Genomic Analysis Reveals Disruption of Striatal Neuronal Development and Therapeutic Targets in Human Huntington’s Disease Neural Stem Cells von Ring, Karen L., An, Mahru C., Zhang, Ningzhe, O’Brien, Robert N., Ramos, Eliana Marisa, Gao, Fuying, Atwood, Robert, Bailus, Barbara J., Melov, Simon, Mooney, Sean D., Coppola, Giovanni, Ellerby, Lisa M.

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In Vivo Applications of Cell-Penetrating Zinc-Finger Transcription Factors von Ren, Chonghua, Adams, Alexa N., Pyles, Benjamin, Bailus, Barbara J., O’Geen, Henriette, Segal, David J.

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Modulating FKBP5/FKBP51 and autophagy lowers HTT (huntingtin) levels von Bailus, Barbara J., Scheeler, Stephen M., Simons, Jesse, Sanchez, Maria A., Tshilenge, Kizito-Tshitoko, Creus-Muncunill, Jordi, Naphade, Swati, Lopez-Ramirez, Alejandro, Zhang, Ningzhe, Lakshika Madushani, Kuruwitage, Moroz, Stanislav, Loureiro, Ashley, Schreiber, Katherine H., Hausch, Felix, Kennedy, Brian K., Ehrlich, Michelle E., Ellerby, Lisa M.

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iPSC-based drug screening for Huntington's disease von Zhang, Ningzhe, Bailus, Barbara J, Ring, Karen L, Ellerby, Lisa M

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Protein Delivery of an Artificial Transcription Factor Restores Widespread Ube3a Expression in an Angelman Syndrome Mouse Brain von Bailus, Barbara J, Pyles, Benjamin, McAlister, Michelle M, O'Geen, Henriette, Lockwood, Sarah H, Adams, Alexa N, Nguyen, Jennifer Trang T, Yu, Abigail, Berman, Robert F, Segal, David J

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The prospect of molecular therapy for Angelman syndrome and other monogenic neurologic disorders von Bailus, Barbara J, Segal, David J

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Purified Protein Delivery to Activate an Epigenetically Silenced Allele in Mouse Brain von Pyles, Benjamin, Bailus, Barbara J., O’Geen, Henriette, Segal, David J.

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iPSC-based drug screening for Huntington׳s disease von Zhang, Ningzhe, Bailus, Barbara J, Ring, Karen L, Ellerby, Lisa M

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ZIKA AS A CELL PENETRATING PEPTIDE FOR DELIVERY TO THE BRAIN von Bailus, Barbara J, Ellerby, Lisa M

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