Progression Of Vision Loss In Patients With Geographic Atrophy- A Disease Model von Arjunji, R, Wang, F, Gutierrez, B, Bhattacharyya, A, Alfonso, R, Williams, R, Dabbous, O

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CO204 Primary and Secondary Endpoints Used in Recent (2022) Alzheimer’s Disease (AD) Phase III Clinical Trials von Arjunji, R., Massey, J., Maru, B., Crosland, E., Gregory, S., Kern, R.

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EPH39 A Targeted Literature Review (TLR) of Clinical, Humanistic, and Economic Burden of Alzheimer’s Disease (AD) in the United States (US) von Kern, R, Massey, J, Arjunji, R, Gallagher, S, Tinajero, M, Miller, S, Cheung, A, Knappett, M, Vaughan, B, Howell, C

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PRO18 ASSESSMENT OF COST-EFFECTIVENESS RESULTS FROM ICER ULTRA-RARE DISORDER REVIEWS von Arjunji, R., Venkitaramani, D., Wiesner, T., Maru, B., Dabbous, O.

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PND24 Burden of Illness of Spinal Muscular Atrophy: An Update von Droege, M., Dabbous, O., Arjunji, R., Patel, A., Gauthier-Loiselle, M., Cloutier, M., Sproule, D.M.

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SMA - CLINICAL von Droege, M., Dabbous, O., Arjunji, R., Gauthier-Loiselle, M., Cloutier, M., Sproule, D.

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SMA - CLINICAL: P.78 Burden of illness of spinal muscular atrophy type 1 (SMA1): an update von Droege, M., Dabbous, O., Arjunji, R., Gauthier-Loiselle, M., Cloutier, M., Sproule, D.

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The value of onasemnogene abeparvovec (AVXS-101) gene-replacement therapy for spinal muscular atrophy type 1 von Dabbous, O., Sproule, D.M., Feltner, D.E., Droege, M., Khan, F., Arjunji, R.

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Burden of illness of spinal muscular atrophy type 1 (SMA1) von Droege, M., Dabbous, O., Arjunji, R., Seda, J., Gauthier-Loiselle, M., Cloutier, M., Sproule, D.M.

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Comparative effectiveness of biologics for the management of rheumatoid arthritis: systematic review and network meta-analysis von Alfonso-Cristancho, Rafael, Armstrong, Nigel, Arjunji, Ramesh, Riemsma, Rob, Worthy, Gill, Ganguly, Rita, Kleijnen, Jos

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PMU30 COST-EFFECTIVENESS ANALYSIS OF NEWBORN SCREENING FOR SPINAL MUSCULAR ATROPHY (SMA) IN THE UNITED STATES von Arjunji, R., Zhou, J., Patel, A., Edwards, M.L., Harvey, M., Soverino, M., Dabbous, O.

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PRO51 COST-EFFECTIVENESS AND BUDGET IMPACT OF ONASEMNOGENE ABEPARVOVEC FOR SPINAL MUSCULAR ATROPHY TYPE 1: POST-HOC ANALYSIS OF A MODEL DEVELOPED BY ICER von Dabbous, O., Dean, R., Arjunji, R., Sproule, D.M., Feltner, D.E., Malone, D.C.

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P.210Burden of illness of spinal muscular atrophy type 1 (SMA1) von Droege, M., Dabbous, O., Arjunji, R., Seda, J., Gauthier-Loiselle, M., Cloutier, M., Sproule, D.

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P.358The value of AVXS-101 gene-replacement therapy (GRT) for spinal muscular atrophy type 1 (SMA1): improved survival, pulmonary and nutritional support, and motor function with d... von Dabbous, O., Sproule, D., Feltner, D., Droege, M., Khan, F., Arjunji, R.

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TP2 TREATMENT PATTERNS IN SPINAL MUSCULAR ATROPHY: INTERVIEWS WITH HEALTHCARE PROFESSIONALS IN THE UNITED KINGDOM von Dabbous, O., Germain, N., Maru, B., Aballéa, S., Desroches, M., Toumi, M., Arjunji, R.

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PND17 SELECTING APPROPRIATE OUTCOME MEASURES FOR ALS CLINICAL TRIALS von Arjunji, R., Glowienka, E., Maru, B., Wiesner, T., Meriggioli, M., Dabbous, O.

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PRO10 USE OF SINGLE DOSE GENE-REPLACEMENT THERAPY FOR THE TREATMENT OF SPINAL MUSCULAR ATROPHY TYPE 1: A UNITED STATES PAYER BUDGET IMPACT ANALYSIS von Malone, D., Miller, B., Dean, R., Arjunji, R., Jensen, I.S., Maru, B., Dabbous, O.

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RO2 ASSESSING THE RELATIONSHIP BETWEEN LIFELONG VALUE AND PRICING FOR ORPHAN DRUGS IN ULTRA-RARE DISEASES von Dabbous, O., Zhou, Z.Y., Tang, C., Harvey, M., Wu, E.Q., Arjunji, R.

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PRO22 BURDEN OF ILLNESS OF SPINAL MUSCULAR ATROPHY: AN UPDATE von Droege, M., Dabbous, O., Arjunji, R., Gauthier-Loiselle, M., Cloutier, M., Sproule, D.M.

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PMU36 COST-UTILITY ANALYSIS OF SINGLE DOSE GENE-REPLACEMENT THERAPY FOR SPINAL MUSCULAR ATROPHY TYPE 1 COMPARED TO CHRONIC NUSINERSEN TREATMENT IN JAPAN von Dean, R., Miller, B., Arjunji, R., Awano, H., Igarashi, A., Tanaka, S., Feltner, D.E., Sproule, D.M., Jensen, I., Dabbous, O.

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