PCR229 Impact of Fibrodysplasia Ossificans Progressiva on Living Adaptations and Employment: Burden of Illness Survey Results from the United States and Canada von Al Mukaddam, M., Toder, K.S., Davis, M., Croskery, K., Grandoulier, A.S., Boing, E., Shamseddine, N., Kaplan, F.S.

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CO32 Heterotopic Ossification in Palovarotene-Treated and Untreated Individuals with Fibrodysplasia Ossificans Progressiva: Matched and Weighted Analyses von Al Mukaddam, M., Baujat, G., Cheung, A.M., De Cunto, C., Hsiao, E.C., Keen, R., Marden, J., Signorovitch, J., Boing, E., Marino, R., Strahs, A., Pignolo, R.J.

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PCR24 The Humanistic and Economic Impact of Fibrodysplasia Ossificans Progressiva on Primary Caregivers: Results From an International Burden of Illness Survey von Al Mukaddam, M, Toder, KS, Davis, M, Croskery, K, Grandoulier, AS, Boing, E, Kaplan, FS

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PCR44 Quantifying Outcomes in Fibrodysplasia Ossificans Progressiva (FOP) By Patient Age: Results from an International Burden of Illness Survey von Al Mukaddam, M, Toder, KS, Davis, M, Croskery, K, Grandoulier, AS, Böing, EA, Kaplan, FS

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POSA427 Assessment of the Impact of Fibrodysplasia Ossificans Progressiva on Quality of Life for Patients and their Families Using an International Burden of Illness Survey von Al Mukaddam, M, Toder, KS, Davis, M, Croskery, K, Grandoulier, AS, Whalen, J, Kaplan, FS

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POSA426 Assessment of the Economic Impact of Fibrodysplasia Ossificans Progressiva on Patients and their Families Using an International Burden of Illness Survey von Al Mukaddam, M, Toder, KS, Davis, M, Croskery, K, Grandoulier, AS, Whalen, J, Kaplan, FS

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POSC373 Use of Aids, Assistive Devices and Adaptations by Individuals with Fibrodysplasia Ossificans Progressiva (FOP): 36-Month Results from a Global Natural History Study von Al Mukaddam, M, Baujat, G, Houchard, A, Hsiao, EC, Keen, R, Marino, R, Pignolo, RJ, Kaplan, FS

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Hypoparathyroidism due to 22Q11 Deletion Syndrome Presenting as Acute Cardiomyopathy von Agarwal, Rahul, Kallish, Staci, Al Mukaddam, Mona

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Fibrodysplasia ossificans progressiva (FOP): A disorder of osteochondrogenesis von Kaplan, Frederick S., Al Mukaddam, Mona, Stanley, Alexandra, Towler, O. Will, Shore, Eileen M.

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Reduction of New Heterotopic Ossification (HO) in the Open‐Label, Phase 3 MOVE Trial of Palovarotene for Fibrodysplasia Ossificans Progressiva (FOP) von Pignolo, Robert J., Hsiao, Edward C., Al Mukaddam, Mona, Baujat, Geneviève, Berglund, Staffan K., Brown, Matthew A., Cheung, Angela M., De Cunto, Carmen, Delai, Patricia, Haga, Nobuhiko, Kannu, Peter, Keen, Richard, Le Quan Sang, Kim‐Hanh, Mancilla, Edna E., Marino, Rose, Strahs, Andrew, Kaplan, Frederick S.

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Matrix metalloproteinase-9 deficiency confers resilience in fibrodysplasia ossificans progressiva in a man and mice von Lounev, Vitali, Groppe, Jay C, Brewer, Niambi, Wentworth, Kelly L, Smith, Victoria, Xu, Meiqi, Schomburg, Lutz, Bhargava, Pankaj, Al Mukaddam, Mona, Hsiao, Edward C, Shore, Eileen M, Pignolo, Robert J, Kaplan, Frederick S

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Garetosmab in fibrodysplasia ossificans progressiva: a randomized, double-blind, placebo-controlled phase 2 trial von Di Rocco, Maja, Forleo-Neto, Eduardo, Pignolo, Robert J., Keen, Richard, Orcel, Philippe, Funck-Brentano, Thomas, Roux, Christian, Kolta, Sami, Madeo, Annalisa, Bubbear, Judith S., Tabarkiewicz, Jacek, Szczepanek, Małgorzata, Bachiller-Corral, Javier, Cheung, Angela M., Dahir, Kathryn M., Botman, Esmée, Raijmakers, Pieter G., Al Mukaddam, Mona, Tile, Lianne, Portal-Celhay, Cynthia, Sarkar, Neena, Hou, Peijie, Musser, Bret J., Boyapati, Anita, Mohammadi, Kusha, Mellis, Scott J., Rankin, Andrew J., Economides, Aris N., Trotter, Dinko Gonzalez, Herman, Gary A., O’Meara, Sarah J., DelGizzi, Richard, Weinreich, David M., Yancopoulos, George D., Eekhoff, E. Marelise W., Kaplan, Frederick S.

