Cell type-selective targeted delivery of a recombinant lysosomal enzyme for enzyme therapies von Baik, Andrew D., Calafati, Philip, Zhang, Xiaoli, Aaron, Nina A., Mehra, Antonia, Moller-Tank, Sven, Miloscio, Lawrence, Praggastis, Maria, Giovannone, Nicholas, Pan, Cheryl, Tang, Yajun, Bridges, Susannah, Mujica, Alejo, Barbounis, Peter, Yanolatos, Jean, Gale, Nicholas, Li, Ning, Kyratsous, Christos A., Schoenherr, Christopher J., Murphy, Andrew J., Economides, Aris N., Cygnar, Katherine D.

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Skeletal phenotype amelioration in mucopolysaccharidosis VI requires intervention at the earliest stages of postnatal development von Hwang-Wong, Elizabeth, Amar, Gabrielle, Das, Nanditha, Zhang, Xiaoli, Aaron, Nina, Gale, Kirsten, Rothman, Nyanza, Fante, Massimo, Baik, Andrew, Bhargava, Ajay, Fricker, Arun, McAlister, Michelle, Rabinowitz, Jeremy, Lees-Shepard, John, Nannuru, Kalyan, Economides, Aris N, Cygnar, Katherine D

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Liver-specific AAV gene therapy corrects lipid storage in LAL-D model mice but does not prevent lipid accumulation in acquired fatty liver model mice von Aaron, Nina A., Baik, Andrew D., Economides, Aris N., Cygnar, Katherine D.

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Delivering therapeutic lysosomal enzyme to the CNS: A rapid, large-scale screen identifies optimal characteristics of BBB-crossing TFRC antibodies von Praggastis, Maria, Gale, Kirsten, Baik, Andrew, Aaron, Nina, Rothman, Nyanza, Zhang, Xiaoli, Giovannone, Nicholas, Hwang-Wong, Elizabeth, Cygnar, Katherine D.

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Delivering therapeutic lysosomal enzyme to the CNS: A rapid, large-scale in vivo screen identifies optimal characteristics of BBB-crossing TFRC antibodies von Praggastis, Maria, Gale, Kirsten, Baik, Andrew, Aaron, Nina, Rothman, Nyanza, Zhang, Xiaoli, Giovannone, Nicholas, Hwang-Wong, Elizabeth, Cygnar, Katherine D.

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BBB-targeted GAA delivered as gene therapy treats CNS and muscle in Pompe disease model mice von Praggastis, Maria, Gale, Kirsten, Baik, Andrew, Calafati, Philip, Aaron, Nina, Rothman, Nyanza, Zhang, Xiaoli, Giovannone, Nicholas, Hwang, Elizabeth, Economides, Aris, Cygnar, Katherine

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Defining phenotype reversibility in lysosomal disease: Leveraging a COIN model in mucopolysaccharidosis type VI (MPS VI) von Hwang-Wong, Elizabeth, Amar, Gabrielle, Das, Nanditha, Zhang, Xiaoli, Rothman, Nyanza, Calafati, Philip, Aaron, Nina, Gale, Kirsten, Fante, Massimo, Lees-Shepard, John, Nannuru, Kalyan, Baik, Andrew, Economides, Aris, Cygnar, Katherine

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Next-generation antibody-guided enzyme replacement therapy in Pompe disease mice von Baik, Andrew, Aaron, Nina, Birnbaum, Matthew S., Schoenherr, Christopher J., Murphy, Andrew J., Economides, Aris N., Cygnar, Katherine D.

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High seroprevalence for SARS-CoV-2 among household members of essential workers detected using a dried blood spot assay von McDade, Thomas W, McNally, Elizabeth M, Zelikovich, Aaron S, D'Aquila, Richard, Mustanski, Brian, Miller, Aaron, Vaught, Lauren A, Reiser, Nina L, Bogdanovic, Elena, Fallon, Katherine S, Demonbreun, Alexis R

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Candida albicans Morphogenesis Programs Control the Balance between Gut Commensalism and Invasive Infection von Witchley, Jessica N., Penumetcha, Pallavi, Abon, Nina V., Woolford, Carol A., Mitchell, Aaron P., Noble, Suzanne M.

