AAV vectors: The Rubik’s cube of human gene therapy von Pupo, Amaury, Fernández, Audry, Low, Siew Hui, François, Achille, Suárez-Amarán, Lester, Samulski, Richard Jude

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Human gene therapy von Anderson, W F

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Gene Insertion Into Genomic Safe Harbors for Human Gene Therapy von Papapetrou, Eirini P, Schambach, Axel

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Delivery and Specificity of CRISPR-Cas9 Genome Editing Technologies for Human Gene Therapy von Gori, Jennifer L, Hsu, Patrick D, Maeder, Morgan L, Shen, Shen, Welstead, G Grant, Bumcrot, David

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The Next Phase of Human Gene-Therapy Oversight von Collins, Francis S, Gottlieb, Scott

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Initial results from a first-in-human gene therapy trial on X-linked retinitis pigmentosa caused by mutations in RPGR von Cehajic-Kapetanovic, Jasmina, Xue, Kanmin, Martinez-Fernandez de la Camara, Cristina, Nanda, Anika, Davies, Alexandra, Wood, Laura J., Salvetti, Anna Paola, Fischer, M. Dominik, Aylward, James W., Barnard, Alun R., Jolly, Jasleen K., Luo, Edmond, Lujan, Brandon J., Ong, Tuyen, Girach, Aniz, Black, Graeme C. M., Gregori, Ninel Z., Davis, Janet L., Rosa, Potyra R., Lotery, Andrew J., Lam, Byron L., Stanga, Paulo E., MacLaren, Robert E.

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Virus-mediated gene delivery for human gene therapy von Giacca, Mauro, Zacchigna, Serena

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Current State of Human Gene Therapy: Approved Products and Vectors von Shchaslyvyi, Aladdin Y., Antonenko, Svitlana V., Tesliuk, Maksym G., Telegeev, Gennadiy D.

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Human gene therapy: A patent analysis von Zhou, Wuyuan, Wang, Xiang

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Quality Control Testing, Characterization and Critical Quality Attributes of Adeno‐Associated Virus Vectors Used for Human Gene Therapy von Wright, J. Fraser

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Genomic discovery of potent chromatin insulators for human gene therapy von Liu, Mingdong, Maurano, Matthew T, Wang, Hao, Qi, Heyuan, Song, Chao-Zhong, Navas, Patrick A, Emery, David W, Stamatoyannopoulos, John A, Stamatoyannopoulos, George

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The effect of human gene therapy for RPE65-associated Leber's congenital amaurosis on visual function: a systematic review and meta-analysis von Wang, Xue, Yu, Chaofeng, Tzekov, Radouil T, Zhu, Yihua, Li, Wensheng

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Human gene therapy: A scientometric analysis von Zhou, Wuyuan, Wang, Xiang

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Adeno-associated virus serotypes: vector toolkit for human gene therapy von Wu, Zhijian, Asokan, Aravind, Samulski, R Jude

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First-in-Human Gene Therapy Trial of AAV8-hCARp.hCNGB3 in Adults and Children With CNGB3-associated Achromatopsia von Michaelides, Michel, Hirji, Nashila, Wong, Sui Chien, Besirli, Cagri G., Zaman, Serena, Kumaran, Neruban, Georgiadis, Anastasios, Smith, Alexander J., Ripamonti, Caterina, Gottlob, Irene, Robson, Anthony G., Thiadens, Alberta, Henderson, Robert H., Fleck, Penny, Anglade, Eddy, Dong, Xiangwen, Capuano, George, Lu, Wentao, Berry, Pamela, Kane, Thomas, Naylor, Stuart, Georgiou, Michalis, Kalitzeos, Angelos, Ali, Robin R., Forbes, Alexandria, Bainbridge, James

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Human gene therapy for RPE65 isomerase deficiency activates the retinoid cycle of vision but with slow rod kinetics von Cideciyan, Artur V, Aleman, Tomas S, Boye, Sanford L, Schwartz, Sharon B, Kaushal, Shalesh, Roman, Alejandro J, Pang, Ji-jing, Sumaroka, Alexander, Windsor, Elizabeth A.M, Wilson, James M, Flotte, Terence R, Fishman, Gerald A, Heon, Elise, Stone, Edwin M, Byrne, Barry J, Jacobson, Samuel G, Hauswirth, William W

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30 Years Later-Reflections on Human Gene Therapy: An Interview with Terry Flotte, MD von Davies, Kevin

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Retroviral integration and human gene therapy von Bushman, Frederic D

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Prime Editing for Human Gene Therapy: Where Are We Now? von Godbout, Kelly, Tremblay, Jacques P

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Isolation of novel simian adenoviruses from macaques for development of a vector for human gene therapy and vaccines von Lan, Wendong, Quan, Lulu, Li, Yiqiang, Ou, Junxian, Duan, Biyan, Mei, Ting, Tan, Xiao, Chen, Weiwei, Feng, Liqiang, Wan, Chengsong, Zhao, Wei, Chodosh, James, Seto, Donald, Zhang, Qiwei

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