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An ACVR1R375P pathogenic variant in two families with mild fibrodysplasia ossificans progressiva von Kaplan, Frederick S., Groppe, Jay C., Xu, Meiqi, Towler, O. Will, Grunvald, Eduardo, Kalunian, Kenneth, Kallish, Staci, Al Mukaddam, Mona, Pignolo, Robert J., Shore, Eileen M.

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Special considerations for clinical trials in fibrodysplasia ossificans progressiva (FOP) von Hsiao, Edward C., Di Rocco, Maja, Cali, Amanda, Zasloff, Michael, Al Mukaddam, Mona, Pignolo, Robert J., Grunwald, Zvi, Netelenbos, Coen, Keen, Richard, Baujat, Genevieve, Brown, Matthew A., Cho, Tae‐Joon, De Cunto, Carmen, Delai, Patricia, Haga, Nobuhiko, Morhart, Rolf, Scott, Christiaan, Zhang, Keqin, Diecidue, Robert J., Friedman, Clive S., Kaplan, Fredrick S., Eekhoff, Elisabeth M.W.

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Prevalence and risk factors for kidney stones in fibrodysplasia ossificans progressiva von Gupta, Rishi R., Delai, Patricia L.R., Glaser, David L., Rocke, David M., Al Mukaddam, Mona, Pignolo, Robert J., Kaplan, Frederick S.

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Characterization of flare-ups and impact of garetosmab in adults with fibrodysplasia ossificans progressiva: a post hoc analysis of the randomized, double-blind, placebo-controlled... von Keen, Richard, Dahir, Kathryn M, McGinniss, Jennifer, Sanchez, Robert J, Mellis, Scott, Economides, Aris N, Di Rocco, Maja, Orcel, Philippe, Roux, Christian, Tabarkiewicz, Jacek, Bachiller-Corral, Javier, Cheung, Angela M, Al Mukaddam, Mona, Mohammadi, Kusha, Gu, Jing, Srinivasan, Dushyanth, Trotter, Dinko Gonzalez, Eekhoff, E Marelise W, Kaplan, Frederick S, Pignolo, Robert J

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Off-on-off-on use of imatinib in three children with fibrodysplasia ossificans progressiva von Kaplan, Frederick S., Teachey, David T., Andolina, Jeffrey R., Siegel, David M., Mancilla, Edna E., Hsiao, Edward C., Al Mukaddam, Mona, Rocke, David M., Pignolo, Robert J.

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Most Fractures Treated Nonoperatively in Individuals With Fibrodysplasia Ossificans Progressiva Heal With a Paucity of Flareups, Heterotopic Ossification, and Loss of Mobility von Lindborg, Carter M., Al Mukaddam, Mona, Baujat, Genevieve, Cho, Tae-Joon, De Cunto, Carmen L., Delai, Patricia L. R., Eekhoff, Elisabeth M. W., Haga, Nobuhiko, Hsiao, Edward C., Morhart, Rolf, de Ruiter, Ruben, Scott, Christiaan, Seemann, Petra, Szczepanek, Małgorzata, Tabarkiewicz, Jacek, Pignolo, Robert J., Kaplan, Frederick S.

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Self-reported baseline phenotypes from the International Fibrodysplasia Ossificans Progressiva (FOP) Association Global Registry von Pignolo, Robert J., Cheung, Kin, Kile, Sammi, Fitzpatrick, Mary Anne, De Cunto, Carmen, Al Mukaddam, Mona, Hsiao, Edward C., Baujat, Genevieve, Delai, Patricia, Eekhoff, Elisabeth M.W., Di Rocco, Maja, Grunwald, Zvi, Haga, Nobuhiko, Keen, Richard, Levi, Benjamin, Morhart, Rolf, Scott, Christiaan, Sherman, Adam, Zhang, Keqin, Kaplan, Fredrick S.

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Heterozygous variant in WNT1 gene in two brothers with early onset osteoporosis von Turin, Christie G., Joeng, Kyu Sang, Kallish, Staci, Raper, Anna, Asher, Stephanie, Campeau, Philippe M., Khan, Amna N., Al Mukaddam, Mona

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