Precise small-molecule cleavage of an r(CUG) repeat expansion in a myotonic dystrophy mouse model von Angelbello, Alicia J., Rzuczek, Suzanne G., Mckee, Kendra K., Chen, Jonathan L., Olafson, Hailey, Cameron, Michael D., Moss, Walter N., Wang, Eric T., Disney, Matthew D.

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Bleomycin Can Cleave an Oncogenic Noncoding RNA von Angelbello, Alicia J., Disney, Matthew D.

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A Toxic RNA Catalyzes the Cellular Synthesis of Its Own Inhibitor, Shunting It to Endogenous Decay Pathways von Benhamou, Raphael I., Angelbello, Alicia J., Wang, Eric T., Disney, Matthew D.

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A blood-brain penetrant RNA-targeted small molecule triggers elimination of r(G 4 C 2 ) exp in c9ALS/FTD via the nuclear RNA exosome von Bush, Jessica A, Meyer, Samantha M, Fuerst, Rita, Tong, Yuquan, Li, Yue, Benhamou, Raphael I, Aikawa, Haruo, Zanon, Patrick R A, Gibaut, Quentin M R, Angelbello, Alicia J, Gendron, Tania F, Zhang, Yong-Jie, Petrucelli, Leonard, Heick Jensen, Torben, Childs-Disney, Jessica L, Disney, Matthew D

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Structure-Specific Cleavage of an RNA Repeat Expansion with a Dimeric Small Molecule Is Advantageous over Sequence-Specific Recognition by an Oligonucleotide von Benhamou, Raphael I, Angelbello, Alicia J, Andrews, Ryan J, Wang, Eric T, Moss, Walter N, Disney, Matthew D

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Development of pharmacophore models for small molecules targeting RNA: Application to the RNA repeat expansion in myotonic dystrophy type 1 von Angelbello, Alicia J., González, Àlex L., Rzuczek, Suzanne G., Disney, Matthew D.

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A Toxic RNA Templates the Synthesis of its own Fluorogenic Inhibitor by Using a Bioorthogonal Tetrazine Ligation in Cells and Tissues von Angelbello, Alicia J., Disney, Matthew D.

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