O17 Highly efficient base editing of homozygous and heterozygous COL7A1 variants in fibroblasts from patients with recessive dystrophic epidermolysis bullosa using adenine base edi... von Guri, Ina, Brooks, Imogen, Alrokh, Yara, Kazamizadeh, Aidni, Graham, Carina, Hart, Steven, McGrath, John, Jackow, Joanna

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P09 Next-generation sequencing: on-and off-target analysis of gene editing in fibroblasts from patients with recessive dystrophic epidermolysis bullosa von Kazemizadeh, Aidin, Brooks, Imogen, Guri, Ina, Alrokh, Yara, Balon, Katarzyna, Laczmanski, Lukasz, McGrath, John, Jackow-Malinowska, Joanna

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Lipid Nanoparticles Efficiently Deliver the Base Editor ABE8e for COL7A1 Correction in Dystrophic Epidermolysis Bullosa Fibroblasts In Vitro von Guri-Lamce, Ina, Alrokh, Yara, Graham, Carina, Maeshima, Ruhina, Rognoni, Emanuel, Caley, Matthew, Łaczmański, Łukasz, Hart, Stephen L., McGrath, John A., Jacków-Malinowska, Joanna

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Topical gene editing therapeutics using lipid nanoparticles: 'gene creams' for genetic skin diseases? von Guri-Lamce, Ina, AlRokh, Yara, Kim, Youngah, Maeshima, Ruhina, Graham, Carina, Hart, Stephen L, McGrath, John A, Jacków-Malinowska, Joanna

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Highly efficient biallelic correction of homozygous COL7A1 mutation using ABE8e adenine base editor von Brooks, Imogen R, Alrokh, Yara, Kazemizadeh, Aidin, Balon, Katarzyna, Newby, Gregory, Liu, David R, Łaczmański, Łukasz, McGrath, John A, Jacków-Malinowska, Joanna

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Topical gene editing therapeutics using lipid nanoparticles: 'gene creams' for genetic skin diseases? von Guri-Lamce, Ina, AlRokh, Yara, Kim, Youngah, Maeshima, Ruhina, Graham, Carina, Hart, Stephen L, McGrath, John A, Jackow-Malinowska, Joanna

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Lipid Nanoparticles Efficiently Deliver the Base Editor ABE8e for COL7A1 Correction in Dystrophic Epidermolysis Bullosa Fibroblasts In Vitro von Guri-Lamce, Ina, Alrokh, Yara, Graham, Carina, Maeshima, Ruhina, Rognoni, Emanuel, Caley, Matthew, Łaczmański, Łukasz, Hart, Stephen L, McGrath, John A, Jacków-Malinowska, Joanna

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