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Dose-rate coefficients for external exposure to radionuclides uniformly distributed in soil to an infinite depth von Satoh, Daiki, Petoussi-Henss, Nina

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Reward prediction errors create event boundaries in memory von Rouhani, Nina, Norman, Kenneth A., Niv, Yael, Bornstein, Aaron M.

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De Novo Lipid Synthesis Facilitates Gemcitabine Resistance through Endoplasmic Reticulum Stress in Pancreatic Cancer von Tadros, Saber, Shukla, Surendra K, King, Ryan J, Gunda, Venugopal, Vernucci, Enza, Abrego, Jaime, Chaika, Nina V, Yu, Fang, Lazenby, Audrey J, Berim, Lyudmyla, Grem, Jean, Sasson, Aaron R, Singh, Pankaj K

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Dissociable Effects of Surprising Rewards on Learning and Memory von Rouhani, Nina, Norman, Kenneth A., Niv, Yael

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A low-cost paper-based synthetic biology platform for analyzing gut microbiota and host biomarkers von Takahashi, Melissa K., Tan, Xiao, Dy, Aaron J., Braff, Dana, Akana, Reid T., Furuta, Yoshikazu, Donghia, Nina, Ananthakrishnan, Ashwin, Collins, James J.

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A Robust Design Capture-Recapture Analysis of Abundance, Survival and Temporary Emigration of Three Odontocete Species in the Gulf of Corinth, Greece von Santostasi, Nina Luisa, Bonizzoni, Silvia, Bearzi, Giovanni, Eddy, Lavinia, Gimenez, Olivier

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Triglyceride Lowering with Pemafibrate to Reduce Cardiovascular Risk von Das Pradhan, Aruna, Glynn, Robert J., Fruchart, Jean-Charles, MacFadyen, Jean G., Zaharris, Elaine S., Everett, Brendan M., Campbell, Stuart E., Oshima, Ryu, Amarenco, Pierre, Blom, Dirk J., Brinton, Eliot A., Eckel, Robert H., Elam, Marshall B., Felicio, João S., Ginsberg, Henry N., Goudev, Assen, Ishibashi, Shun, Joseph, Jacob, Kodama, Tatsuhiko, Koenig, Wolfgang, Leiter, Lawrence A., Lorenzatti, Alberto J., Mankovsky, Boris, Marx, Nikolaus, Nordestgaard, Børge G., Páll, Dénes, Ray, Kausik K., Santos, Raul D., Soran, Handrean, Susekov, Andrey, Tendera, Michal, Yokote, Koutaro, Paynter, Nina P., Buring, Julie E., Libby, Peter, Ridker, Paul M

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NAD+ precursor modulates post-ischemic mitochondrial fragmentation and reactive oxygen species generation via SIRT3 dependent mechanisms von Klimova, Nina, Fearnow, Adam, Long, Aaron, Kristian, Tibor

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Landscape of innate lymphoid cells in human head and neck cancer reveals divergent NK cell states in the tumor microenvironment von Moreno-Nieves, Uriel Y., Tay, Joshua K., Saumyaa, Saumyaa, Horowitz, Nina B., Shin, June Ho, Mohammad, Imran A., Luca, Bogdan, Mundy, David C., Gulati, Gunsagar S., Bedi, Nikita, Chang, Serena, Chen, Chen, Kaplan, Michael J., Rosenthal, Eben L., Holsinger, F. Christopher, Divi, Vasu, Baik, Fred M., Sirjani, Davud B., Gentles, Andrew J., Newman, Aaron M., Freud, Aharon G., Sunwoo, John B.

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Human preferences toward algorithmic advice in a word association task von Bogert, Eric, Lauharatanahirun, Nina, Schecter, Aaron

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