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Giant axonal neuropathy: cross-sectional analysis of a large natural history cohort von Bharucha-Goebel, Diana X, Norato, Gina, Saade, Dimah, Paredes, Eduardo, Biancavilla, Victoria, Donkervoort, Sandra, Kaur, Rupleen, Lehky, Tanya, Fink, Margaret, Armao, Diane, Gray, Steven J, Waite, Melissa, Debs, Sarah, Averion, Gilberto, Hu, Ying, Zein, Wadih M, Foley, A Reghan, Jain, Minal, Bönnemann, Carsten G

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Intrathecal Gene Therapy for Giant Axonal Neuropathy von Bharucha-Goebel, Diana X., Todd, Joshua J., Saade, Dimah, Norato, Gina, Jain, Minal, Lehky, Tanya, Bailey, Rachel M., Chichester, Jessica A., Calcedo, Roberto, Armao, Diane, Foley, A. Reghan, Mohassel, Payam, Tesfaye, Eshetu, Carlin, Bradley P., Seremula, Beth, Waite, Melissa, Zein, Wadih M., Huryn, Laryssa A., Crawford, Thomas O., Sumner, Charlotte J., Hoke, Ahmet, Heiss, John D., Charnas, Lawrence, Hooper, Jody E., Bouldin, Thomas W., Kang, Elizabeth M., Rybin, Denis, Gray, Steven J., Bönnemann, Carsten G.

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