Identification of preexisting adaptive immunity to Cas9 proteins in humans von Charlesworth, Carsten T., Deshpande, Priyanka S., Dever, Daniel P., Camarena, Joab, Lemgart, Viktor T., Cromer, M. Kyle, Vakulskas, Christopher A., Collingwood, Michael A., Zhang, Liyang, Bode, Nicole M., Behlke, Mark A., Dejene, Beruh, Cieniewicz, Brandon, Romano, Rosa, Lesch, Benjamin J., Gomez-Ospina, Natalia, Mantri, Sruthi, Pavel-Dinu, Mara, Weinberg, Kenneth I., Porteus, Matthew H.

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A high-fidelity Cas9 mutant delivered as a ribonucleoprotein complex enables efficient gene editing in human hematopoietic stem and progenitor cells von Vakulskas, Christopher A., Dever, Daniel P., Rettig, Garrett R., Turk, Rolf, Jacobi, Ashley M., Collingwood, Michael A., Bode, Nicole M., McNeill, Matthew S., Yan, Shuqi, Camarena, Joab, Lee, Ciaran M., Park, So Hyun, Wiebking, Volker, Bak, Rasmus O., Gomez-Ospina, Natalia, Pavel-Dinu, Mara, Sun, Wenchao, Bao, Gang, Porteus, Matthew H., Behlke, Mark A.

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Dorsal Raphe Serotonin Neurons Mediate CO2-Induced Arousal from Sleep von Smith, Haleigh R, Leibold, Nicole K, Rappoport, Daniel A, Ginapp, Callie M, Purnell, Benton S, Bode, Nicole M, Alberico, Stephanie L, Kim, Young-Cho, Audero, Enrica, Gross, Cornelius T, Buchanan, Gordon F

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Dorsal Raphe Serotonin Neurons Mediate CO 2 -Induced Arousal from Sleep von Smith, Haleigh R, Leibold, Nicole K, Rappoport, Daniel A, Ginapp, Callie M, Purnell, Benton S, Bode, Nicole M, Alberico, Stephanie L, Kim, Young-Cho, Audero, Enrica, Gross, Cornelius T, Buchanan, Gordon F

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Gene replacement of α-globin with β-globin restores hemoglobin balance in β-thalassemia-derived hematopoietic stem and progenitor cells von Cromer, M. Kyle, Camarena, Joab, Martin, Renata M., Lesch, Benjamin J., Vakulskas, Christopher A., Bode, Nicole M., Kurgan, Gavin, Collingwood, Michael A., Rettig, Garrett R., Behlke, Mark A., Lemgart, Viktor T., Zhang, Yankai, Goyal, Ankush, Zhao, Feifei, Ponce, Ezequiel, Srifa, Waracharee, Bak, Rasmus O., Uchida, Naoya, Majeti, Ravindra, Sheehan, Vivien A., Tisdale, John F., Dever, Daniel P., Porteus, Matthew H.

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AsCas12a ultra nuclease facilitates the rapid generation of therapeutic cell medicines von Zhang, Liyang, Zuris, John A., Viswanathan, Ramya, Edelstein, Jasmine N., Turk, Rolf, Thommandru, Bernice, Rube, H. Tomas, Glenn, Steve E., Collingwood, Michael A., Bode, Nicole M., Beaudoin, Sarah F., Lele, Swarali, Scott, Sean N., Wasko, Kevin M., Sexton, Steven, Borges, Christopher M., Schubert, Mollie S., Kurgan, Gavin L., McNeill, Matthew S., Fernandez, Cecilia A., Myer, Vic E., Morgan, Richard A., Behlke, Mark A., Vakulskas, Christopher A.

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Comparative analysis of CRISPR off-target discovery tools following ex vivo editing of CD34+ hematopoietic stem and progenitor cells von Cromer, M. Kyle, Majeti, Kiran R., Rettig, Garrett R., Murugan, Karthik, Kurgan, Gavin L., Bode, Nicole M., Hampton, Jessica P., Vakulskas, Christopher A., Behlke, Mark A., Porteus, Matthew H.

