Erratum to: Increased glucocerebrosidase (GBA) 2 activity in GBA1 deficient mice brains and in Gaucher leucocytes von Burke, Derek G., Rahim, Ahad A., Waddington, Simon N., Karlsson, Stefan, Enquist, Ida, Bhatia, Kailash, Mehta, Atul, Vellodi, Ashok, Heales, Simon

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Erratum to: Enzyme replacement therapy for mucopolysaccharidosis VI—experience in Taiwan von Lin, Hsiang-Yu, Chen, Ming-Ren, Chuang, Chih-Kuang, Chen, Chih-Ping, Lin, Dar-Shong, Chien, Yin-Hsiu, Ke, Yu-Yuan, Tsai, Fuu-Jen, Pan, Hui-Ping, Lin, Shio-Jean, Hwu, Wuh-Liang, Niu, Dau-Ming, Lee, Ni-Chung, Lin, Shuan-Pei

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Erratum to: Expanded newborn screening in Greece: 30 months of experience von Loukas, Yannis L., Soumelas, Georgios-Stefanos, Dotsikas, Yannis, Georgiou, Vassiliki, Molou, Elina, Thodi, Georgia, Boutsini, Maria, Biti, Sofia, Papadopoulos, Konstantinos

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Journal of Inherited Metabolic Disease

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Erratum to: Isolated remethylation disorders: do our treatments benefit patients? von Schiff, Manuel, Benoist, Jean-François, Tilea, Bogdana, Royer, Nicolas, Giraudier, Stéphane, de Baulny, Hélène Ogier

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Erratum to: Carnitine levels in 26,462 individuals from the nationwide screening program for primary carnitine deficiency in the Faroe Islands von Rasmussen, Jan, Nielsen, Olav W., Janzen, Nils, Duno, Morten, Gislason, Hannes, Køber, Lars, Steuerwald, Ulrike, Lund, Allan M.

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Erratum to: Females experience a more severe disease course in batten disease von Cialone, Jennifer, Adams, Heather, Augustine, Erika F., Marshall, Frederick J., Kwon, Jennifer M., Newhouse, Nicole, Vierhile, Amy, Levy, Erika, Dure, Leon S., Rose, Katherine R., Ramirez-Montealegre, Denia, de Blieck, Elisabeth A., Mink, Jonathan W.

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Erratum to: Urine analysis of glucose tetrasaccharide by HPLC; a useful marker for the investigation of patients with Pompe and other glycogen storage diseases von Manwaring, Victoria, Prunty, Helen, Bainbridge, Katie, Burke, Derek, Finnegan, Niamh, Franses, Rebecca, Lam, Amanda, Vellodi, Ashok, Heales, Simon

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Journal of inherited metabolic disease

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Erratum to: Diagnosis of tetrahydrobiopterin deficiency using filter paper blood spots: further development of the method and 5 years experience von Opladen, Thomas, Abu Seda, Bettina, Rassi, Anahita, Thöny, Beat, Hoffmann, Georg F., Blau, Nenad

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Erratum to: Is prenatal myo-inositol deficiency a mechanism of CNS injury in galactosemia? von Berry, Gerard T.

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Brain: Biochemistry and Inherited Metabolic Disease (The combined supplements 1 and 2 of Journal of inherited metabolic disease, vol. 5, 1982) von Shih, Vivian F.

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Brain: Biochemistry and Inherited Metabolic Disease (The combined supplements 1 and 2 of Journal of inherited metabolic disease, vol. 5, 1982) : edited by N. R. Belton, N. A. J. Carson, R. A. Harkness, R. J. Pollitt and J. Stern, MTP Press, 1982. £17.95 (x + 128 pages) ISBN 0 852 00484 2 von Shih, Vivian F.

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Clinical effectiveness of enzyme replacement therapy with galsulfase in mucopolysaccharidosis type VI treatment: Systematic review von Gomes, Dalila Fernandes, Gallo, Luciana Guerra, Leite, Betânia Ferreira, Silva, Roberta Borges, da Silva, Everton Nunes

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Enzyme replacement therapy with galsulfase for mucopolysaccharidosis type VI von Brunelli, Marcela Junqueira, Brunelli, Marcela Junqueira, Atallah, Álvaro N, da Silva, Edina MK

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Tyrosine supplementation for phenylketonuria von Remmington, Tracey, Remmington, Tracey, Smith, Sherie

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Dietary interventions (plant sterols, stanols, omega‐3 fatty acids, soy protein and dietary fibers) for familial hypercholesterolaemia von Malhotra, Anita, Shafiq, Nusrat, Arora, Anjuman, Singh, Meenu, Kumar, Rajendra, Malhotra, Samir, Shafiq, Nusrat

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Enzyme replacement therapy with galsulfase for mucopolysaccharidosis type VI von Brunelli, Marcela Junqueira, Atallah, Álvaro N, da Silva, Edina MK, Brunelli, Marcela Junqueira

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Ex-Vivo Autologous Stem Cell Gene Therapy Clinical Trial for Mucopolysaccharidosis Type IIIA: Trial in Progress - NCT04201405 von Kinsella, Jane L, Wynn, Robert F, Bigger, Brian, Thrasher, Adrian J., Booth, Claire, Buckland, Karen, Izotova, Natalia, Rust, Stewart, Weisberg, Daniel, Church, Heather J, Brammeier, Kathryn L, Tylee, Karen L, Jones, Ceri, Lee, Helena, Ford, Laura, Sadegholnejat, Atusa, Ellison, Stuart, Jones, Simon A

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Tyrosine supplementation for phenylketonuria von Webster, Diana, Wildgoose, Joanne, Webster, Diana

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