pivirotto, P J, Petry, H, Bankiewicz, K S

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Efficient delivery of liposome-mediated MGMT-siRNA reinforces the cytotoxity of temozolomide in GBM-initiating cells von Kato, T, Natsume, A, Toda, H, Iwamizu, H, Sugita, T, Hachisu, R, Watanabe, R, Yuki, K, Motomura, K, Bankiewicz, K, Wakabayashi, T

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Convection-Enhanced Delivery of AAV Vector in Parkinsonian Monkeys; In Vivo Detection of Gene Expression and Restoration of Dopaminergic Function Using Pro-drug Approach von Bankiewicz, Krys S., Eberling, Jamie L., Kohutnicka, Malgorzata, Jagust, William, Pivirotto, Phillip, Bringas, John, Cunningham, Janet, Budinger, Thomas F., Harvey-White, Judith

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Magnetic Resonance Imaging-Guided Delivery of Adeno-Associated Virus Type 2 to the Primate Brain for the Treatment of Lysosomal Storage Disorders von SALEGIO, E. Aguilar, KELLS, A. P, FIANDACA, M. S, BANKIEWICZ, K. S, RICHARDSON, R. M, HADACZEK, P, FORSAYETH, J, BRINGAS, J, SARDI, S. P, PASSINI, M. A, SHIHABUDDIN, L. S, CHENG, S. H

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Slow AAV2 clearance from the brain of nonhuman primates and anti-capsid immune response von Samaranch, L, Hadaczek, P, Kells, A P, Bringas, J R, Stockinger, D, San Sebastian, W, Macayan, M, Samineni, S, Pivirotto, P, Forsayeth, J, Bankiewicz, K S

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Understanding biological activity, tumor response and pseudoprogression in a phase-IIb study of MDNA55 in adults with recurrent or progressive glioblastoma (GB) von Bexon, M.F., Achrol, A., Bankiewicz, K., Brenner, A., Butowski, N., Kesari, S., Merchant, F., Merchant, R., Randazzo, D., Vogelbaum, M., Zabek, M., Sampson, J.

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Convection-enhanced delivery improves distribution and efficacy of tumor-selective retroviral replicating vectors in a rodent brain tumor model von Yin, D, Zhai, Y, Gruber, H E, Ibanez, C E, Robbins, J M, Kells, A P, Kasahara, N, Forsayeth, J, Jolly, D J, Bankiewicz, K S

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Effects of the perivascular space on convection-enhanced delivery of liposomes in primate putamen von Krauze, Michal T., Saito, Ryuta, Noble, Charles, Bringas, John, Forsayeth, John, Mcknight, Tracy R., Park, John, Bankiewicz, Krystof S.

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Convection-enhanced delivery of AAV-2 combined with heparin increases TK gene transfer in the rat brain von Nguyen, John Bang, Sanchez-Pernaute, Rosario, Cunningham, Janet, Bankiewicz, Krys S

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Adeno-Associated Virus Serotype 9 Transduction in the Central Nervous System of Nonhuman Primates von SAMARANCH, Lluis, SALEGIO, Ernesto A, SAN SEBASTIAN, Waldy, KELLS, Adrian P, FOUST, Kevin D, BRINGAS, John R, LAMARRE, Clementine, FORSAYETH, John, KASPAR, Brian K, BANKIEWICZ, Krystof S

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Long-Term Evaluation of a Phase 1 Study of AADC Gene Therapy for Parkinson's Disease von MITTERMEYER, Gabriele, CHRISTINE, Chadwick W, ROSENBLUTH, Kathryn H, BAKER, Suzanne L, STARR, Philip, LARSON, Paul, KAPLAN, Paul L, FORSAYETH, John, AMINOFF, Michael J, BANKIEWICZ, Krystof S

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In vitro generation and transplantation of precursor-derived human dopamine neurons von Sánchez-Pernaute, Rosario, Studer, Lorenz, Bankiewicz, Krys S., Major, Eugene O., McKay, Ronald D.G.

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Heparin Coinfusion during Convection-Enhanced Delivery (CED) Increases the Distribution of the Glial-Derived Neurotrophic Factor (GDNF) Ligand Family in Rat Striatum and Enhances t... von Hamilton, John F., Morrison, Paul F., Chen, Michael Y., Harvey-White, Judith, Pernaute, Rosario S., Phillips, Heidi, Oldfield, Edward, Bankiewicz, Krys S.

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Distribution of AAV2-hAADC-transduced cells after 3 years in Parkinsonian monkeys von Daadi, Marcel M, Pivirotto, Phillip, Bringas, John, Cunningham, Janet, Forsayeth, John, Eberling, Jamie, Bankiewicz, Krys S

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