Sotatercept, a novel transforming growth factor β ligand trap, improves anemia in β-thalassemia: a phase II, open-label, dose-finding study von Cappellini, Maria Domenica, Porter, John, Origa, Raffaella, Forni, Gian Luca, Voskaridou, Ersi, Galactéros, Frédéric, Taher, Ali T, Arlet, Jean-Benoît, Ribeil, Jean-Antoine, Garbowski, Maciej, Graziadei, Giovanna, Brouzes, Chantal, Semeraro, Michaela, Laadem, Abderrahmane, Miteva, Dimana, Zou, Jun, Sung, Victoria, Zinger, Tatiana, Attie, Kenneth M, Hermine, Olivier

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Locally acting ACE‐083 increases muscle volume in healthy volunteers von Glasser, Chad E., Gartner, Michael R., Wilson, Dawn, Miller, Barry, Sherman, Matthew L., Attie, Kenneth M.

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A single ascending-dose study of muscle regulator ace-031 in healthy volunteers von Attie, Kenneth M., Borgstein, Niels G., Yang, Yijun, Condon, Carolyn H., Wilson, Dawn M., Pearsall, Amelia E., Kumar, Ravi, Willins, Debbie A., Seehra, Jas S., Sherman, Matthew L.

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The DART Study: Results from the Dose-Escalation and Expansion Cohorts Evaluating the Combination of Dalantercept plus Axitinib in Advanced Renal Cell Carcinoma von Voss, Martin H, Bhatt, Rupal S, Plimack, Elizabeth R, Rini, Brian I, Alter, Robert S, Beck, J Thaddeus, Wilson, Dawn, Zhang, Xiaosha, Mutyaba, Musa, Glasser, Chad, Attie, Kenneth M, Sherman, Matthew L, Pandya, Shuchi S, Atkins, Michael B

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Myostatin inhibitor ACE‐031 treatment of ambulatory boys with Duchenne muscular dystrophy: Results of a randomized, placebo‐controlled clinical trial von Campbell, Craig, McMillan, Hugh J., Mah, Jean K., Tarnopolsky, Mark, Selby, Kathryn, McClure, Ty, Wilson, Dawn M., Sherman, Matthew L., Escolar, Diana, Attie, Kenneth M.

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Luspatercept for the treatment of anaemia in patients with lower-risk myelodysplastic syndromes (PACE-MDS): a multicentre, open-label phase 2 dose-finding study with long-term exte... von Platzbecker, Uwe, Germing, Ulrich, Götze, Katharina S, Kiewe, Philipp, Mayer, Karin, Chromik, Jörg, Radsak, Markus, Wolff, Thomas, Zhang, Xiaosha, Laadem, Abderrahmane, Sherman, Matthew L, Attie, Kenneth M, Giagounidis, Aristoteles

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Luspatercept improves hemoglobin levels and blood transfusion requirements in a study of patients with β-thalassemia von Piga, Antonio, Perrotta, Silverio, Gamberini, Maria Rita, Voskaridou, Ersi, Melpignano, Angela, Filosa, Aldo, Caruso, Vincenzo, Pietrangelo, Antonello, Longo, Filomena, Tartaglione, Immacolata, Borgna-Pignatti, Caterina, Zhang, Xiaosha, Laadem, Abderrahmane, Sherman, Matthew L., Attie, Kenneth M.

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Effect of testosterone treatment on bone mineral density in men over 65 years of age von SNYDER, P. J, PEACHEY, H, ATTIE, M. F, HADDAD, J. G, STROM, B. L, HANNOUSH, P, BERLIN, J. A, LOH, L, HOLMES, J. H, DLEWATI, A, STALEY, J, SANTANNA, J, KAPOOR, S. C

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370-OR: Optimized Weight Loss with Bimagrumab—Reduced Fat Mass with Increased Muscle Mass by Appetite-Independent Mechanisms von ATTIE, KENNETH M., HEYMSFIELD, STEVEN B., MINDEHOLM, LINDA, SPRUILL, SUSAN, PRUZANSKI, MARK, KLICKSTEIN, LLOYD

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Long-term safety and erythroid response with luspatercept treatment in patients with β-thalassemia von Piga, Antonio, Longo, Filomena, Gamberini, Maria Rita, Voskaridou, Ersi, Ricchi, Paolo, Caruso, Vincenzo, Pietrangelo, Antonello, Zhang, Xiaosha, Shetty, Jeevan K., Attie, Kenneth M., Tartaglione, Immacolata

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Effect of Growth Hormone Treatment on Adult Height of Children with Idiopathic Short Stature von Hintz, Raymond L, Attie, Kenneth M, Baptista, Joyce, Roche, Alex