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Disruption of Protein Processing in the Endoplasmic Reticulum of DYT1 Knock-in Mice Implicates Novel Pathways in Dystonia Pathogenesis von Beauvais, Genevieve, Bode, Nicole M, Watson, Jaime L, Wen, Hsiang, Glenn, Kevin A, Kawano, Hiroyuki, Harata, N Charles, Ehrlich, Michelle E, Gonzalez-Alegre, Pedro

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Genetically corrected RAG2-SCID human hematopoietic stem cells restore V(D)J-recombinase and rescue lymphoid deficiency von Pavel-Dinu, Mara, Gardner, Cameron L., Nakauchi, Yusuke, Kawai, Tomoki, Delmonte, Ottavia M., Palterer, Boaz, Bosticardo, Marita, Pala, Francesca, Viel, Sebastien, Malech, Harry L., Ghanim, Hana Y., Bode, Nicole M., Kurgan, Gavin L., Detweiler, Angela M., Vakulskas, Christopher A., Neff, Norma F., Sheikali, Adam, Menezes, Sherah T., Chrobok, Jade, Hernández González, Elaine M., Majeti, Ravindra, Notarangelo, Luigi D., Porteus, Matthew H.

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What Clients Want: A Conjoint Analysis of Precursors to Coach Selection von Céline Rojon, Nicole Bode, Almuth McDowall

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DYT1 knock-in mice are not sensitized against mitochondrial complex-II inhibition von Bode, Nicole, Massey, Cory, Gonzalez-Alegre, Pedro

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Author Correction: AsCas12a ultra nuclease facilitates the rapid generation of therapeutic cell medicines von Zhang, Liyang, Zuris, John A., Viswanathan, Ramya, Edelstein, Jasmine N., Turk, Rolf, Thommandru, Bernice, Rube, H. Tomas, Glenn, Steve E., Collingwood, Michael A., Bode, Nicole M., Beaudoin, Sarah F., Lele, Swarali, Scott, Sean N., Wasko, Kevin M., Sexton, Steven, Borges, Christopher M., Schubert, Mollie S., Kurgan, Gavin L., McNeill, Matthew S., Fernandez, Cecilia A., Myer, Vic E., Morgan, Richard A., Behlke, Mark A., Vakulskas, Christopher A.

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Engineered AsCas12a Variants with Enhanced Activity and Broadened PAM Compatibility von Collingwood, Michael A, Vakulskas, Christopher A, Zhang, Liyang, Turk, Rolf, Bode, Nicole M, Jacobi, Ashley M, McNeill, Matthew S, McQuisten, Kyle, Thommandru, Bernice, Behlke, Mark A

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The New Social Media in Russia: Political Blogging by the Government and the Opposition von Bode, Nicole, Makarychev, Andrey

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Gene replacement of [alpha]-globin with [beta]-globin restores hemoglobin balance in [beta]-thalassemia-derived hematopoietic stem and progenitor cells von Cromer, M. Kyle, Camarena, Joab, Martin, Renata M, Lesch, Benjamin J, Vakulskas, Christopher A, Bode, Nicole M, Kurgan, Gavin, Collingwood, Michael A, Rettig, Garret R, Behlke, Mark A, Lemgart, Viktor T, Zhang, Yankai, Goyal, Ankush, Zhao, Feifei, Ponce, Ezequiel, Srifa, Waracharee, Bak, Rasmus O

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Dorsal Raphe Serotonin Neurons Mediate CO^sub 2^^sup -^Induced Arousal from Sleep von Smith, Haleigh R, Leibold, Nicole K, Rappoport, Daniel A, Ginapp, Callie M, Purnell, Benton S, Bode, Nicole M, Alberico, Stephanie L, Kim, Young-Cho, Audero, Enrica, Gross, Cornelius T, Buchanan, Gordon F

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A high-fidelity Cas9 mutant delivered as a ribonucleoprotein complex enables efficient gene editing in human haematopoietic stem and progenitor cells von Vakulskas, Christopher A., Dever, Daniel P., Rettig, Garrett R., Turk, Rolf, Jacobi, Ashley M., Collingwood, Michael A., Bode, Nicole M., McNeill, Matthew S., Yan, Shuqi, Camarena, Joab, Lee, Ciaran M., Park, So Hyun, Wiebking, Volker, Bak, Rasmus O., Gomez-Ospina, Natalia, Pavel-Dinu, Mara, Sun, Wenchao, Bao, Gang, Porteus, Matthew H., Behlke, Mark A.

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Silencing Primary Dystonia: Lentiviral-Mediated RNA Interference Therapy for DYT1 Dystonia von Gonzalez-Alegre, Pedro, Bode, Nicole, Davidson, Beverly L, Paulson, Henry L

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Transcriptional and proteomic profiling in a cellular model of DYT1 dystonia von Martin, J.N, Bair, T.B, Bode, N, Dauer, W.T, Gonzalez-Alegre, P

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The ubiquitin ligase FBG1 promotes the degradation of the disease-linked protein torsinA through the ubiquitin proteasome pathway and macroautophagy von Gordon, Kara L, Glenn, Kevin A, Bode, Nicole, Wen, Hsiang M, Paulson, Henry L, Gonzalez-Alegre, Pedro

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