Functional correction in mouse models of muscular dystrophy using exon-skipping tricyclo-DNA oligomers von Goyenvalle, Aurélie, Griffith, Graziella, Babbs, Arran, Andaloussi, Samir El, Ezzat, Kariem, Avril, Aurélie, Dugovic, Branislav, Chaussenot, Rémi, Ferry, Arnaud, Voit, Thomas, Amthor, Helge, Bühr, Claudia, Schürch, Stefan, Wood, Matthew J A, Davies, Kay E, Vaillend, Cyrille, Leumann, Christian, Garcia, Luis

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The potential of utrophin and dystrophin combination therapies for Duchenne muscular dystrophy von Guiraud, Simon, Edwards, Benjamin, Babbs, Arran, Squire, Sarah E, Berg, Adam, Moir, Lee, Wood, Matthew J, Davies, Kay E

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Temporal transcriptomics suggest that twin-peaking genes reset the clock von Pembroke, William G, Babbs, Arran, Davies, Kay E, Ponting, Chris P, Oliver, Peter L

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Embryonic myosin is a regeneration marker to monitor utrophin-based therapies for DMD von Guiraud, Simon, Edwards, Benjamin, Squire, Sarah E, Moir, Lee, Berg, Adam, Babbs, Arran, Ramadan, Nesrine, Wood, Matthew J, Davies, Kay E

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Rescue of severely affected dystrophin/utrophin-deficient mice through scAAV-U7snRNA-mediated exon skipping von GOYENVALLE, Aurélie, BABBS, Arran, WRIGHT, Jordan, WILKINS, Vivienne, POWELL, Dave, GARCIA, Luis, DAVIES, Kay E

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Second-generation compound for the modulation of utrophin in the therapy of DMD von Guiraud, Simon, Squire, Sarah E, Edwards, Benjamin, Chen, Huijia, Burns, David T, Shah, Nandini, Babbs, Arran, Davies, Stephen G, Wynne, Graham M, Russell, Angela J, Elsey, David, Wilson, Francis X, Tinsley, Jon M, Davies, Kay E

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Prevention of Dystrophic Pathology in Severely Affected Dystrophin/Utrophin-deficient Mice by Morpholino-oligomer-mediated Exon-skipping von Goyenvalle, Aurélie, Babbs, Arran, Powell, Dave, Kole, Ryszard, Fletcher, Sue, Wilton, Steve D, Davies, Kay E

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Synthesis of SMT022357 enantiomers and in vivo evaluation in a Duchenne muscular dystrophy mouse model von Babbs, Arran, Berg, Adam, Chatzopoulou, Maria, Davies, Kay E., Davies, Stephen G., Edwards, Benjamin, Elsey, David J., Emer, Enrico, Figuccia, Aude L.A., Fletcher, Ai M., Guiraud, Simon, Harriman, Shawn, Moir, Lee, Robinson, Neil, Rowley, Jessica A., Russell, Angela J., Squire, Sarah E., Thomson, James E., Tinsley, Jonathon M., Wilson, Francis X., Wynne, Graham M.

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Enhanced Exon-skipping Induced by U7 snRNA Carrying a Splicing Silencer Sequence: Promising Tool for DMD Therapy von Goyenvalle, Aurélie, Babbs, Arran, van Ommen, Gert-Jan B, Garcia, Luis, Davies, Kay E

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dominant mutation in Snap25 causes impaired vesicle trafficking, sensorimotor gating, and ataxia in the blind-drunk mouse von Jeans, Alexander F, Oliver, Peter L, Johnson, Reuben, Capogna, Marco, Vikman, Jenny, Molnár, Zoltán, Babbs, Arran, Partridge, Christopher J, Salehi, Albert, Bengtsson, Martin, Eliasson, Lena, Rorsman, Patrik, Davies, Kay E

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Micro-utrophin Improves Cardiac and Skeletal Muscle Function of Severely Affected D2/ mdx Mice von Kennedy, Tahnee L, Guiraud, Simon, Edwards, Ben, Squire, Sarah, Moir, Lee, Babbs, Arran, Odom, Guy, Golebiowski, Diane, Schneider, Joel, Chamberlain, Jeffrey S, Davies, Kay E

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The Cellular Processing Capacity Limits the Amounts of Chimeric U7 snRNA Available for Antisense Delivery von Eckenfelder, Agathe, Tordo, Julie, Babbs, Arran, Davies, Kay E, Goyenvalle, Aurélie, Danos, Olivier

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From diagnosis to therapy in Duchenne muscular dystrophy von Babbs, Arran, Chatzopoulou, Maria, Edwards, Ben, Squire, Sarah E., Wilkinson, Isabel V. L., Wynne, Graham M., Russell, Angela J., Davies, Kay E.

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Identification of serum protein biomarkers for utrophin based DMD therapy von Guiraud, Simon, Edwards, Benjamin, Squire, Sarah E., Babbs, Arran, Shah, Nandini, Berg, Adam, Chen, Huijia, Davies, Kay E.

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Engineering Multiple U7snRNA Constructs to Induce Single and Multiexon-skipping for Duchenne Muscular Dystrophy von Goyenvalle, Aurélie, Wright, Jordan, Babbs, Arran, Wilkins, Vivienne, Garcia, Luis, Davies, Kay E

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2‑Arylbenzo[d]oxazole Phosphinate Esters as Second-Generation Modulators of Utrophin for the Treatment of Duchenne Muscular Dystrophy von Babbs, Arran, Berg, Adam, Chatzopoulou, Maria, Davies, Kay E, Davies, Stephen G, Edwards, Benjamin, Elsey, David J, Emer, Enrico, Guiraud, Simon, Harriman, Shawn, Lecci, Cristina, Moir, Lee, Peters, David, Robinson, Neil, Rowley, Jessica A, Russell, Angela J, Squire, Sarah E, Tinsley, Jonathon M, Wilson, Francis X, Wynne, Graham M

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Diaphragm rescue alone prevents heart dysfunction in dystrophic mice von CRISP, Alastair, HAIFANG YIN, STUCKEY, Daniel J, CLARKE, Kieran, DAVIES, Kay E, WOOD, Matthew J. A, GOYENVALLE, Aurelie, BETTS, Corinne, MOULTON, Hong M, SEOW, Yiqi, BABBS, Arran, MERRITT, Thomas, SALEH, Amer F, GAIT, Michael J

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Data from: Temporal transcriptomics suggest that twin-peaking genes reset the clock von Pembroke, William G., Babbs, Arran, Davies, Kay E., Ponting, Chris P., Oliver, Peter L.

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LincInfo_S3 von Pembroke, William G., Babbs, Arran, Davies, Kay E., Ponting, Chris P., Oliver, Peter L.

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GeneInfo_S2 von Pembroke, William G., Babbs, Arran, Davies, Kay E., Ponting, Chris P., Oliver, Peter L.

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