Forskolin induced swelling (FIS) assay in intestinal organoids to guide eligibility for compassionate use treatment in a CF patient with a rare genotype von Aalbers, B.L., Brunsveld, J.E., van der Ent, C.K., van den Eijnden, J.C., Beekman, J.M., Heijerman, H.G.M.

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Females with cystic fibrosis have a larger decrease in sweat chloride in response to lumacaftor/ivacaftor compared to males von Aalbers, B.L., Hofland, R.W., Bronsveld, I., de Winter-de Groot, K.M., Arets, H.G.M., de Kiviet, A.C., van Oirschot-van de Ven, M.M.M., Kruijswijk, M.A., Schotman, S., Michel, S., van der Ent, C.K., Heijerman, H.G.M.

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Clinical effect of lumacaftor/ivacaftor in F508del homozygous CF patients with FEV1 ≥ 90% predicted at baseline von Aalbers, B.L., de Winter-de Groot, K.M., Arets, H.G.M., Hofland, R.W., de Kiviet, A.C., van Oirschot-van de Ven, M.M.M., Kruijswijk, M.A., Schotman, S., Michel, S., van der Ent, C.K., Heijerman, H.G.M.

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P261 Clinical effect of lumacaftor/ivacaftor in F508del homozygous cystic fibrosis patients with FEV1 ≥90% predicted at baseline von Aalbers, B.L., de Winter-de Groot, K.M., Arets, H.G.M., Hofland, R.W., de Kiviet, A.C., van Oirschot-van de Ven, M.M.M., Kruijswijk, M.A., Schotman, S., Michel, S., van der Ent, C.K., Heijerman, H.G.M.

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