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Long-Term Efficacy and Safety of Luspatercept for Anemia Treatment in Patients With Lower-Risk Myelodysplastic Syndromes: The Phase II PACE-MDS Study von Platzbecker, Uwe, Götze, Katharina S, Kiewe, Philipp, Germing, Ulrich, Mayer, Karin, Radsak, Markus, Wolff, Thomas, Chromik, Joerg, Sockel, Katja, Oelschlägel, Uta, Haase, Detlef, Illmer, Thomas, Al-Ali, Haifa Kathrin, Silling, Gerda, Reynolds, Joseph G, Zhang, Xiaosha, Attie, Kenneth M, Shetty, Jeevan K, Giagounidis, Aristoteles

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Efficacy and Safety Results of Long-Term Growth Hormone Treatment of Idiopathic Short Stature von Kemp, Stephen F., Kuntze, Joyce, Attie, Kenneth M., Maneatis, Thomas, Butler, S., Frane, James, Lippe, Barbara

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Growth Hormone (GH) Dose-Response in Young Adults with Childhood-Onset GH Deficiency: A Two-Year, Multicenter, Multiple-Dose, Placebo-Controlled Study von Underwood, Louis E., Attie, Kenneth M., Baptista, Joyce

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A phase 1 study of ACE‐536, a regulator of erythroid differentiation, in healthy volunteers von Attie, Kenneth M., Allison, Mark J., McClure, Ty, Boyd, Ingrid E., Wilson, Dawn M., Pearsall, Amelia E., Sherman, Matthew L.

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Growth hormone therapy of Turner's syndrome: Beneficial effect on adult height von Rosenfeld, Ron G., Attie, Kenneth M., Frane, James, Brasel, Anne, Burstein, Stephen, Cara, Jose F., Chernausek, Steven, Gotlin, Ronald W., Kuntze, Joyce, Lippe, Barbara M., Mahoney, C.Patrick, Moore, Wayne V., Saenger, Paul, Johanson, Ann J.

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Randomized Phase 2 Study of ACE-083 in Patients With Charcot-Marie-Tooth Disease von Thomas, Florian P., Brannagan, Thomas H., Butterfield, Russell J., Desai, Urvi, Habib, Ali A., Herrmann, David N., Eichinger, Katy J., Johnson, Nicholas E., Karam, Chafic, Pestronk, Alan, Quinn, Colin, Shy, Michael E., Statland, Jeffrey M., Subramony, Sub H., Walk, David, Stevens-Favorite, Katherine, Miller, Barry, Leneus, Ashley, Fowler, Marcie, van de Rijn, Marc, Attie, Kenneth M.

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Sotatercept with long-term extension for the treatment of anaemia in patients with lower-risk myelodysplastic syndromes: a phase 2, dose-ranging trial von Komrokji, Rami, Garcia-Manero, Guillermo, Ades, Lionel, Prebet, Thomas, Steensma, David P, Jurcic, Joseph G, Sekeres, Mikkael A, Berdeja, Jesus, Savona, Michael R, Beyne-Rauzy, Odile, Stamatoullas, Aspasia, DeZern, Amy E, Delaunay, Jacques, Borthakur, Gautam, Rifkin, Robert, Boyd, Thomas E, Laadem, Abderrhamane, Vo, Bond, Zhang, Jennie, Puccio-Pick, Marie, Attie, Kenneth M, Fenaux, Pierre, List, Alan F

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Randomized phase 2 study of ACE‐083, a muscle‐promoting agent, in facioscapulohumeral muscular dystrophy von Statland, Jeffrey M., Campbell, Craig, Desai, Urvi, Karam, Chafic, Díaz‐Manera, Jordi, Guptill, Jeffrey T., Korngut, Lawrence, Genge, Angela, Tawil, Rabi N., Elman, Lauren, Joyce, Nanette C., Wagner, Kathryn R., Manousakis, Georgios, Amato, Anthony A., Butterfield, Russell J., Shieh, Perry B., Wicklund, Matthew, Gamez, Josep, Bodkin, Cynthia, Pestronk, Alan, Weihl, Conrad C., Vilchez‐Padilla, Juan J., Johnson, Nicholas E., Mathews, Katherine D., Miller, Barry, Leneus, Ashley, Fowler, Marcie, Rijn, Marc, Attie, Kenneth M.

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A phase 2 study of dalantercept, an activin receptor‐like kinase‐1 ligand trap, in patients with recurrent or metastatic squamous cell carcinoma of the head and neck von Jimeno, Antonio, Posner, Marshall R., Wirth, Lori J., Saba, Nabil F., Cohen, Roger B., Popa, Elizabeta C., Argiris, Athanassios, Grossmann, Kenneth F., Sukari, Ammar, Wilson, Dawn, Zhang, Xiaosha, Sun, Jade, Glasser, Chad, Attie, Kenneth M., Sherman, Matthew L., Pandya, Susan S., Weiss, Jared

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